An Open-Label Dose Escalation Study to Evaluate the Safety of Administration of Nonviral Stromal Cell-Derived Factor-1 Plasmid to Treat Symptomatic Ischemic Heart Failure
Penn, Marc S, Mendelsohn, Farrell O, Schaer, Gary L, Sherman, Warren, Farr, MaryJane, Pastore, Joseph, Rouy, Didier, Clemens, Ruth, Aras, Rahul, Losordo, Douglas W
Published in Circulation research (01.03.2013)
Published in Circulation research (01.03.2013)
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Rationale and design of the Transendocardial Injection of Autologous Human Cells (bone marrow or mesenchymal) in Chronic Ischemic Left Ventricular Dysfunction and Heart Failure Secondary to Myocardial Infarction (TAC-HFT) trial: A randomized, double-blind, placebo-controlled study of safety and efficacy
Trachtenberg, Barry, MD, Velazquez, Darcy L., RN, BSN, Williams, Adam R., MD, McNiece, Ian, PhD, Fishman, Joel, MD, PhD, Nguyen, Kim, PhD, Rouy, Didier, MD, PhD, Altman, Peter, PhD, Schwarz, Richard, PhD, Mendizabal, Adam, MS, Oskouei, Behzad, MD, Byrnes, John, MD, Soto, Victor, MD, Tracy, Melissa, MD, Zambrano, Juan Pablo, MD, Heldman, Alan W., MD, Hare, Joshua M., MD
Published in The American heart journal (01.03.2011)
Published in The American heart journal (01.03.2011)
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Improvement of Local Cell Delivery Using Helix Transendocardial Delivery Catheter in a Porcine Heart
Mitsutake, Yoshiaki, Pyun, Wook Bum, Rouy, Didier, Foo, Cheryl Wong Po, Stertzer, Simon H., Altman, Peter, Ikeno, Fumiaki
Published in International Heart Journal (2017)
Published in International Heart Journal (2017)
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High-Efficiency Gene Transfer into Skeletal Muscle Mediated by Electric Pulses
Mir, Lluis M., Michel F. Bureau, Gehl, Julie, Rangara, Ravi, Rouy, Didier, Caillaud, Jean-Michel, Delaere, Pia, Branellec, Didier, Schwartz, Bertrand, Scherman, Daniel
Published in Proceedings of the National Academy of Sciences - PNAS (13.04.1999)
Published in Proceedings of the National Academy of Sciences - PNAS (13.04.1999)
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Comparison of Allogeneic vs Autologous Bone Marrow–Derived Mesenchymal Stem Cells Delivered by Transendocardial Injection in Patients With Ischemic Cardiomyopathy: The POSEIDON Randomized Trial
Hare, Joshua M, Fishman, Joel E, Gerstenblith, Gary, DiFede Velazquez, Darcy L, Zambrano, Juan P, Suncion, Viky Y, Tracy, Melissa, Ghersin, Eduard, Johnston, Peter V, Brinker, Jeffrey A, Breton, Elayne, Davis-Sproul, Janice, Schulman, Ivonne H, Byrnes, John, Mendizabal, Adam M, Lowery, Maureen H, Rouy, Didier, Altman, Peter, Wong Po Foo, Cheryl, Ruiz, Phillip, Amador, Alexandra, Da Silva, Jose, McNiece, Ian K, Heldman, Alan W
Published in JAMA : the journal of the American Medical Association (12.12.2012)
Published in JAMA : the journal of the American Medical Association (12.12.2012)
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Transendocardial Mesenchymal Stem Cells and Mononuclear Bone Marrow Cells for Ischemic Cardiomyopathy: The TAC-HFT Randomized Trial
Heldman, Alan W, DiFede, Darcy L, Fishman, Joel E, Zambrano, Juan P, Trachtenberg, Barry H, Karantalis, Vasileios, Mushtaq, Muzammil, Williams, Adam R, Suncion, Viky Y, McNiece, Ian K, Ghersin, Eduard, Soto, Victor, Lopera, Gustavo, Miki, Roberto, Willens, Howard, Hendel, Robert, Mitrani, Raul, Pattany, Pradip, Feigenbaum, Gary, Oskouei, Behzad, Byrnes, John, Lowery, Maureen H, Sierra, Julio, Pujol, Mariesty V, Delgado, Cindy, Gonzalez, Phillip J, Rodriguez, Jose E, Bagno, Luiza Lima, Rouy, Didier, Altman, Peter, Foo, Cheryl Wong Po, da Silva, Jose, Anderson, Erica, Schwarz, Richard, Mendizabal, Adam, Hare, Joshua M
Published in JAMA : the journal of the American Medical Association (01.01.2014)
Published in JAMA : the journal of the American Medical Association (01.01.2014)
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Journal Article
Intramyocardial Stem Cell Injection in Patients With Ischemic Cardiomyopathy: Functional Recovery and Reverse Remodeling
Williams, Adam R, Trachtenberg, Barry, Velazquez, Darcy L, McNiece, Ian, Altman, Peter, Rouy, Didier, Mendizabal, Adam M, Pattany, Pradip M, Lopera, Gustavo A, Fishman, Joel, Zambrano, Juan P, Heldman, Alan W, Hare, Joshua M
Published in Circulation research (01.04.2011)
Published in Circulation research (01.04.2011)
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Four-Year Follow-up of the Alta Study, a Phase 1/2 Study of Giroctocogene Fitelparvovec (PF-07055480/SB-525) Gene Therapy in Adults with Severe Hemophilia Α
Harrington, Thomas J., Giermasz, Adam, Visweshwar, Nathan, Leavitt, Andrew D., Konkle, Barbara A., Rupon, Jeremy, Dirusso, Gregory, Tseng, Li-Jung, de los Angeles Resa, Maria, Ganne, Florence, Agathon, Delphine, Plonski, Frank, Rouy, Didier, Cockroft, Bettina M., Fang, Annie F., Arkin, Steven
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Updated Results of a Phase 1/2 Clinical Study of Zinc Finger Nuclease-Mediated Editing of BCL11A in Autologous Hematopoietic Stem Cells for Transfusion-Dependent Beta Thalassemia
Walters, Mark C., Smith, Angela R., Schiller, Gary J., Esrick, Erica B., Williams, David A., Gogoleva, Tatiana, Rouy, Didier, Cockroft, Bettina M., Vercellotti, Gregory M.
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Updated Results of the Alta Study, a Phase 1/2 Study of Giroctocogene Fitelparvovec (PF-07055480/SB-525) Gene Therapy in Adults with Severe Hemophilia Α
Giermasz, Adam, Visweshwar, Nathan, Harrington, Thomas J., Leavitt, Andrew D, Konkle, Barbara, Rupon, Jeremy, Di Russo, Gregory, Tseng, Li-Jung, de los Angeles Resa, Maria, Ganne, Florence, Agathon, Delphine, Plonski, Frank, Rouy, Didier, Cockroft, Bettina M., Fang, Annie, Arkin, Steven
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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Updated Follow-up of the Alta Study, a Phase 1/2, Open Label, Adaptive, Dose-Ranging Study to Assess the Safety and Tolerability of SB-525 Gene Therapy in Adult Patients with Severe Hemophilia A
Konkle, Barbara A., Stine, Kimo, Visweshwar, Nathan, Harrington, Thomas J., Leavitt, Andrew D., Giermasz, Adam, Arkin, Steven, Di Russo, Gregory, Snyder, Ashley, Woolfson, Adrian, Rouy, Didier
Published in Blood (13.11.2019)
Published in Blood (13.11.2019)
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Journal Article
Updated Follow-up of the Alta Study, a Phase 1/2 Study of Giroctocogene Fitelparvovec (SB-525) Gene Therapy in Adults with Severe Hemophilia a
Leavitt, Andrew D., Konkle, Barbara A., Stine, Kimo, Visweshwar, Nathan, Harrington, Thomas J., Giermasz, Adam, Arkin, Steven, Fang, Annie, Plonski, Frank, Smith, Lynne, Tseng, Li-Jung, Di Russo, Gregory, Cockroft, Bettina M, Rupon, Jeremy, Rouy, Didier
Published in Blood (05.11.2020)
Published in Blood (05.11.2020)
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Journal Article
Updated Results of the Alta Study, a Phase 1/2 Study of Giroctocogene Fitelparvovec (PF-07055480/SB-525) Gene Therapy in Adults with Severe Hemophilia a
Visweshwar, Nathan, Harrington, Thomas J., Leavitt, Andrew D, Konkle, Barbara A., Giermasz, Adam, Stine, Kimo, Rupon, Jeremy, Di Russo, Gregory, Tseng, Li-Jung, de los Angeles Resa, Maria, Ganne, Florence, Agathon, Delphine, Plonski, Frank, Rouy, Didier, Cockroft, Bettina M., Fang, Annie, Arkin, Steven
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Plasma storage at −80 °C does not protect matrix metalloproteinase-9 from degradation
Rouy, Didier, Ernens, Isabelle, Jeanty, Céline, Wagner, Daniel R.
Published in Analytical biochemistry (15.03.2005)
Published in Analytical biochemistry (15.03.2005)
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First-in-human in vivo genome editing via AAV-zinc-finger nucleases for mucopolysaccharidosis I/II and hemophilia B
Harmatz, Paul, Prada, Carlos E., Burton, Barbara K., Lau, Heather, Kessler, Craig M., Cao, Liching, Falaleeva, Marina, Villegas, Andres G., Zeitler, Jennifer, Meyer, Kathleen, Miller, Weston, Wong Po Foo, Cheryl, Vaidya, Sagar, Swenson, Wendy, Shiue, Lisa H., Rouy, Didier, Muenzer, Joseph
Published in Molecular therapy (07.12.2022)
Published in Molecular therapy (07.12.2022)
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Journal Article
Plasma storage at -80 degrees C does not protect matrix metalloproteinase-9 from degradation
Rouy, Didier, Ernens, Isabelle, Jeanty, Céline, Wagner, Daniel R
Published in Analytical biochemistry (15.03.2005)
Published in Analytical biochemistry (15.03.2005)
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HDL3 binds to glycosylphosphatidylinositol-anchored proteins to activate signalling pathways
Nazih-Sanderson, F, Lestavel, S, Nion, S, Rouy, D, Denefle, P, Fruchart, J C, Clavey, V, Delbart, C
Published in Biochimica et biophysica acta (21.08.1997)
Published in Biochimica et biophysica acta (21.08.1997)
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