Delivery Approaches for Therapeutic Genome Editing and Challenges
Ates, Ilayda, Rathbone, Tanner, Stuart, Callie, Bridges, P Hudson, Cottle, Renee N
Published in Genes (23.09.2020)
Published in Genes (23.09.2020)
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Journal Article
Ex vivo gene editing and cell therapy for hereditary tyrosinemia type 1
Ates, Ilayda, Stuart, Callie, Rathbone, Tanner, Barzi, Mercedes, He, Gordon, Major, Angela M, Shankar, Vijay, Lyman, Rachel A, Angner, Sidney S, Mackay, Trudy F C, Srinivasan, Shanthi, Farris, Alton Brad, Bissig, Karl-Dimiter, Cottle, Renee N
Published in Hepatology communications (01.05.2024)
Published in Hepatology communications (01.05.2024)
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Journal Article
Electroporation-Mediated Delivery of Cas9 Ribonucleoproteins Results in High Levels of Gene Editing in Primary Hepatocytes
Rathbone, Tanner, Ates, Ilayda, Fernando, Lawrence, Addlestone, Ethan, Lee, Ciaran M, Richards, Vincent P, Cottle, Renee N
Published in CRISPR journal (01.06.2022)
Published in CRISPR journal (01.06.2022)
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Journal Article