Extensive multilineage analysis in patients with mixed chimerism after allogeneic transplantation for sickle cell disease: insight into hematopoiesis and engraftment thresholds for gene therapy
Magnani, Alessandra, Pondarré, Corinne, Bouazza, Naïm, Magalon, Jeremy, Miccio, Annarita, Six, Emmanuelle, Roudaut, Cecile, Arnaud, Cécile, Kamdem, Annie, Touzot, Fabien, Gabrion, Aurélie, Magrin, Elisa, Couzin, Chloé, Fusaro, Mathieu, André, Isabelle, Vernant, Jean-Paul, Gluckman, Eliane, Bernaudin, Françoise, Bories, Dominique, Cavazzana, Marina
Published in Haematologica (Roma) (01.05.2020)
Published in Haematologica (Roma) (01.05.2020)
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Journal Article
Long-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: the HGB-205 trial
Magrin, Elisa, Semeraro, Michaela, Hebert, Nicolas, Joseph, Laure, Magnani, Alessandra, Chalumeau, Anne, Gabrion, Aurélie, Roudaut, Cécile, Marouene, Jouda, Lefrere, Francois, Diana, Jean-Sebastien, Denis, Adeline, Neven, Bénédicte, Funck-Brentano, Isabelle, Negre, Olivier, Renolleau, Sylvain, Brousse, Valentine, Kiger, Laurent, Touzot, Fabien, Poirot, Catherine, Bourget, Philippe, El Nemer, Wassim, Blanche, Stéphane, Tréluyer, Jean-Marc, Asmal, Mohammed, Walls, Courtney, Beuzard, Yves, Schmidt, Manfred, Hacein-Bey-Abina, Salima, Asnafi, Vahid, Guichard, Isabelle, Poirée, Maryline, Monpoux, Fabrice, Touraine, Philippe, Brouzes, Chantal, de Montalembert, Mariane, Payen, Emmanuel, Six, Emmanuelle, Ribeil, Jean-Antoine, Miccio, Annarita, Bartolucci, Pablo, Leboulch, Philippe, Cavazzana, Marina
Published in Nature medicine (01.01.2022)
Published in Nature medicine (01.01.2022)
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Journal Article
Clonal tracking in gene therapy patients reveals a diversity of human hematopoietic differentiation programs
Six, Emmanuelle, Guilloux, Agathe, Denis, Adeline, Lecoules, Arnaud, Magnani, Alessandra, Vilette, Romain, Male, Frances, Cagnard, Nicolas, Delville, Marianne, Magrin, Elisa, Caccavelli, Laure, Roudaut, Cécile, Plantier, Clemence, Sobrino, Steicy, Gregg, John, Nobles, Christopher L., Everett, John K., Hacein-Bey-Abina, Salima, Galy, Anne, Fischer, Alain, Thrasher, Adrian J., André, Isabelle, Cavazzana, Marina, Bushman, Frederic D.
Published in Blood (09.04.2020)
Published in Blood (09.04.2020)
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Journal Article
Severe hematopoietic stem cell inflammation compromises chronic granulomatous disease gene therapy
Sobrino, Steicy, Magnani, Alessandra, Semeraro, Michaela, Martignetti, Loredana, Cortal, Akira, Denis, Adeline, Couzin, Chloé, Picard, Capucine, Bustamante, Jacinta, Magrin, Elisa, Joseph, Laure, Roudaut, Cécile, Gabrion, Aurélie, Soheili, Tayebeh, Cordier, Corinne, Lortholary, Olivier, Lefrere, François, Rieux-Laucat, Frédéric, Casanova, Jean-Laurent, Bodard, Sylvain, Boddaert, Nathalie, Thrasher, Adrian J., Touzot, Fabien, Taque, Sophie, Suarez, Felipe, Marcais, Ambroise, Guilloux, Agathe, Lagresle-Peyrou, Chantal, Galy, Anne, Rausell, Antonio, Blanche, Stephane, Cavazzana, Marina, Six, Emmanuelle
Published in Cell reports. Medicine (21.02.2023)
Published in Cell reports. Medicine (21.02.2023)
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Journal Article
Successful in utero stem cell transplantation in X-linked severe combined immunodeficiency
Magnani, Alessandra, Jouannic, Jean-Marie, Rosain, Jérémie, Gabrion, Aurélie, Touzot, Fabien, Roudaut, Cécile, Kracker, Sven, Mahlaoui, Nizar, Toubert, Antoine, Clave, Emmanuel, Macintyre, Elisabeth A., Radford-Weiss, Isabelle, Alcantara, Marion, Magrin, Elisa, Ternaux, Brigitte, Nisoy, Jennifer, Caccavelli, Laure, Darras, Anne-Marie, Picard, Capucine, Blanche, Stéphane, Cavazzana, Marina
Published in Blood advances (12.02.2019)
Published in Blood advances (12.02.2019)
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Journal Article
Long-Term Follow-up Study after Lentiviral Hematopoietic Stem/Progenitor Cell Gene Therapy for Wiskott - Aldrich Syndrome
Magnani, Alessandra, Semeraro, Michaela, ADAM, Frédéric, Booth, Claire, Dupre, Loic, Morris, Emma C, Gabrion, Aurélie, Roudaut, Cecile, Borgel, Delphine, Toubert, Antoine, Clave, Emmanuel, Abdo, Chrystelle, Gorochov, Guy, Petermann, Rachel, Guiot, Mélanie, Miyara, Makoto, Moshous, Despina, Magrin, Elisa, Denis, Adeline, Suarez, Felipe, Lagresle-Peyrou, Chantal, Doto, Aoife, Everett, John K., Trinquand, Amélie, Guisset, Marianne, Xu-Bayford, Jin Hua, Hacein-Bey-Abina, Salima, Kauskot, Alexandre, Elfeky, Reem, Rivat, Christine, Abbas, Sarah, Gaspar, Bobby H, Macintyre, Elizabeth A., Picard, Capucine, Bushman, Frederic D., Galy, Anne, Fischer, Alain, Six, Emmanuelle, Thrasher, Adrian J., Cavazzana, Marina
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Journal Article
Diverse and Distinct Human Hematopoietic Differentiation Programs Generate By Bone Marrow and G-CSF Mobilized Hematopoietic Stem and Progenitors Cells
Six, Emmanuelle, Guilloux, Agathe, Nobles, Christopher, Zreik, Rawya, Lecoules, Arnaud, Everett, John, Vilette, Romain, Cagnard, Nicolas, Male, Frances, Magnani, Alessandra, Magrin, Elisa, Caccavelli, Laure, Roudaut, Cecile, Plantier, Clemence, Galy, Anne, Thrasher, Adrian J, Andre-Schmutz, Isabelle, Berry, Charles C, Cavazzana, Marina, Bushman, Frederic D
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Journal Article
754. Exploring the Human Hematopoietic Hierarchy Through Retroviral Integration Sites Tracking in the Wiskott Aldrich Syndrome Gene Therapy Trial
Six, Emmanuelle, Caccavelli, Laure, Roudaut, Cecile, Male, Frances, Wu, Yinghua, Cagnard, Nicolas, Magnani, Alessandra, Touzot, Fabien, Magrin, Elisa, Galy, Anne, André-Schmutz, Isabelle, Abina, Salima Hacein-Bey, Jais, Jean-Philippe, Berry, Charles C., Bushman, Frederic D., Cavazzana, Marina
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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Journal Article
Preclinical Assessment for Gene Addition Strategy in Familial Hemophagocytic Lymphohistiocytosis Related to Munc 13-4 Deficiency
Lagresle-Peyrou, Chantal, Diana, Jean-Sebastien, Magrin, Elisa, Aussel, Clotilde, Sorel, Natael, Aslan, Yetki, Roudaut, Cécile, Schwartz, Eden, Gabrion, Aurélie, Tuchmann-Durand, Caroline, Lefrere, Francois, Galy, Anne, Moshous, Despina, Cavazzana, Marina
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
Clinical Results of the Drepaglobe Trial for Sickle Cell Disease Patients
Magrin, Elisa, Magnani, Alessandra, Semeraro, Michaela, Hebert, Nicolas, Joseph, Laure, Leblanc, Olivia, Gabrion, Aurélie, Roudaut, Cécile, Maulet, Axelle, Chalumeau, Anne, Kiger, Laurent, Marouene, Jouda, Jolaine, Valérie, Treluyer, Jean-Marc, Marçais, Ambroise, Suarez, Felipe, Hermine, Olivier, Mavilio, Fulvio, Six, Emmanuelle, El Nemer, Wassim, Bartolucci, Pablo, Miccio, Annarita, Cavazzana, Marina
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Journal Article
689. The Content of the More Immature Hematopoietic Stem Cells (HSCs) Is Dependent from the Underlying Genetic Diseases: Consequence on Transduction Efficiencies
Caccavelli, Laure, Roudaut, Cécile, Joigneaux, Maeva, Blondeau, Johanna, Touzot, Fabien, Hacein-Bey-Abina, Salima, Cavazzana, Marina
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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Journal Article
225. Preserving CD4+ T-Cells Phenotype and Function Upon Ex Vivo Lentiviral Transduction
Hmitou, Isabelle, Ouedrani, Amani, Djerroudi, Lounes, Roudaut, Cécile, Caccavelli, Laure, Soheili, Tayebeh S., André-Schmutz, Isabelle, Cavazzana, Marina, Touzot, Fabien
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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Journal Article
B Cell Reconstitution after Gene Therapy in Patients with Wiskott Aldrich Syndrome and Comparison with Mismatched Allogeneic Hematopoietic Stem Cell Transplantation
Magnani, Alessandra, Roudaut, Cécile, Gabrion, Aurelie, Caccavelli, Laure, Touzot, Fabien, Neven, Benedicte, Moshous, Despina, Mahlaoui, Nizar, Clave, Emmanuel, Toubert, Antoine, Fischer, Alain, Cavazzana, Marina
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
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Journal Article
425. Production of Gene Corrected T Cell Precursors for Therapy of SCID X1
Lagresle-Peyrou, Chantal, Roudaut, Cécile, Gabrion, Aurélie, Caccavelli, Laure, Sadek, Hanem, Chouteau, Myriam, Reimann, Christian, Hacein-Bey-Abina, Salima, Cavazzana, Marina, André-Schmutz, Isabelle
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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Journal Article
a Diversity of Human Hematopoietic Differentiation Programs Identified through In Vivo Tracking of Hematopoiesis in Wiskott-Aldrich Syndrome Patients
Six, Emmanuelle, Caccavelli, Laure, Lecoules, Arnaud, Nobles, Christopher L, Male, France, Roudaut, Cécile, Plantier, Clemence, Magnani, Alessandra, Magrin, Elisa, Cagnard, Nicolas, Galy, Anne, Thrasher, Adrian J, hacein-Bey Abina, Salima, Guilloux, Agathe, Andre-Schmutz, Isabelle, Berry, Charles C., Bushman, frederic D., Cavazzana, Marina
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article