Burosumab Therapy in Children with X-Linked Hypophosphatemia
Carpenter, Thomas O, Whyte, Michael P, Imel, Erik A, Boot, Annemieke M, Högler, Wolfgang, Linglart, Agnès, Padidela, Raja, van’t Hoff, William, Mao, Meng, Chen, Chao-Yin, Skrinar, Alison, Kakkis, Emil, San Martin, Javier, Portale, Anthony A
Published in The New England journal of medicine (24.05.2018)
Published in The New England journal of medicine (24.05.2018)
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Journal Article
Burosumab Therapy for X-Linked Hypophosphatemia and Therapeutic Implications for CKD
Perwad, Farzana, Portale, Anthony A
Published in Clinical journal of the American Society of Nephrology (05.07.2019)
Published in Clinical journal of the American Society of Nephrology (05.07.2019)
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Journal Article
Burosumab Improved Histomorphometric Measures of Osteomalacia in Adults with X‐Linked Hypophosphatemia: A Phase 3, Single‐Arm, International Trial
Insogna, Karl L, Rauch, Frank, Kamenický, Peter, Ito, Nobuaki, Kubota, Takuo, Nakamura, Akie, Zhang, Lin, Mealiffe, Matt, San Martin, Javier, Portale, Anthony A
Published in Journal of bone and mineral research (01.12.2019)
Published in Journal of bone and mineral research (01.12.2019)
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Journal Article
Waist-to-height ratio, body mass index, and cardiovascular risk profile in children with chronic kidney disease
Sgambat, Kristen, Roem, Jennifer, Mitsnefes, Mark, Portale, Anthony A., Furth, Susan, Warady, Bradley, Moudgil, Asha
Published in Pediatric nephrology (Berlin, West) (01.09.2018)
Published in Pediatric nephrology (Berlin, West) (01.09.2018)
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A Randomized, Double‐Blind, Placebo‐Controlled, Phase 3 Trial Evaluating the Efficacy of Burosumab, an Anti‐FGF23 Antibody, in Adults With X‐Linked Hypophosphatemia: Week 24 Primary Analysis
Insogna, Karl L, Briot, Karine, Imel, Erik A, Kamenický, Peter, Ruppe, Mary D, Portale, Anthony A, Weber, Thomas, Pitukcheewanont, Pisit, Cheong, Hae Il, Jan de Beur, Suzanne, Imanishi, Yasuo, Ito, Nobuaki, Lachmann, Robin H, Tanaka, Hiroyuki, Perwad, Farzana, Zhang, Lin, Chen, Chao‐Yin, Theodore‐Oklota, Christina, Mealiffe, Matt, San Martin, Javier, Carpenter, Thomas O
Published in Journal of bone and mineral research (01.08.2018)
Published in Journal of bone and mineral research (01.08.2018)
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Journal Article
Burosumab versus conventional therapy in children with X-linked hypophosphataemia: a randomised, active-controlled, open-label, phase 3 trial
Imel, Erik A, Glorieux, Francis H, Whyte, Michael P, Munns, Craig F, Ward, Leanne M, Nilsson, Ola, Simmons, Jill H, Padidela, Raja, Namba, Noriyuki, Cheong, Hae Il, Pitukcheewanont, Pisit, Sochett, Etienne, Högler, Wolfgang, Muroya, Koji, Tanaka, Hiroyuki, Gottesman, Gary S, Biggin, Andrew, Perwad, Farzana, Mao, Meng, Chen, Chao-Yin, Skrinar, Alison, San Martin, Javier, Portale, Anthony A
Published in The Lancet (British edition) (15.06.2019)
Published in The Lancet (British edition) (15.06.2019)
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Journal Article
Sustained Efficacy and Safety of Burosumab, a Monoclonal Antibody to FGF23, in Children With X-Linked Hypophosphatemia
Linglart, Agnès, Imel, Erik A, Whyte, Michael P, Portale, Anthony A, Högler, Wolfgang, Boot, Annemieke M, Padidela, Raja, Van't Hoff, William, Gottesman, Gary S, Chen, Angel, Skrinar, Alison, Scott Roberts, Mary, Carpenter, Thomas O
Published in The journal of clinical endocrinology and metabolism (17.02.2022)
Published in The journal of clinical endocrinology and metabolism (17.02.2022)
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Journal Article
Characterization of FGF23-Dependent Egr-1 Cistrome in the Mouse Renal Proximal Tubule
Portale, Anthony A, Zhang, Martin Y H, David, Valentin, Martin, Aline, Jiao, Yan, Gu, Weikuan, Perwad, Farzana
Published in PloS one (20.11.2015)
Published in PloS one (20.11.2015)
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Journal Article
FGF-23 regulates CYP27B1 transcription in the kidney and in extra-renal tissues
Chanakul, Ankanee, Zhang, Martin Y H, Louw, Andrew, Armbrecht, Harvey J, Miller, Walter L, Portale, Anthony A, Perwad, Farzana
Published in PloS one (03.09.2013)
Published in PloS one (03.09.2013)
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Journal Article
Fibroblast Growth Factor 23 and Risk of CKD Progression in Children
Portale, Anthony A, Wolf, Myles S, Messinger, Shari, Perwad, Farzana, Jüppner, Harald, Warady, Bradley A, Furth, Susan L, Salusky, Isidro B
Published in Clinical journal of the American Society of Nephrology (07.11.2016)
Published in Clinical journal of the American Society of Nephrology (07.11.2016)
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Journal Article
Prolonged Correction of Serum Phosphorus in Adults With X-Linked Hypophosphatemia Using Monthly Doses of KRN23
Imel, Erik A, Zhang, Xiaoping, Ruppe, Mary D, Weber, Thomas J, Klausner, Mark A, Ito, Takahiro, Vergeire, Maria, Humphrey, Jeffrey S, Glorieux, Francis H, Portale, Anthony A, Insogna, Karl, Peacock, Munro, Carpenter, Thomas O
Published in The journal of clinical endocrinology and metabolism (01.07.2015)
Published in The journal of clinical endocrinology and metabolism (01.07.2015)
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Journal Article
Continued Beneficial Effects of Burosumab in Adults with X-Linked Hypophosphatemia: Results from a 24-Week Treatment Continuation Period After a 24-Week Double-Blind Placebo-Controlled Period
Portale, Anthony A., Carpenter, Thomas O., Brandi, Maria Luisa, Briot, Karine, Cheong, Hae II, Cohen-Solal, Martine, Crowley, Rachel, Jan De Beur, Suzanne, Eastell, Richard, Imanishi, Yasuo, Imel, Erik A., Ing, Steven, Ito, Nobuaki, Javaid, Muhammad, Kamenicky, Peter, Keen, Richard, Kubota, Takuo, Lachmann, Robin, Perwad, Farzana, Pitukcheewanont, Pisit, Ralston, Stuart H., Takeuchi, Yasuhiro, Tanaka, Hiroyuki, Weber, Thomas J., Yoo, Han-Wook, Zhang, Lin, Theodore-Oklota, Christina, Mealiffe, Matt, San Martin, Javier, Insogna, Karl
Published in Calcified tissue international (01.09.2019)
Published in Calcified tissue international (01.09.2019)
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Journal Article
Disordered FGF23 and Mineral Metabolism in Children with CKD
Portale, Anthony A, Wolf, Myles, Jüppner, Harald, Messinger, Shari, Kumar, Juhi, Wesseling-Perry, Katherine, Schwartz, George J, Furth, Susan L, Warady, Bradley A, Salusky, Isidro B
Published in Clinical journal of the American Society of Nephrology (01.02.2014)
Published in Clinical journal of the American Society of Nephrology (01.02.2014)
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Journal Article
Fracture Burden and Risk Factors in Childhood CKD: Results from the CKiD Cohort Study
Denburg, Michelle R, Kumar, Juhi, Jemielita, Thomas, Brooks, Ellen R, Skversky, Amy, Portale, Anthony A, Salusky, Isidro B, Warady, Bradley A, Furth, Susan L, Leonard, Mary B
Published in Journal of the American Society of Nephrology (01.02.2016)
Published in Journal of the American Society of Nephrology (01.02.2016)
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Journal Article
FGF23 and Left Ventricular Hypertrophy in Children with CKD
Mitsnefes, Mark M, Betoko, Aisha, Schneider, Michael F, Salusky, Isidro B, Wolf, Myles Selig, Jüppner, Harald, Warady, Bradley A, Furth, Susan L, Portale, Anthony A
Published in Clinical journal of the American Society of Nephrology (06.01.2018)
Published in Clinical journal of the American Society of Nephrology (06.01.2018)
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Journal Article
Rickets
Carpenter, Thomas O, Shaw, Nick J, Portale, Anthony A, Ward, Leanne M, Abrams, Steven A, Pettifor, John M
Published in Nature reviews. Disease primers (21.12.2017)
Published in Nature reviews. Disease primers (21.12.2017)
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Journal Article
Effect of Burosumab Compared With Conventional Therapy on Younger vs Older Children With X-linked Hypophosphatemia
Ward, Leanne M, Glorieux, Francis H, Whyte, Michael P, Munns, Craig F, Portale, Anthony A, Hogler, Wolfgang, Simmons, Jill H, Gottesman, Gary S, Padidela, Raja, Namba, Noriyuki, Cheong, Hae Il, Nilsson, Ola, Mao, Meng, Chen, Angel, Skrinar, Alison, Roberts, Mary Scott, Imel, Erik A
Published in The journal of clinical endocrinology and metabolism (01.08.2022)
Published in The journal of clinical endocrinology and metabolism (01.08.2022)
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Journal Article