Gene therapy delivered micro-dystrophins co-localize with transgenic utrophin in dystrophic skeletal muscle fibers
Krishna, Swathy, Piepho, Arden B., Lake, Dana M., Cumby, Laurel R., Lortz, Kaelyn K., Lowe, Jeovanna, Chamberlain, Jeffrey S., Rafael-Fortney, Jill A.
Published in Neuromuscular disorders : NMD (01.03.2024)
Published in Neuromuscular disorders : NMD (01.03.2024)
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Journal Article
Mineralocorticoid receptor antagonists and glucocorticoids differentially affect skeletal muscle inflammation and pathology in muscular dystrophy
Howard, Zachary M, Gomatam, Chetan K, Rabolli, Charles P, Lowe, Jeovanna, Piepho, Arden B, Bansal, Shyam S, Accornero, Federica, Rafael-Fortney, Jill A
Published in JCI insight (10.10.2022)
Published in JCI insight (10.10.2022)
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Micro-dystrophin gene therapy demonstrates long-term cardiac efficacy in a severe Duchenne muscular dystrophy model
Piepho, Arden B., Lowe, Jeovanna, Cumby, Laurel R., Dorn, Lisa E., Lake, Dana M., Rastogi, Neha, Gertzen, Megan D., Sturgill, Sarah L., Odom, Guy L., Ziolo, Mark T., Accornero, Federica, Chamberlain, Jeffrey S., Rafael-Fortney, Jill A.
Published in Molecular therapy. Methods & clinical development (09.03.2023)
Published in Molecular therapy. Methods & clinical development (09.03.2023)
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Optimization and scaling of patient-derived brain organoids uncovers deep phenotypes of disease
Shah, Kevan, Bedi, Rishi, Rogozhnikov, Alex, Ramkumar, Pavan, Tong, Zhixiang, Rash, Brian, Morgan, Stanton, Sorokin, Jordan, Apaydin, Cagsar, Batarse, Anthony, Bergamaschi, Julia, Blattner, Robert, Brown, Spencer, Bosshardt, Anthony, Castrillo, Carlos, Dang, Brenda, Drusinsky, Shiron, Enriquez, Luigi, Grayson, David, Hilliard, Juliana, Hsu, Pei-Ken, Johnson, Chili, Jones, Ryan, Lash, Andy, Chia-Yao, Lee, Li, Kelly, Mckay, Austin, Mount, Elliot, Nicola, Justin, Oumzil, Ismael, Paek, Justin, Pascoe, Deborah, Piepho, Arden, Poust, Sean, Quang, Daphne, Schultz, Matthew, Sims, Jessica, Taylor, Patrick, Geffen Treiman, Wueseke, Oliver, Young, Noah, Pollen, Alex Aaron, Flanzer, Doug, Chao, Daniel, Skibinski, Gaia, Kato, Saul, Escola, Sean
Published in bioRxiv (29.08.2020)
Published in bioRxiv (29.08.2020)
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