Ribitol dose-dependently enhances matriglycan expression and improves muscle function with prolonged life span in limb girdle muscular dystrophy 2I mouse model
Wu, Bo, Drains, Morgan, Shah, Sapana N, Lu, Pei Juan, Leroy, Victoria, Killilee, Jessalyn, Rawls, Raegan, Tucker, Jason D, Blaeser, Anthony, Lu, Qi Long
Published in PloS one (01.12.2022)
Published in PloS one (01.12.2022)
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Journal Article
Ribitol dose-dependently enhances matriglycan expression and improves muscle function with prolonged life span in limb girdle muscular dystrophy 2I mouse model
Bo Wu, Morgan Drains, Sapana N. Shah, Pei Juan Lu, Victoria Leroy, Jessalyn Killilee, Raegan Rawls, Jason D. Tucker, Anthony Blaeser, Qi Long Lu
Published in PloS one (01.12.2022)
Published in PloS one (01.12.2022)
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Journal Article
Improved efficacy of FKRP AAV gene therapy by combination with ribitol treatment for LGMD2I
Cataldi, Marcela P, Vannoy, Charles H, Blaeser, Anthony, Tucker, Jason D, Leroy, Victoria, Rawls, Raegan, Killilee, Jessalyn, Holbrook, Molly C, Lu, Qi Long
Published in Molecular therapy (06.12.2023)
Published in Molecular therapy (06.12.2023)
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Journal Article