Navigating the orphan medicinal product designation: Evidence requirements for gene therapies in Europe
Palomo, G.M., Pose-Boirazian, T., Naumann-Winter, F., Costa, E., Duarte, D.M., Kalland, M.E., Malikova, E., Matusevicius, D., Vitezic, D., Larsson, K., Magrelli, A., Stoyanova-Beninska, V., Mariz, S.
Published in Molecular therapy (25.10.2024)
Published in Molecular therapy (25.10.2024)
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