Single Systemic Administration of a Gene Therapy Leading to Disease Treatment in Metachromatic Leukodystrophy Arsa Knock-Out Mice
St Martin, Thia, Seabrook, Tania A, Gall, Katherine, Newman, Jenn, Avila, Nancy, Hayes, April, Kivaa, Monicah, Lotterhand, Jason, Mercaldi, Michael, Patel, Kruti, Rivas, Israel J, Woodcock, Stephen, Wright, Teresa L, Seymour, Albert B, Francone, Omar L, Gingras, Jacinthe
Published in The Journal of neuroscience (10.05.2023)
Published in The Journal of neuroscience (10.05.2023)
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