I06 Allele-selective inhibition of mutant htt transcription throughout the brain after subcutaneous administration of a patrol™-enabled investigational genetic therapy in the r6/2 Huntington’s disease transgenic mouse model
Friedlander, Robert M, Caro, Valentina Di, Carlisle, Diane L, Monks, Noel R, Stoltzfus, Dani M, Bennett, Natasha L, Suofu, Yalikun, Kim, Jinho, Li, Fang, Wang, Xiaomin, Yeh, Stacy M, Baranov, Oxana V, Baranov, Sergei V, Badeau, Barry A, Gleaton, Jeremy W, Cintrón-Rosado, Gabriel A, Dyer, Ryan R, Stephan, Dietrich A, Mann, William R, Rojas-Caro, Sandra E
Published in Journal of neurology, neurosurgery and psychiatry (12.09.2022)
Published in Journal of neurology, neurosurgery and psychiatry (12.09.2022)
Get full text
Journal Article