Recombinant factor IX Fc fusion protein in children with haemophilia B (Kids B-LONG): results from a multicentre, non-randomised phase 3 study
Fischer, Kathelijn, Kulkarni, Roshni, Nolan, Beatrice, Mahlangu, Johnny, Rangarajan, Savita, Gambino, Giulia, Diao, Lei, Ramirez-Santiago, Alejandra, Pierce, Glenn F, Allen, Geoffrey
Published in The Lancet. Haematology (01.02.2017)
Published in The Lancet. Haematology (01.02.2017)
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Phase 3 Study of Danicopan, an Oral Complement Factor D Inhibitor, As Add-on Therapy to a C5 Inhibitor in Patients with Paroxysmal Nocturnal Hemoglobinuria with Clinically Evident Extravascular Hemolysis
Kulasekararaj, Austin, Risitano, Antonio, Lee, Jong Wook, Huang, Mingjun, Nishimura, Jun-Ichi, Ramirez-Santiago, Alejandra, Brodsky, Robert
Published in Blood (05.11.2020)
Published in Blood (05.11.2020)
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Treatment Patterns and Costs of Transfusion and Chelation in Commercially-Insured and Medicaid Patients with Transfusion-Dependent β-Thalassemia
Paramore, Clark, Vlahiotis, Anna, Moynihan, Meghan, Cappell, Katherine, Ramirez-Santiago, Alejandra
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Long-term safety and efficacy of extended-interval prophylaxis with recombinant factor IX Fc fusion protein (rFIXFc) in subjects with haemophilia B
Pasi, K John, Fischer, Kathelijn, Ragni, Margaret, Nolan, Beatrice, Perry, David J, Kulkarni, Roshni, Ozelo, Margareth, Mahlangu, Johnny, Shapiro, Amy D, Baker, Ross I, Bennett, Carolyn M, Barnes, Christopher, Oldenburg, Johannes, Matsushita, Tadashi, Yuan, Huixing, Ramirez-Santiago, Alejandra, Pierce, Glenn F, Allen, Geoffrey, Mei, Baisong
Published in Thrombosis and haemostasis (2017)
Published in Thrombosis and haemostasis (2017)
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Long Term Safety and Efficacy of Recombinant Factor IX Fc Fusion Protein (rFIXFc) Prophylaxis in Children with Hemophilia B: Interim Results of the B-Yond Extension Study
Ducore, Jonathan M., Fischer, Kathelijn, Kulkarni, Roshni, Nolan, Beatrice, Bennett, Carolyn M., Perry, David J, Yuan, Huixing, Ramirez-Santiago, Alejandra, Ferrante, Francesca, Lethagen, Stefan
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article
Clinical Outcomes in Children with Hemophilia B Treated Long Term with rFIXFc: Interim Results of the B-YOND Extension Study
Kulkarni, Roshni, Nolan, Beatrice, Bennett, Carolyn M., Fischer, Kathelijn, Perry, David J, Barnes, Christopher, Yuan, Huixing, Ramirez-Santiago, Alejandra, Pierce, Glenn F, Mei, Baisong
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
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Journal Article
Clinical Outcomes in Adults/Adolescents with Hemophilia B Treated Long Term with Recombinant Factor IX Fc Fusion Protein (rFIXFc) Prophylaxis: Interim Results of the B-Yond Extension Study
Matsushita, Tadashi, Mahlangu, Johnny, Shapiro, Amy D, Pasi, K John, Ragni, Margaret V., Ozelo, Margareth C, Oldenburg, Johannes, Baker, Ross I, Yuan, Huixing, Ramirez-Santiago, Alejandra, Ferrante, Francesca, Lethagen, Stefan
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article
Extended-Interval Prophylaxis with rFIXFc in Adults and Adolescents with Hemophilia B: Interim Results of the B-YOND Extension Study
Mahlangu, Johnny, Shapiro, Amy D, Pasi, K John, Ragni, Margaret V, Ozelo, Margareth Castro, Oldenburg, Johannes, Matsushita, Tadashi, Baker, Ross I, Yuan, Huixing, Ramirez-Santiago, Alejandra, Pierce, Glenn F, Allen, Geoffrey, Mei, Baisong
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
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