Enhanced Enrichment and Purification of Blood-Derived T-Cells Using a Novel Hydrogel Technology
Armstead, Andrea, Kevlahan, Sean, Reil, Darcy, Bortell, Rita, Brehm, Michael
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
Get full text
Journal Article
Limb Perfusion Delivery of a rAAV1 Alpha-1 Antitrypsin Vector in Non-Human Primates Is Safe but Insufficient for Therapy
Pires-Ferreira, Debora, Reil, Darcy, Tang, Qiushi, Blackwood, Meghan, Gallagher, Thomas, Keeler, Allison M., Chichester, Jessica A., Vyhnal, Kristin K., Lindborg, Jane A., Benson, Janet, Fu, Dongtao, Flotte, Terence R., Gruntman, Alisha M.
Published in Genes (10.09.2024)
Published in Genes (10.09.2024)
Get full text
Journal Article
Biodistribution and safety of a single rAAV3B-AAT vector for silencing and replacement of alpha-1 antitrypsin in Cynomolgus macaques
Blackwood, Meghan, Gruntman, Alisha M., Tang, Qiushi, Pires-Ferreira, Debora, Reil, Darcy, Kondratov, Oleksandr, Marsic, Damien, Zolotukhin, Sergei, Gernoux, Gwladys, Keeler, Allison M., Mueller, Christian, Flotte, Terence R.
Published in Molecular therapy. Methods & clinical development (14.03.2024)
Published in Molecular therapy. Methods & clinical development (14.03.2024)
Get full text
Journal Article
705. Selective Advantage of Hepatocytes Expressing Wild-Type Alpha-1 Antitrypsin (AAT) in a Novel Human Liver Xenograft Model: A Model for Correction of a Gain-Of-Function Mutation
Tang, Qiushi, BrehmM, Michael S., Flotte, Terence R., Reil, Darcy L., Shultz, Leonard D., Greiner, Dale L., Mueller, Christian
Published in Molecular therapy (01.05.2015)
Published in Molecular therapy (01.05.2015)
Get full text
Journal Article