Neurologic Recovery in MPS I and MPS II Mice by AAV9-Mediated Gene Transfer to the CNS After the Development of Cognitive Dysfunction
Podetz-Pedersen, Kelly M, Laoharawee, Kanut, Singh, Sajya, Nguyen, Tam T, Smith, Miles C, Temme, Alexa, Kozarsky, Karen, McIvor, R Scott, Belur, Lalitha R
Published in Human gene therapy (01.01.2023)
Published in Human gene therapy (01.01.2023)
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Identification of rtl1, a retrotransposon-derived imprinted gene, as a novel driver of hepatocarcinogenesis
Riordan, Jesse D, Keng, Vincent W, Tschida, Barbara R, Scheetz, Todd E, Bell, Jason B, Podetz-Pedersen, Kelly M, Moser, Catherine D, Copeland, Neal G, Jenkins, Nancy A, Roberts, Lewis R, Largaespada, David A, Dupuy, Adam J
Published in PLoS genetics (01.04.2013)
Published in PLoS genetics (01.04.2013)
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Differential Adeno-Associated Virus Mediated Gene Transfer to Sensory Neurons following Intrathecal Delivery by Direct Lumbar Puncture
Vulchanova, Lucy, Schuster, Daniel J, Belur, Lalitha R, Riedl, Maureen S, Podetz-Pedersen, Kelly M, Kitto, Kelley F, Wilcox, George L, McIvor, R Scott, Fairbanks, Carolyn A
Published in Molecular pain (28.05.2010)
Published in Molecular pain (28.05.2010)
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Intranasal Adeno-Associated Virus Mediated Gene Delivery and Expression of Human Iduronidase in the Central Nervous System: A Noninvasive and Effective Approach for Prevention of Neurologic Disease in Mucopolysaccharidosis Type I
Belur, Lalitha R, Temme, Alexa, Podetz-Pedersen, Kelly M, Riedl, Maureen, Vulchanova, Lucy, Robinson, Nicholas, Hanson, Leah R, Kozarsky, Karen F, Orchard, Paul J, Frey, 2nd, William H, Low, Walter C, McIvor, R Scott
Published in Human gene therapy (01.07.2017)
Published in Human gene therapy (01.07.2017)
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Prevention of Neurocognitive Deficiency in Mucopolysaccharidosis Type II Mice by Central Nervous System-Directed, AAV9-Mediated Iduronate Sulfatase Gene Transfer
Laoharawee, Kanut, Podetz-Pedersen, Kelly M, Nguyen, Tam T, Evenstar, Laura B, Kitto, Kelley F, Nan, Zhenhong, Fairbanks, Carolyn A, Low, Walter C, Kozarsky, Karen F, McIvor, R Scott
Published in Human gene therapy (01.08.2017)
Published in Human gene therapy (01.08.2017)
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Journal Article
Comparative Effectiveness of Intracerebroventricular, Intrathecal, and Intranasal Routes of AAV9 Vector Administration for Genetic Therapy of Neurologic Disease in Murine Mucopolysaccharidosis Type I
Belur, Lalitha R, Romero, Megan, Lee, Junggu, Podetz-Pedersen, Kelly M, Nan, Zhenhong, Riedl, Maureen S, Vulchanova, Lucy, Kitto, Kelley F, Fairbanks, Carolyn A, Kozarsky, Karen F, Orchard, Paul J, Frey, 2nd, William H, Low, Walter C, McIvor, R Scott
Published in Frontiers in molecular neuroscience (10.05.2021)
Published in Frontiers in molecular neuroscience (10.05.2021)
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Journal Article
Inhibition of angiogenesis and suppression of colorectal cancer metastatic to the liver using the Sleeping Beauty Transposon System
Belur, Lalitha R, Podetz-Pedersen, Kelly M, Sorenson, Brent S, Hsu, Alice H, Parker, Josh B, Carlson, Cathy S, Saltzman, Daniel A, Ramakrishnan, S, McIvor, R Scott
Published in Molecular cancer (10.02.2011)
Published in Molecular cancer (10.02.2011)
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Journal Article
Non-invasive intravenous administration of AAV9 transducing iduronate sulfatase leads to global metabolic correction and prevention of neurologic deficits in a mouse model of Hunter syndrome
Laoharawee, Kanut, Podetz-Pedersen, Kelly M., Nguyen, Tam T., Singh, Sajya M., Smith, Miles C., Belur, Lalitha R., Low, Walter C., Kozarsky, Karen F., McIvor, R. Scott
Published in Molecular genetics and metabolism reports (01.03.2023)
Published in Molecular genetics and metabolism reports (01.03.2023)
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Journal Article
Dose-Dependent Prevention of Metabolic and Neurologic Disease in Murine MPS II by ZFN-Mediated In Vivo Genome Editing
Laoharawee, Kanut, DeKelver, Russell C., Podetz-Pedersen, Kelly M., Rohde, Michelle, Sproul, Scott, Nguyen, Hoang-Oanh, Nguyen, Tam, St. Martin, Susan J., Ou, Li, Tom, Susan, Radeke, Robert, Meyer, Kathleen E., Holmes, Michael C., Whitley, Chester B., Wechsler, Thomas, McIvor, R. Scott
Published in Molecular therapy (04.04.2018)
Published in Molecular therapy (04.04.2018)
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Journal Article
Phenotypic Correction of Murine Mucopolysaccharidosis Type II by Engraftment of Ex Vivo Lentiviral Vector-Transduced Hematopoietic Stem and Progenitor Cells
Smith, Miles C, Belur, Lalitha R, Karlen, Andrea D, Erlanson, Olivia, Podetz-Pedersen, Kelly M, McKenzie, Jessica, Detellis, Jenn, Gagnidze, Khatuna, Parsons, Geoffrey, Robinson, Nicholas, Labarre, Shelby, Shah, Saumil, Furcich, Justin, Lund, Troy C, Tsai, Hsing-Chen, McIvor, R Scott, Bonner, Melissa
Published in Human gene therapy (01.12.2022)
Published in Human gene therapy (01.12.2022)
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A Broad Range of Dose Optima Achieve High-level, Long-term Gene Expression After Hydrodynamic Delivery of Sleeping Beauty Transposons Using Hyperactive SB100x Transposase
Podetz-Pedersen, Kelly M, Olson, Erik R, Somia, Nikunj V, Russell, Stephen J, McIvor, R Scott
Published in Molecular therapy. Nucleic acids (2016)
Published in Molecular therapy. Nucleic acids (2016)
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Journal Article
Intravenous delivery for treatment of mucopolysaccharidosis type I: A comparison of AAV serotypes 9 and rh10
Belur, Lalitha R., Podetz-Pedersen, Kelly M., Tran, Thuy An, Mesick, Joshua A., Singh, Nathaniel M., Riedl, Maureen, Vulchanova, Lucy, Kozarsky, Karen F., McIvor, R. Scott
Published in Molecular genetics and metabolism reports (01.09.2020)
Published in Molecular genetics and metabolism reports (01.09.2020)
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Journal Article
Supraspinal gene transfer by intrathecal adeno-associated virus serotype 5
Schuster, Daniel J, Belur, Lalitha R, Riedl, Maureen S, Schnell, Stephen A, Podetz-Pedersen, Kelly M, Kitto, Kelley F, McIvor, R Scott, Vulchanova, Lucy, Fairbanks, Carolyn A
Published in Frontiers in neuroanatomy (05.08.2014)
Published in Frontiers in neuroanatomy (05.08.2014)
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Journal Article
ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome
Ou, Li, DeKelver, Russell C., Rohde, Michelle, Tom, Susan, Radeke, Robert, St. Martin, Susan J., Santiago, Yolanda, Sproul, Scott, Przybilla, Michelle J., Koniar, Brenda L., Podetz-Pedersen, Kelly M., Laoharawee, Kanut, Cooksley, Renee D., Meyer, Kathleen E., Holmes, Michael C., McIvor, R. Scott, Wechsler, Thomas, Whitley, Chester B.
Published in Molecular therapy (02.01.2019)
Published in Molecular therapy (02.01.2019)
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Journal Article
Role of transgene regulation in ex vivo lentiviral correction of artemis deficiency
Multhaup, Megan M, Podetz-Pedersen, Kelly M, Karlen, Andrea D, Olson, Erik R, Gunther, Roland, Somia, Nikunj V, Blazar, Bruce R, Cowan, Morton J, McIvor, R Scott
Published in Human gene therapy (01.04.2015)
Published in Human gene therapy (01.04.2015)
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Journal Article
Gene expression in lung and liver after intravenous infusion of polyethylenimine complexes of Sleeping Beauty transposons
Podetz-Pedersen, Kelly M, Bell, Jason B, Steele, Terry W J, Wilber, Andrew, Shier, W Thomas, Belur, Lalitha R, McIvor, R Scott, Hackett, Perry B
Published in Human gene therapy (01.02.2010)
Published in Human gene therapy (01.02.2010)
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Journal Article
Protection of Mice from Methotrexate Toxicity by ex Vivo Transduction Using Lentivirus Vectors Expressing Drug-Resistant Dihydrofolate Reductase
Gori, Jennifer L, Podetz-Pedersen, Kelly, Swanson, Debra, Karlen, Andrea D, Gunther, Roland, Somia, Nikunj V, McIvor, R Scott
Published in The Journal of pharmacology and experimental therapeutics (01.09.2007)
Published in The Journal of pharmacology and experimental therapeutics (01.09.2007)
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