Efficacy and Safety of Encaleret in Autosomal Dominant Hypocalcemia Type 1
Gafni, Rachel I., Hartley, Iris R., Roszko, Kelly L., Nemeth, Edward F., Pozo, Karen A., Lombardi, Ed, Sridhar, Ananth V., Roberts, Mary S., Fox, Jonathan C., Collins, Michael T.
Published in The New England journal of medicine (28.09.2023)
Published in The New England journal of medicine (28.09.2023)
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Endogenous endophthalmitis secondary to perirenal abscess
Lizana, Nemecio, Parrao, Diego, Larrañaga, Matías, Figueroa‐Vercellino, Juan P, Pozo, Karen, Bravo, Juan Cristóbal
Published in IJU case reports (01.09.2023)
Published in IJU case reports (01.09.2023)
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Infigratinib Reduces Fibroblast Growth Factor 23 (FGF23) and Increases Blood Phosphate in Tumor‐Induced Osteomalacia
Hartley, Iris R., Roszko, Kelly L., Li, Xiaobai, Pozo, Karen, Streit, Jamie, Rivero, Jaydira, Magone, M. Teresa, Smith, Michaele R., Vold, Roo, Dambkowski, Carl L., Collins, Michael T., Gafni, Rachel I.
Published in JBMR plus (01.08.2022)
Published in JBMR plus (01.08.2022)
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Encaleret Normalized Mineral Homeostasis in Autosomal Dominant Hypocalcemia Type 1 (ADH1) in a Phase 2 Study: FR-OR08
Roszko, Kelly, Gafni, Rachel, Hartley, Iris R., Nemeth, Edward F., Pozo, Karen A., Lombardi, Ed, Roberts, Mary S., Adler, Scott H., Collins, Michael
Published in Journal of the American Society of Nephrology (01.11.2022)
Published in Journal of the American Society of Nephrology (01.11.2022)
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Abstract 14476: Effects of Encaleret on Corrected QT Interval in Autosomal Dominant Hypocalcemia Type 1: Early Results From an Ongoing Phase 2b, Open-Label, Dose-Ranging Study
Hartley, Iris, Gafni, Rachel, Roszko, Kelly, Pozo, Karen, Collins, Michael T, Nemeth, Edward, Sani-Grosso, Ramei, Sridhar, Ananth, Stapleton, Lyndsay, Roberts, Mary Scott, Fox, Jonathan
Published in Circulation (New York, N.Y.) (16.11.2021)
Published in Circulation (New York, N.Y.) (16.11.2021)
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Magone, M. Teresa, Hartley, Iris R., FitzGibbon, Edmond, Bishop, Rachel, Arango, Mike, Moran, Susan, Vold, Roo, Rivero, Jaydira del, Pozo, Karen, Streit, Jamie, Roszko, Kelly L., Collins, Michael T., Gafni, Rachel I.
Published in Ophthalmology (Rochester, Minn.) (01.09.2021)
Published in Ophthalmology (Rochester, Minn.) (01.09.2021)
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Ocular Adverse Effects of Infigratinib, a New Fibroblast Growth Factor Receptor Tyrosine Kinase Inhibitor
Magone, M. Teresa, Hartley, Iris R., Fitzgibbon, Edmond, Bishop, Rachel, Arango, Mike, Moran, Susan, Vold, Roo, Rivero, Jaydira del, Pozo, Karen, Streit, Jamie, Roszko, Kelly L., Collins, Michael T., Gafni, Rachel I.
Published in Ophthalmology (Rochester, Minn.) (01.04.2021)
Published in Ophthalmology (Rochester, Minn.) (01.04.2021)
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OR23-03 Sustained Normalization Of Mineral Homeostasis In Autosomal Dominant Hypocalcemia Type 1: Results From A Phase 2 Study Over 18 Months Of Encaleret (CLTX-305) Treatment (NCT04581629)
Ilana Gafni, Rachel, Ruth Hartley, Iris, Lauter Roszko, Kelly, Nemeth, Edward F, Pozo, Karen A, Mathew, Arun, Scott Roberts, Mary, Adler, Scott H, Collins, Michael T
Published in Journal of the Endocrine Society (05.10.2023)
Published in Journal of the Endocrine Society (05.10.2023)
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OR21-2 Encaleret (CLTX-305) Restored Mineral Homeostasis in a Phase 2 Study in Autosomal Dominant Hypocalcemia Type 1 (ADH1)
Collins, Michael, Fox, Jonathan, Hartley, Iris, Mathew, Arun, Nemeth, Edward, Pozo, Karen, Roberts, Mary Scott, Roszko, Kelly, Sani-Grosso, Ramei, Sridhar, Ananth, Gafni, Rachel
Published in Journal of the Endocrine Society (01.11.2022)
Published in Journal of the Endocrine Society (01.11.2022)
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Effects of Encaleret (CLTX-305) on Mineral Physiology in Autosomal Dominant Hypocalcemia Type 1 Demonstrate Proof-of-Concept: Early Results from a Phase 2B, Open-Label, Dose-Ranging Study [NCT04581629]
Gafni, Rachel, Hartley, Iris, Roszko, Kelly, Nemeth, Edward, Pozo, Karen, Sani-Grosso, Ramei, Mathew, Arun, Sridhar, Ananth, Roberts, Mary Scott, Fox, Jonathan, Collins, Michael
Published in Bone Reports (01.05.2022)
Published in Bone Reports (01.05.2022)
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상염색체 우성 저칼슘혈증 타입 1(ADH1)의 치료를 위한 트리페닐 칼시라이틱 화합물
FOX JONATHAN, KOMEYLI ALI, COLLINS MICHAEL T, ROBERTS MARY SCOTT, POZO KAREN A, SANI GROSSO RAMEI, SRIDHAR ANANTH, HARTLEY IRIS R, GAFNI RACHEL I, ROSZKO KELLY B. L, BRUCE SIMON
Year of Publication 27.07.2023
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Year of Publication 27.07.2023
Patent
A Phase 2B, Open-Label, Dose-Ranging Study of Encaleret (CLTX-305) in Autosomal Dominant Hypocalcemia Type 1 (ADH1)
Gafni, Rachel Ilana, Hartley, Iris Ruth, Roszko, Kelly Lauter, Nemeth, Edward F, Pozo, Karen A, Sani-Grosso, Ramei, Sridhar, Ananth, Fox, Jonathan C, Collins, Michael T
Published in Journal of the Endocrine Society (03.05.2021)
Published in Journal of the Endocrine Society (03.05.2021)
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Magone, M Teresa, Hartley, Iris R, FitzGibbon, Edmond, Bishop, Rachel, Arango, Mike, Moran, Susan, Vold, Roo, Rivero, Jaydira Del, Pozo, Karen, Streit, Jamie, Roszko, Kelly L, Collins, Michael T, Gafni, Rachel I
Published in Ophthalmology (Rochester, Minn.) (01.09.2021)
Published in Ophthalmology (Rochester, Minn.) (01.09.2021)
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The Effects of Encaleret (CLTX-305) on Mineral Physiology in Autosomal Dominant Hypocalcemia Type 1 (ADH1) Demonstrate Proof-of-Concept: Early Results From an Ongoing Phase 2b, Open-Label, Dose-Ranging Study
Gafni, Rachel Ilana, Hartley, Iris Ruth, Roszko, Kelly Lauter, Nemeth, Edward F, Pozo, Karen A, Sani-Grosso, Ramei, Sridhar, Ananth, Kennedy, William D, Fox, Jonathan C, Collins, Michael T
Published in Journal of the Endocrine Society (03.05.2021)
Published in Journal of the Endocrine Society (03.05.2021)
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TRIPHENYL CALCILYTIC COMPOUNDS FOR THE TREATMENT OF AUTOSOMAL DOMINANT HYPOCALCEMIA TYPE 1 (ADH1)
BRUCE, Simon, FOX, Jonathan, ROSZKO, Kelly, SANI-GROSSO, Ramei, ROBERTS, Mary Scott, KOMEYLI, Ali, SRIDHAR, Ananth, HARTLEY, Iris, COLLINS, Michael, GAFNI, Rachel, POZO, Karen
Year of Publication 02.05.2024
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Year of Publication 02.05.2024
Patent
TRIPHENYL CALCILYTIC COMPOUNDS FOR THE TREATMENT OF AUTOSOMAL DOMINANT HYPOCALCEMIA TYPE 1 (ADH1)
BRUCE, Simon, FOX, Jonathan, ROSZKO, Kelly, SANI-GROSSO, Ramei, ROBERTS, Mary Scott, KOMEYLI, Ali, SRIDHAR, Ananth, HARTLEY, Iris, COLLINS, Michael, GAFNI, Rachel, POZO, Karen
Year of Publication 01.06.2023
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Year of Publication 01.06.2023
Patent
TRIPHENYL CALCILYTIC COMPOUNDS FOR THE TREATMENT OF AUTOSOMAL DOMINANT HYPOCALCEMIA TYPE 1 (ADH1)
BRUCE, Simon, HARTLEY, Iris, R, FOX, Jonathan, SANI-GROSSO, Ramei, ROBERTS, Mary Scott, KOMEYLI, Ali, SRIDHAR, Ananth, COLLINS, Michael, T, GAFNI, Rachel, I, POZO, Karen, A, ROSZKO, Kelly, B. L
Year of Publication 26.07.2023
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Year of Publication 26.07.2023
Patent