Adeno-Associated Virus Vector Genomes Persist as Episomal Chromatin in Primate Muscle
PENAUD-BUDLOO, Magalie, LE GUINER, Caroline, SNYDER, Richard O, NOWROUZI, Ali, TOROMANOFF, Alice, CHEREL, Yan, CHENUAUD, Pierre, SCHMIDT, Manfred, VON KALLE, Christof, ROLLING, Fabienne, MOULLIER, Philippe
Published in Journal of Virology (01.08.2008)
Published in Journal of Virology (01.08.2008)
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Transgene regulation using the tetracycline-inducible TetR-KRAB system after AAV-mediated gene transfer in rodents and nonhuman primates
Le Guiner, Caroline, Stieger, Knut, Toromanoff, Alice, Guilbaud, Mickaël, Mendes-Madeira, Alexandra, Devaux, Marie, Guigand, Lydie, Cherel, Yan, Moullier, Philippe, Rolling, Fabienne, Adjali, Oumeya
Published in PloS one (23.09.2014)
Published in PloS one (23.09.2014)
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Successful Gene Therapy in the RPGRIP1-deficient Dog: a Large Model of Cone–Rod Dystrophy
Lhériteau, Elsa, Petit, Lolita, Weber, Michel, Le Meur, Guylène, Deschamps, Jack-Yves, Libeau, Lyse, Mendes-Madeira, Alexandra, Guihal, Caroline, François, Achille, Guyon, Richard, Provost, Nathalie, Lemoine, Françoise, Papal, Samantha, El-Amraoui, Aziz, Colle, Marie-Anne, Moullier, Philippe, Rolling, Fabienne
Published in Molecular therapy (01.02.2014)
Published in Molecular therapy (01.02.2014)
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Cross-Packaging of a Single Adeno-Associated Virus (AAV) Type 2 Vector Genome into Multiple AAV Serotypes Enables Transduction with Broad Specificity
Rabinowitz, Joseph E, Rolling, Fabienne, Li, Chengwen, Conrath, Hervè, Xiao, Weidong, Xiao, Xiao, Samulski, R Jude
Published in Journal of Virology (01.01.2002)
Published in Journal of Virology (01.01.2002)
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Detection of Intact rAAV Particles up to 6 Years After Successful Gene Transfer in the Retina of Dogs and Primates
Stieger, Knut, Schroeder, Josef, Provost, Nathalie, Mendes-Madeira, Alexandra, Belbellaa, Brahim, Meur, Guylène Le, Weber, Michel, Deschamps, Jack-Yves, Lorenz, Birgit, Moullier, Philippe, Rolling, Fabienne
Published in Molecular therapy (01.03.2009)
Published in Molecular therapy (01.03.2009)
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Immuno-histochemical analysis of rod and cone reaction to RPE65 deficiency in the inferior and superior canine retina
Klein, Daniela, Mendes-Madeira, Alexandra, Schlegel, Patrice, Rolling, Fabienne, Lorenz, Birgit, Haverkamp, Silke, Stieger, Knut
Published in PloS one (21.01.2014)
Published in PloS one (21.01.2014)
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Long-term doxycycline-regulated transgene expression in the retina of nonhuman primates following subretinal injection of recombinant AAV vectors
Stieger, Knut, Le Meur, Guylène, Lasne, Françoise, Weber, Michel, Deschamps, Jack-Yves, Nivard, Delphine, Mendes-Madeira, Alexandra, Provost, Nathalie, Martin, Laurent, Moullier, Philippe, Rolling, Fabienne
Published in Molecular therapy (01.05.2006)
Published in Molecular therapy (01.05.2006)
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Preclinical studies on specific gene therapy for recessive retinal degenerative diseases
Stieger, Knut, Chauveau, Christine, Rolling, Fabienne
Published in Current gene therapy (01.10.2010)
Published in Current gene therapy (01.10.2010)
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Journal Article
Immune responses to gene product of inducible promoters
Le Guiner, Caroline, Stieger, Knut, Snyder, Richard O, Rolling, Fabienne, Moullier, Philippe
Published in Current gene therapy (01.10.2007)
Published in Current gene therapy (01.10.2007)
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Journal Article
Adeno-associated virus capsid serotype identification: Analytical methods development and application
Van Vliet, Kim, Mohiuddin, Yasmin, McClung, Scott, Blouin, Veronique, Rolling, Fabienne, Moullier, Philippe, Agbandje-McKenna, Mavis, Snyder, Richard O.
Published in Journal of virological methods (01.08.2009)
Published in Journal of virological methods (01.08.2009)
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Journal Article
Safety and Long-Term Efficacy of AAV4 Gene Therapy in Patients with RPE65 Leber Congenital Amaurosis
Le Meur, Guylène, Lebranchu, Pierre, Billaud, Fanny, Adjali, Oumeya, Schmitt, Sébastien, Bézieau, Stéphane, Péréon, Yann, Valabregue, Romain, Ivan, Catherine, Darmon, Christophe, Moullier, Philippe, Rolling, Fabienne, Weber, Michel
Published in Molecular therapy (03.01.2018)
Published in Molecular therapy (03.01.2018)
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Journal Article
In vivo gene regulation using tetracycline-regulatable systems
Stieger, Knut, Belbellaa, Brahim, Le Guiner, Caroline, Moullier, Philippe, Rolling, Fabienne
Published in Advanced drug delivery reviews (02.07.2009)
Published in Advanced drug delivery reviews (02.07.2009)
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AAV-mediated Gene Therapy Halts Retinal Degeneration in PDE6β-deficient Dogs
Pichard, Virginie, Provost, Nathalie, Mendes-Madeira, Alexandra, Libeau, Lyse, Hulin, Philippe, Tshilenge, Kizito-Tshitoko, Biget, Marine, Ameline, Baptiste, Deschamps, Jack-Yves, Weber, Michel, Le Meur, Guylène, Colle, Marie-Anne, Moullier, Philippe, Rolling, Fabienne
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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Journal Article
Restoration of Vision in the pde6β-deficient Dog, a Large Animal Model of Rod-cone Dystrophy
Petit, Lolita, Lhériteau, Elsa, Weber, Michel, Le Meur, Guylène, Deschamps, Jack-Yves, Provost, Nathalie, Mendes-Madeira, Alexandra, Libeau, Lyse, Guihal, Caroline, Colle, Marie-Anne, Moullier, Philippe, Rolling, Fabienne
Published in Molecular therapy (01.11.2012)
Published in Molecular therapy (01.11.2012)
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Efficient central nervous system AAVrh10-mediated intrathecal gene transfer in adult and neonate rats
Hordeaux, J, Dubreil, L, Deniaud, J, Iacobelli, F, Moreau, S, Ledevin, M, Le Guiner, C, Blouin, V, Le Duff, J, Mendes-Madeira, A, Rolling, F, Cherel, Y, Moullier, P, Colle, M-A
Published in Gene therapy (01.04.2015)
Published in Gene therapy (01.04.2015)
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Journal Article
Restoration of vision in RPE65-deficient Briard dogs using an AAV serotype 4 vector that specifically targets the retinal pigmented epithelium
LE MEUR, G, STIEGER, K, ALI, R. R, HAMEL, C, MOULLIER, P, ROLLING, F, SMITH, A. J, WEBER, M, DESCHAMPS, J. Y, NIVARD, D, MENDES-MADEIRA, A, PROVOST, N, PEREON, Y, CHEREL, Y
Published in Gene therapy (01.02.2007)
Published in Gene therapy (01.02.2007)
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Journal Article
Lack of Immunotoxicity After Regional Intravenous (RI) Delivery of rAAV to Nonhuman Primate Skeletal Muscle
Toromanoff, Alice, Adjali, Oumeya, Larcher, Thibaut, Hill, Marcelo, Guigand, Lydie, Chenuaud, Pierre, Deschamps, Jack-Yves, Gauthier, Olivier, Blancho, Gilles, Vanhove, Bernard, Rolling, Fabienne, Chérel, Yan, Moullier, Philippe, Anegon, Ignacio, Le Guiner, Caroline
Published in Molecular therapy (01.01.2010)
Published in Molecular therapy (01.01.2010)
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Journal Article
Safety and Efficacy of Regional Intravenous (RI) Versus Intramuscular (IM) Delivery of rAAV1 and rAAV8 to Nonhuman Primate Skeletal Muscle
Toromanoff, Alice, Chérel, Yan, Guilbaud, Mickaël, Penaud-Budloo, Magalie, Snyder, Richard O, Haskins, Mark E, Deschamps, Jack-Yves, Guigand, Lydie, Podevin, Guillaume, Arruda, Valder R, High, Katherine A, Stedman, Hansell H, Rolling, Fabienne, Anegon, Ignacio, Moullier, Philippe, Le Guiner, Caroline
Published in Molecular therapy (01.07.2008)
Published in Molecular therapy (01.07.2008)
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