High-throughput analysis of hematopoietic stem cell engraftment after intravenous and intracerebroventricular dosing
Plasschaert, Robert N., DeAndrade, Mark P., Hull, Fritz, Nguyen, Quoc, Peterson, Tara, Yan, Aimin, Loperfido, Mariana, Baricordi, Cristina, Barbarossa, Luigi, Yoon, John K., Dogan, Yildirim, Unnisa, Zeenath, Schindler, Jeffrey W., van Til, Niek P., Biasco, Luca, Mason, Chris
Published in Molecular therapy (05.10.2022)
Published in Molecular therapy (05.10.2022)
Get full text
Journal Article
Preclinical lentiviral hematopoietic stem cell gene therapy corrects Pompe disease-related muscle and neurological manifestations
Yoon, John K., Schindler, Jeffrey W., Loperfido, Mariana, Baricordi, Cristina, DeAndrade, Mark P., Jacobs, Mary E., Treleaven, Christopher, Plasschaert, Robert N., Yan, Aimin, Barese, Cecilia N., Dogan, Yildirim, Chen, Vicky Ping, Fiorini, Claudia, Hull, Fritz, Barbarossa, Luigi, Unnisa, Zeenath, Ivanov, Daniel, Kutner, Robert H., Guda, Swaroopa, Oborski, Christine, Maiwald, Tim, Michaud, Véronique, Rothe, Michael, Schambach, Axel, Pfeifer, Richard, Mason, Chris, Biasco, Luca, van Til, Niek P.
Published in Molecular therapy (17.09.2024)
Published in Molecular therapy (17.09.2024)
Get full text
Journal Article
CTCF binding site sequence differences are associated with unique regulatory and functional trends during embryonic stem cell differentiation
Plasschaert, Robert N, Vigneau, Sébastien, Tempera, Italo, Gupta, Ravi, Maksimoska, Jasna, Everett, Logan, Davuluri, Ramana, Mamorstein, Ronen, Lieberman, Paul M, Schultz, David, Hannenhalli, Sridhar, Bartolomei, Marisa S
Published in Nucleic acids research (01.01.2014)
Published in Nucleic acids research (01.01.2014)
Get full text
Journal Article
CTCF binding site sequence differences are associated with unique regulatory and functional trends during embryonic stem cell differentiation
Plasschaert, R. N., Vigneau, S., Tempera, I., Gupta, R., Maksimoska, J., Everett, L., Davuluri, R., Marmorstein, R., Lieberman, P. M., Schultz, D., Hannenhalli, S., Bartolomei, M. S.
Published in Nucleic acids research (17.06.2014)
Published in Nucleic acids research (17.06.2014)
Get full text
Journal Article
Preclinical lentiviral vector-mediated hematopoietic stem and progenitor cell gene therapy corrects Pompe disease-related muscle and neurological manifestations
Yoon, John K, Schindler, Jeffrey W, Loperfido, Mariana, Baricordi, Cristina, DeAndrade, Mark P, Jacobs, Mary E, Treleaven, Christopher, Plasschaert, Robert N, Yan, Aimin, Barese, Cecilia N, Dogan, Yildirim, Chen, Vicky Ping, Fiorini, Claudia, Hull, Fritz, Barbarossa, Luigi, Unnisa, Zeenath, Ivanov, Daniel, Kutner, Robert H, Guda, Swaroopa, Oborski, Christine, Maiwald, Tim, Michaud, Véronique, Rothe, Michael, Schambach, Axel, Pfeifer, Richard, Mason, Chris, Biasco, Luca, van Til, Niek P
Published in Molecular therapy (17.09.2024)
Get full text
Published in Molecular therapy (17.09.2024)
Journal Article
High-throughput characterization of hematopoietic stem cell engraftment after intravenous and intracerebroventricular dosing
Plasschaert, Robert N, DeAndrade, Mark P, Hull, Fritz, Nguyen, Quoc, Peterson, Tara, Yan, Aimin, Loperfido, Mariana, Baricordi, Cristina, Barbarossa, Luigi, Yoon, John K, Dogan, Yildirim, Unnisa, Zeenath, Schindler, Jeffrey W, van Til, Niek P, Biasco, Luca, Mason, Chris
Published in Molecular therapy (25.05.2022)
Get full text
Published in Molecular therapy (25.05.2022)
Journal Article
Genetically engineered microglia-like cells have therapeutic potential for neurodegenerative disease
Plasschaert, Robert N, Deandrade, Mark P, Hull, Fritz, Nguyen, Quoc, Peterson, Tara, Yan, Aimin, Loperfido, Mariana, Baricordi, Cristina, Barbarossa, Luigi, Yoon, John K, Yildirim Dogan, Unnisa, Zeenath, Schindler, Jeffrey W, Van Til, Niek P, Biasco, Luca, Mason, Chris
Published in bioRxiv (18.09.2021)
Published in bioRxiv (18.09.2021)
Get full text
Paper