Generation and comparison of CRISPR-Cas9 and Cre-mediated genetically engineered mouse models of sarcoma
Huang, Jianguo, Chen, Mark, Whitley, Melodi Javid, Kuo, Hsuan-Cheng, Xu, Eric S., Walens, Andrea, Mowery, Yvonne M., Van Mater, David, Eward, William C., Cardona, Diana M., Luo, Lixia, Ma, Yan, Lopez, Omar M., Nelson, Christopher E., Robinson-Hamm, Jacqueline N., Reddy, Anupama, Dave, Sandeep S., Gersbach, Charles A., Dodd, Rebecca D., Kirsch, David G.
Published in Nature communications (10.07.2017)
Published in Nature communications (10.07.2017)
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Journal Article
Transgenic overexpression of ribonucleotide reductase improves cardiac performance
Nowakowski, Sarah G., Kolwicz, Stephen C., Korte, Frederick Steven, Luo, Zhaoxiong, Robinson-Hamm, Jacqueline N., Page, Jennifer L., Brozovich, Frank, Weiss, Robert S., Tian, Rong, Murry, Charles E., Regnier, Michael
Published in Proceedings of the National Academy of Sciences - PNAS (09.04.2013)
Published in Proceedings of the National Academy of Sciences - PNAS (09.04.2013)
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Journal Article
Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy
Nelson, Christopher E., Wu, Yaoying, Gemberling, Matthew P., Oliver, Matthew L., Waller, Matthew A., Bohning, Joel D., Robinson-Hamm, Jacqueline N., Bulaklak, Karen, Castellanos Rivera, Ruth M., Collier, Joel H., Asokan, Aravind, Gersbach, Charles A.
Published in Nature medicine (01.03.2019)
Published in Nature medicine (01.03.2019)
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Journal Article
Gene therapies that restore dystrophin expression for the treatment of Duchenne muscular dystrophy
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Journal Article
Book Review
Genome engineering: a new approach to gene therapy for neuromuscular disorders
Nelson, Christopher E., Robinson-Hamm, Jacqueline N., Gersbach, Charles A.
Published in Nature reviews. Neurology (01.11.2017)
Published in Nature reviews. Neurology (01.11.2017)
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Journal Article
Full-length dystrophin restoration via targeted exon integration by AAV-CRISPR in a humanized mouse model of Duchenne muscular dystrophy
Pickar-Oliver, Adrian, Gough, Veronica, Bohning, Joel D., Liu, Siyan, Robinson-Hamm, Jacqueline N., Daniels, Heather, Majoros, William H., Devlin, Garth, Asokan, Aravind, Gersbach, Charles A.
Published in Molecular therapy (03.11.2021)
Published in Molecular therapy (03.11.2021)
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Journal Article
317. Screening S. Aureus CRISPR-Cas9 Paired-Guide RNAs for Efficient Targeted Deletion in Duchenne Muscular Dystrophy
Tycko, Josh, Huston, Nick, Robinson-Hamm, Jacqueline N., Wilson, Chris, Gersbach, Charles A., Hsu, Patrick D., Bumcrot, David
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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Journal Article
504. Restoration of Dystrophin Expression by Gene Editing with S. aureus Cas9 in Models of Duchenne Muscular Dystrophy
Robinson-Hamm, Jacqueline N., Nelson, Christopher E., Rivera, Ruth M. Castellanos, Aartsma-Rus, Annemieke, Asokan, Aravind, Gersbach, Charles A.
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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Journal Article
Abstract A17: Generation and comparison of CRISPR/Cas9 and Cre-mediated genetically engineered mouse models of sarcoma
Huang, Jianguo, Chen, Mark, Whitley, Melodi Javid, Kuo, Hsuan-Cheng, Xu, Eric S., Walens, Andrea, Mowery, Yvonne M., Mater, David Van, Eward, William C., Cardona, Diana M., Luo, Lixia, Ma, Yan, Lopez, Omar M., Nelson, Christopher E., Robinson-Hamm, Jacqueline N., Reddy, Anupama, Dave, Sandeep S., Gersbach, Charles A., Dodd, Rebecca D., Kirsch, David G.
Published in Clinical cancer research (15.01.2018)
Published in Clinical cancer research (15.01.2018)
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Journal Article
Abstract 2810: Using CRISPR/Cas9 to generate primary soft tissue sarcoma in genetically engineered and wild-type mice
Huang, Jianguo, Chen, Mark, Whitley, Melodi J., Kuo, Hsuan-Cheng, Walens, Andrea, Mowery, Yvonne M., Mater, David V., Eward, William, Cardona, Diana M., Luo, Lixia, Ma, Yan, Nelson, Christopher E., Robinson-Hamm, Jacqueline N., Gersbach, Charles A., Dodd, Rebecca D., Kirsch, David G.
Published in Cancer research (Chicago, Ill.) (01.07.2017)
Published in Cancer research (Chicago, Ill.) (01.07.2017)
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Journal Article
397. Correction of the Dystrophin Gene By the CRISPR/Cas9 System in a Mouse Model of Muscular Dystrophy
Nelson, Christopher E., Moreb, David G. Ousterout, Jacqueline N. Robinson-Hamm, Eirik A., Castellanos, Ruth M., Ann Ran, Fei, Yan, Winston, Zhang, Feng, Asokan, Aravind, Gersbach, Charles A.
Published in Molecular therapy (01.05.2015)
Published in Molecular therapy (01.05.2015)
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Journal Article
Increased Fatigue Resistance of Skeletal Muscle with Elevated 2-Deoxy-ATP following Ribonucleotide Reductase Overexpression
Robinson-Hamm, Jacqueline N., Nowakowski, Sarah G., Siegel, Michael P., Faber, Rachel M., Weiss, Robert S., Banks, Glen B., Marcinek, David J., Regnier, Michael
Published in Biophysical journal (29.01.2013)
Published in Biophysical journal (29.01.2013)
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Journal Article
Broad Transgenic, and Cardiac-Specific Viral Mediated, Over-Expression of Ribonucleotide Reductase Increases In Vivo Cardiac Contractility
Korte, F. Steven, Odom, Guy L., Dai, Jin, Kolwicz, Stephen C., Robinson-Hamm, Jacqueline N., Tian, Rong, Hauschka, Stephen D., Chamberlain, Jeffrey S., Weiss, Robert S., Murry, Charles E., Regnier, Michael
Published in Biophysical journal (31.01.2012)
Published in Biophysical journal (31.01.2012)
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