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Published in Journal of thrombosis and haemostasis (01.08.2015)
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Autophagy determines efficiency of liver‐directed gene therapy with adeno‐associated viral vectors
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Armour, S., Nordin, J., Costa Verdera, H., Cohen, D., Sellier, P., Crosariol, M., Collaud, F., Riling, C., Quinn, W., Hanby, H., Cagin, U., Puzzo, F., Haurigot, V., Ronzitti, G., Colella, P., Anguela, X., Mingozzi, F.
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TH.O.18 - Adeno associated vector-based gene therapy strategy for type 3 glycogen storage disease
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Published in Neuromuscular disorders : NMD (01.10.2017)
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Adeno associated vector-based gene therapy strategy for type 3 glycogen storage disease
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Published in Neuromuscular disorders : NMD (01.10.2017)
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Whole-body rescue of Pompe disease with AAV liver delivery of engineered secretable GAA transgenes
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Published in Neuromuscular disorders : NMD (01.10.2017)
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TH.O.17 - Whole-body rescue of Pompe disease with AAV liver delivery of engineered secretable GAA transgenes
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Published in Neuromuscular disorders : NMD (01.10.2017)
Published in Neuromuscular disorders : NMD (01.10.2017)
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Values in alcoholics
MACHOVER, S, PUZZO, F S, PLUMEAU, F E
Published in Quarterly journal of studies on alcohol (01.06.1962)
Published in Quarterly journal of studies on alcohol (01.06.1962)
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