Preclinical Enzyme Replacement Therapy with a Recombinant β-Galactosidase-Lectin Fusion for CNS Delivery and Treatment of GM1-Gangliosidosis
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Published in Cells (Basel, Switzerland) (01.08.2022)
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Quality assessment of recombinant proteins produced in plants
Medrano, Giuliana, Dolan, Maureen C, Condori, Jose, Radin, David N, Cramer, Carole L
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Published in Methods in molecular biology (Clifton, N.J.) (01.01.2012)
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High-throughput imaging method for direct assessment of GM1 ganglioside levels in mammalian cells
Acosta, Walter, Martin, Reid, Radin, David N., Cramer, Carole L.
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Published in Data in brief (01.03.2016)
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Enzyme replacement for GM1-gangliosidosis: Uptake, lysosomal activation, and cellular disease correction using a novel β-galactosidase:RTB lectin fusion
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Published in Molecular genetics and metabolism (01.02.2016)
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Novel bioproduction and delivery strategies for MPS IIIA enzyme replacement therapeutics
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Published in Molecular genetics and metabolism (01.02.2016)
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Enzyme replacement therapy with α-L-iduronidase and lectin RTB fusion protein in treating murine Hurler syndrome
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Published in Molecular genetics and metabolism (01.02.2016)
Published in Molecular genetics and metabolism (01.02.2016)
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Uptake, lysosomal activation, and disease correction in GM1 Gangliosidosis cells by plant-made β-galactosidase: Lectin fusions
Ayala, Jorge, Acosta, Walter, Condori, Jose, Annunziata, Ida, Katta, Varun, Flory, Ashley, Martin, Reid, Radin, Jonathan, Cramer, Carole L., d'Azzo, Alessandra, Radin, David N.
Published in Molecular genetics and metabolism (01.02.2016)
Published in Molecular genetics and metabolism (01.02.2016)
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Lectin-mediated delivery of α-L-iduronidase: A novel approach for MPS I enzyme replacement therapy
Acosta, Walter L., Ou, Li, Ayala, Jorge, Condori, Jose, Katta, Varun, Flory, Ashley, Martin, Reid, Radin, Jonathan, Whitley, Chester B., Cramer, Carole L., Radin, David N.
Published in Molecular genetics and metabolism (01.02.2016)
Published in Molecular genetics and metabolism (01.02.2016)
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