Towards a combined therapy for spinal muscular atrophy based on opposing effects of an antisense oligonucleotide on chromatin and splicing
Marasco, Luciano E, Dujardin, Gwendal, Sousa-Luis, Rui, Liu, Ying Hsiu, Stigliano, Jose, Nomakuchi, Tomoki, Proudfoot, Nicholas R, Krainer, Adrian, Kornblihtt, Alberto R
Published in bioRxiv (24.09.2021)
Published in bioRxiv (24.09.2021)
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