hPSC-Derived Striatal Cells Generated Using a Scalable 3D Hydrogel Promote Recovery in a Huntington Disease Mouse Model
Adil, Maroof M., Gaj, Thomas, Rao, Antara T., Kulkarni, Rishikesh U., Fuentes, Christina M., Ramadoss, Gokul N., Ekman, Freja K., Miller, Evan W., Schaffer, David V.
Published in Stem cell reports (08.05.2018)
Published in Stem cell reports (08.05.2018)
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Allele-Specific Gene Editing Rescues Pathology in a Human Model of Charcot-Marie-Tooth Disease Type 2E
Feliciano, Carissa M, Wu, Kenneth, Watry, Hannah L, Marley, Chiara B E, Ramadoss, Gokul N, Ghanim, Hana Y, Liu, Angela Z, Zholudeva, Lyandysha V, McDevitt, Todd C, Saporta, Mario A, Conklin, Bruce R, Judge, Luke M
Published in Frontiers in cell and developmental biology (16.08.2021)
Published in Frontiers in cell and developmental biology (16.08.2021)
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Genome-wide programmable transcriptional memory by CRISPR-based epigenome editing
Nuñez, James K., Chen, Jin, Pommier, Greg C., Cogan, J. Zachery, Replogle, Joseph M., Adriaens, Carmen, Ramadoss, Gokul N., Shi, Quanming, Hung, King L., Samelson, Avi J., Pogson, Angela N., Kim, James Y.S., Chung, Amanda, Leonetti, Manuel D., Chang, Howard Y., Kampmann, Martin, Bernstein, Bradley E., Hovestadt, Volker, Gilbert, Luke A., Weissman, Jonathan S.
Published in Cell (29.04.2021)
Published in Cell (29.04.2021)
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SARS-CoV-2 infection of human iPSC-derived cardiac cells reflects cytopathic features in hearts of patients with COVID-19
Perez-Bermejo, Juan A, Kang, Serah, Rockwood, Sarah J, Simoneau, Camille R, Joy, David A, Silva, Ana C, Ramadoss, Gokul N, Flanigan, Will R, Fozouni, Parinaz, Li, Huihui, Chen, Pei-Yi, Nakamura, Ken, Whitman, Jeffrey D, Hanson, Paul J, McManus, Bruce M, Ott, Melanie, Conklin, Bruce R, McDevitt, Todd C
Published in Science Translational Medicine (21.04.2021)
Published in Science Translational Medicine (21.04.2021)
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BRD2 inhibition blocks SARS-CoV-2 infection by reducing transcription of the host cell receptor ACE2
Samelson, Avi J, Tran, Quang Dinh, Robinot, Rémy, Carrau, Lucia, Rezelj, Veronica V, Kain, Alice Mac, Chen, Merissa, Ramadoss, Gokul N, Guo, Xiaoyan, Lim, Shion A, Lui, Irene, Nuñez, James K, Rockwood, Sarah J, Wang, Jianhui, Liu, Na, Carlson-Stevermer, Jared, Oki, Jennifer, Maures, Travis, Holden, Kevin, Weissman, Jonathan S, Wells, James A, Conklin, Bruce R, TenOever, Benjamin R, Chakrabarti, Lisa A, Vignuzzi, Marco, Tian, Ruilin, Kampmann, Martin
Published in Nature cell biology (01.01.2022)
Published in Nature cell biology (01.01.2022)
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Dopaminergic Neurons Transplanted Using Cell‐Instructive Biomaterials Alleviate Parkinsonism in Rodents
Adil, Maroof M., Rao, Antara T., Ramadoss, Gokul N., Chernavsky, Nicole E., Kulkarni, Rishikesh U., Miller, Evan W., Kumar, Sanjay, Schaffer, David V.
Published in Advanced functional materials (10.10.2018)
Published in Advanced functional materials (10.10.2018)
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BRD2 inhibition blocks SARS-CoV-2 infection by reducing transcription of the host cell receptor ACE2
Samelson, Avi J, Tran, Quang Dinh, Robinot, Rémy, Carrau, Lucia, Rezelj, Veronica V, Mac Kain, Alice, Chen, Merissa, Ramadoss, Gokul N, Guo, Xiaoyan, Lim, Shion A, Lui, Irene, Nunez, James, Rockwood, Sarah J, Wang, Jianhui, Liu, Na, Carlson-Stevermer, Jared, Oki, Jennifer, Maures, Travis, Holden, Kevin, Weissman, Jonathan S, Wells, James A, Conklin, Bruce R, TenOever, Benjamin R, Chakrabarti, Lisa A, Vignuzzi, Marco, Tian, Ruilin, Kampmann, Martin
Published in bioRxiv (20.09.2021)
Published in bioRxiv (20.09.2021)
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SARS-CoV-2 infection of human iPSC-derived cardiac cells predicts novel cytopathic features in hearts of COVID-19 patients
Pérez-Bermejo, Juan A, Kang, Serah, Rockwood, Sarah J, Simoneau, Camille R, Joy, David A, Ramadoss, Gokul N, Silva, Ana C, Flanigan, Will R, Li, Huihui, Nakamura, Ken, Whitman, Jeffrey D, Ott, Melanie, Conklin, Bruce R, McDevitt, Todd C
Published in bioRxiv (12.09.2020)
Published in bioRxiv (12.09.2020)
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Neuronal DNA repair reveals strategies to influence CRISPR editing outcomes
Ramadoss, Gokul N, Namaganda, Samali J, Hamilton, Jennifer R, Sharma, Rohit, Chow, Karena G, Macklin, Bria L, Sun, Mengyuan, Liu, Jia-Cheng, Fellmann, Christof, Watry, Hannah L, Jin, Julianne, Perez, Barbara S, Sandoval Espinoza, Cindy R, Matia, Madeline P, Lu, Serena H, Judge, Luke M, Nussenzweig, Andre, Adamson, Britt, Murthy, Niren, Doudna, Jennifer A, Kampmann, Martin, Conklin, Bruce R
Published in bioRxiv (26.06.2024)
Published in bioRxiv (26.06.2024)
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