A Small Molecule Screen in Stem-Cell-Derived Motor Neurons Identifies a Kinase Inhibitor as a Candidate Therapeutic for ALS
Yang, Yin M., Gupta, Shailesh K., Kim, Kevin J., Powers, Berit E., Cerqueira, Antonio, Wainger, Brian J., Ngo, Hien D., Rosowski, Kathryn A., Schein, Pamela A., Ackeifi, Courtney A., Arvanites, Anthony C., Davidow, Lance S., Woolf, Clifford J., Rubin, Lee L.
Published in Cell stem cell (06.06.2013)
Published in Cell stem cell (06.06.2013)
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Journal Article
The atlas of RNase H antisense oligonucleotide distribution and activity in the CNS of rodents and non-human primates following central administration
Jafar-nejad, Paymaan, Powers, Berit, Soriano, Armand, Zhao, Hien, Norris, Daniel A, Matson, John, DeBrosse-Serra, Beatrice, Watson, Jamie, Narayanan, Padmakumar, Chun, Seung J, Mazur, Curt, Kordasiewicz, Holly, Swayze, Eric E, Rigo, Frank
Published in Nucleic acids research (25.01.2021)
Published in Nucleic acids research (25.01.2021)
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Journal Article
Antisense suppression of glial fibrillary acidic protein as a treatment for Alexander disease
Hagemann, Tracy L., Powers, Berit, Mazur, Curt, Kim, Aneeza, Wheeler, Steven, Hung, Gene, Swayze, Eric, Messing, Albee
Published in Annals of neurology (01.01.2018)
Published in Annals of neurology (01.01.2018)
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Journal Article
Remyelination reporter reveals prolonged refinement of spontaneously regenerated myelin
Powers, Berit E., Sellers, Drew L., Lovelett, Emilie A., Cheung, Willy, Aalami, Sheida P., Zapertov, Nikolai, Maris, Don O., Horner, Philip J.
Published in Proceedings of the National Academy of Sciences - PNAS (05.03.2013)
Published in Proceedings of the National Academy of Sciences - PNAS (05.03.2013)
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Journal Article
Suppression of proteolipid protein rescues Pelizaeus-Merzbacher disease
Elitt, Matthew S, Barbar, Lilianne, Shick, H Elizabeth, Powers, Berit E, Maeno-Hikichi, Yuka, Madhavan, Mayur, Allan, Kevin C, Nawash, Baraa S, Gevorgyan, Artur S, Hung, Stevephen, Nevin, Zachary S, Olsen, Hannah E, Hitomi, Midori, Schlatzer, Daniela M, Zhao, Hien T, Swayze, Adam, LePage, David F, Jiang, Weihong, Conlon, Ronald A, Rigo, Frank, Tesar, Paul J
Published in Nature (London) (17.09.2020)
Published in Nature (London) (17.09.2020)
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Journal Article
Neural deficits in a mouse model of PACS1 syndrome are corrected with PACS1- or HDAC6-targeting therapy
Villar-Pazos, Sabrina, Thomas, Laurel, Yang, Yunhan, Chen, Kun, Lyles, Jenea B, Deitch, Bradley J, Ochaba, Joseph, Ling, Karen, Powers, Berit, Gingras, Sebastien, Kordasiewicz, Holly B, Grubisha, Melanie J, Huang, Yanhua H, Thomas, Gary
Published in Nature communications (17.10.2023)
Published in Nature communications (17.10.2023)
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Journal Article
Axonal thinning and extensive remyelination without chronic demyelination in spinal injured rats
Powers, Berit E, Lasiene, Jurate, Plemel, Jason R, Shupe, Larry, Perlmutter, Steve I, Tetzlaff, Wolfram, Horner, Philip J
Published in The Journal of neuroscience (11.04.2012)
Published in The Journal of neuroscience (11.04.2012)
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Journal Article
Convective forces increase rostral delivery of intrathecal radiotracers and antisense oligonucleotides in the cynomolgus monkey nervous system
Sullivan, Jenna M, Mazur, Curt, Wolf, Daniel A, Horky, Laura, Currier, Nicolas, Fitzsimmons, Bethany, Hesterman, Jacob, Pauplis, Rachel, Haller, Scott, Powers, Berit, Tayefeh, Leighla, DeBrosse-Serra, Bea, Hoppin, Jack, Kordasiewicz, Holly, Swayze, Eric E, Verma, Ajay
Published in Journal of translational medicine (08.08.2020)
Published in Journal of translational medicine (08.08.2020)
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Journal Article
Neuregulin 1 confers neuroprotection in SOD1-linked amyotrophic lateral sclerosis mice via restoration of C-boutons of spinal motor neurons
Lasiene, Jurate, Komine, Okiru, Fujimori-Tonou, Noriko, Powers, Berit, Endo, Fumito, Watanabe, Seiji, Shijie, Jin, Ravits, John, Horner, Philip, Misawa, Hidemi, Yamanaka, Koji
Published in Acta neuropathologica communications (18.02.2016)
Published in Acta neuropathologica communications (18.02.2016)
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Journal Article
Cholesterol-functionalized DNA/RNA heteroduplexes cross the blood-brain barrier and knock down genes in the rodent CNS
Nagata, Tetsuya, Dwyer, Chrissa A, Yoshida-Tanaka, Kie, Ihara, Kensuke, Ohyagi, Masaki, Kaburagi, Hidetoshi, Miyata, Haruka, Ebihara, Satoe, Yoshioka, Kotaro, Ishii, Takashi, Miyata, Kanjiro, Miyata, Kenichi, Powers, Berit, Igari, Tomoko, Yamamoto, Syunsuke, Arimura, Naoto, Hirabayashi, Hideki, Uchihara, Toshiki, Hara, Rintaro Iwata, Wada, Takeshi, Bennett, C Frank, Seth, Punit P, Rigo, Frank, Yokota, Takanori
Published in Nature biotechnology (01.12.2021)
Published in Nature biotechnology (01.12.2021)
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Journal Article
Antisense therapy in a rat model of Alexander disease reverses GFAP pathology, white matter deficits, and motor impairment
Hagemann, Tracy L, Powers, Berit, Lin, Ni-Hsuan, Mohamed, Ahmed F, Dague, Katerina L, Hannah, Seth C, Bachmann, Gemma, Mazur, Curt, Rigo, Frank, Olsen, Abby L, Feany, Mel B, Perng, Ming-Der, Berman, Robert F, Messing, Albee
Published in Science translational medicine (17.11.2021)
Published in Science translational medicine (17.11.2021)
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Journal Article
Time-dependent, bidirectional, anti- and pro-spinal hyper-reflexia and muscle spasticity effect after chronic spinal glycine transporter 2 (GlyT2) oligonucleotide-induced downregulation
Kamizato, Kota, Marsala, Silvia, Navarro, Michael, Kakinohana, Manabu, Platoshyn, Oleksandr, Yoshizumi, Tetsuya, Lukacova, Nadezda, Wancewicz, Ed, Powers, Berit, Mazur, Curt, Marsala, Martin
Published in Experimental neurology (01.07.2018)
Published in Experimental neurology (01.07.2018)
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Journal Article
Brain pharmacology of intrathecal antisense oligonucleotides revealed through multimodal imaging
Mazur, Curt, Powers, Berit, Zasadny, Kenneth, Sullivan, Jenna M., Dimant, Hemi, Kamme, Fredrik, Hesterman, Jacob, Matson, John, Oestergaard, Michael, Seaman, Marc, Holt, Robert W., Qutaish, Mohammed, Polyak, Ildiko, Coelho, Richard, Gottumukkala, Vijay, Gaut, Carolynn M., Berridge, Marc, Albargothy, Nazira J., Kelly, Louise, Carare, Roxana O., Hoppin, Jack, Kordasiewicz, Holly, Swayze, Eric E., Verma, Ajay
Published in JCI insight (17.10.2019)
Published in JCI insight (17.10.2019)
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