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Natural history of liver disease in a large international cohort of children with Alagille syndrome: Results from the GALA study

by Vandriel, Shannon M, Li, Li-Ting, She, Huiyu, Wang, Jian-She, Gilbert, Melissa A, Jankowska, Irena, Czubkowski, Piotr, Gliwicz-Miedzińska, Dorota, Gonzales, Emmanuel M, Jacquemin, Emmanuel, Bouligand, Jérôme, Spinner, Nancy B, Loomes, Kathleen M, Piccoli, David A, D'Antiga, Lorenzo, Nicastro, Emanuele, Sokal, Étienne, Demaret, Tanguy, Ebel, Noelle H, Feinstein, Jeffrey A, Fawaz, Rima, Nastasio, Silvia, Lacaille, Florence, Debray, Dominique, Arnell, Henrik, Fischler, Björn, Siew, Susan, Stormon, Michael, Karpen, Saul J, Romero, Rene, Kim, Kyung Mo, Baek, Woo Yim, Hardikar, Winita, Shankar, Sahana, Roberts, Amin J, Evans, Helen M, Jensen, M Kyle, Kavan, Marianne, Sundaram, Shikha S, Chaidez, Alexander, Karthikeyan, Palaniswamy, Sanchez, Maria Camila, Cavalieri, Maria Lorena, Verkade, Henkjan J, Lee, Way Seah, Squires, James E, Hajinicolaou, Christina, Lertudomphonwanit, Chatmanee, Fischer, Ryan T, Larson-Nath, Catherine, Mozer-Glassberg, Yael, Arikan, Cigdem, Lin, Henry C, Bernabeu, Jesus Quintero, Alam, Seema, Kelly, Deirdre A, Carvalho, Elisa, Ferreira, Cristina Targa, Indolfi, Giuseppe, Quiros-Tejeira, Ruben E, Bulut, Pinar, Calvo, Pier Luigi, Önal, Zerrin, Valentino, Pamela L, Desai, Dev M, Eshun, John, Rogalidou, Maria, Dezsőfi, Antal, Wiecek, Sabina, Nebbia, Gabriella, Pinto, Raquel Borges, Wolters, Victorien M, Tamara, María Legarda, Zizzo, Andréanne N, Garcia, Jennifer, Schwarz, Kathleen, Beretta, Marisa, Sandahl, Thomas Damgaard, Jimenez-Rivera, Carolina, Kerkar, Nanda, Brecelj, Jernej, Mujawar, Quais, Rock, Nathalie, Busoms, Cristina Molera, Karnsakul, Wikrom, Lurz, Eberhard, Santos-Silva, Ermelinda, Blondet, Niviann, Bujanda, Luis, Shah, Uzma, Thompson, Richard J, Hansen, Bettina E, Kamath, Binita M
Published in Hepatology (Baltimore, Md.) (01.02.2023)

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Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA

by Hansen, Bettina E, Vandriel, Shannon M, Vig, Pamela, Garner, Will, Mogul, Douglas B, Loomes, Kathleen M, Piccoli, David A, Rand, Elizabeth B, Jankowska, Irena, Czubkowski, Piotr, Gliwicz-Miedzińska, Dorota, Gonzales, Emmanuel M, Jacquemin, Emmanuel, Bouligand, Jérôme, D'Antiga, Lorenzo, Nicastro, Emanuele, Arnell, Henrik, Fischler, Björn, Sokal, Étienne, Demaret, Tanguy, Siew, Susan, Stormon, Michael, Karpen, Saul J, Romero, Rene, Ebel, Noelle H, Feinstein, Jeffrey A, Roberts, Amin J, Evans, Helen M, Sundaram, Shikha S, Chaidez, Alexander, Hardikar, Winita, Shankar, Sahana, Fischer, Ryan T, Lacaille, Florence, Debray, Dominique, Lin, Henry C, Jensen, M Kyle, Jaramillo, Catalina, Karthikeyan, Palaniswamy, Indolfi, Giuseppe, Verkade, Henkjan J, Larson-Nath, Catherine, Quiros-Tejeira, Ruben E, Valentino, Pamela L, Rogalidou, Maria, Dezsőfi, Antal, Squires, James E, Schwarz, Kathleen, Calvo, Pier Luigi, Bernabeu, Jesus Quintero, Zizzo, Andréanne N, Nebbia, Gabriella, Bulut, Pinar, Santos-Silva, Ermelinda, Fawaz, Rima, Nastasio, Silvia, Karnsakul, Wikrom, Tamara, María Legarda, Busoms, Cristina Molera, Kelly, Deirdre A, Sandahl, Thomas Damgaard, Jimenez-Rivera, Carolina, Banales, Jesus M, Mujawar, Quais, Li, Li-Ting, She, Huiyu, Wang, Jian-She, Kim, Kyung Mo, Oh, Seak Hee, Sanchez, Maria Camila, Cavalieri, Maria Lorena, Lee, Way Seah, Hajinicolaou, Christina, Lertudomphonwanit, Chatmanee, Waisbourd-Zinman, Orith, Arikan, Cigdem, Alam, Seema, Carvalho, Elisa, Melere, Melina, Eshun, John, Önal, Zerrin, Desai, Dev M, Wiecek, Sabina, Pinto, Raquel Borges, Wolters, Victorien M, Garcia, Jennifer, Beretta, Marisa, Kerkar, Nanda, Brecelj, Jernej, Rock, Nathalie, Lurz, Eberhard, Blondet, Niviann, Shah, Uzma, Thompson, Richard J, Kamath, Binita M
Published in Hepatology (Baltimore, Md.) (01.06.2024)

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Serum bile acids are associated with native liver survival in patients with Alagille syndrome: results from the GALA study group

by Murillo Perez, Carla Fiorella, Vandriel, Shannon M., Wang, Jian-She, Liting, Li, She, Huiyu, Jankowska, Irena, Czubkowski, Piotr, Gliwicz, Dorota, Gonzalès, Emmanuel, Jacquemin, Emmanuel, Bouligand, Jérôme, D’Antiga, Lorenzo, Nicastro, Emanuele, Fischler, Björn, Arnell, Henrik, Siew, Susan, Stormon, Michael, Loomes, Kathleen M., Piccoli, David A., Rand, Elizabeth B., Squires, James E., Karpen, Saul J., Romero, Rene, Kasahara, Mureo, Önal, Zerrin, Sokal, Etienne, Demaret, Tanguy, Wiecek, Sabina, Lacaille, Florence, Debray, Dominique, Hardikar, Winita, Shankar, Sahana, Valentino, Pamela, Sundaram, Shikha, Chaidez, Alexander, Ebel, Noelle, Feinstein, Jeffrey, Mozar-Glazberg, Yael, Lin, Henry, Rock, Nathalie, Verkade, Henkjan J., Jensen, M.K., Jaramillo, Catalina, Kim, Kyungmo, Oh, Seak Hee, Brecelj, Jernej, Alam, Seema, Indolfi, Giuseppe, Blondet, Niviann, Fawaz, Rima, Nastasio, Silvia, Calvo, Pier Luigi, Nebbia, Gabriella, Arıkan, Cigdem, Larson-Nath, Catherine, Zizzo, Andréanne N., Sandahl, Thomas Damgaard, Tzivinikos, Christos, El-Koofy, Nehal, Elmonem, Mohamed, Desai, Dev, Karnsakul, Wikrom, Karthikeyan, Palaniswamy, Bulut, Pinar, Kerkar, Nanda, Wolters, Victorien, Roberts, Amin J, Evans, Helen, Sanchez, Maria Camila, Cavalieri, Maria Lorena, Kelly, Deirdre, Lee, Way Seah, Hajinicolaou, Christina, Lertudomphonwanit, Chatmanee, Fischer, Ryan, Bernabeu, Jesús Quintero, Quiros-Tejeira, Ruben E., Melere, Melina, Carvalho, Elisa, Eshun, John, Zellos, Aglaia, Dezsőfi, Antal, Pinto, Raquel Borges, Schwarz, Kathleen, Rogalidou, Maria, Garcia, Jennifer, Tamara, María Legarda, Beretta, Marisa, Mujawar, Quais, Santos-Silva, Ermelinda, Busoms, Cristina Molera, Lurz, Eberhard, Gonçalves, Cristina, Jimenez-Rivera, Carolina, Bañales, Jesús M., Shah, Uzma, Thompson, Richard, Hansen, Bettina, Kamath, Binita M.
Published in JOURNAL OF HEPATOLOGY (01.06.2023)

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