RAN Translation in Huntington Disease
Bañez-Coronel, Monica, Ayhan, Fatma, Tarabochia, Alex D, Zu, Tao, Perez, Barbara A, Tusi, Solaleh Khoramian, Pletnikova, Olga, Borchelt, David R, Ross, Christopher A, Margolis, Russell L, Yachnis, Anthony T, Troncoso, Juan C, Ranum, Laura P W
Published in Neuron (Cambridge, Mass.) (18.11.2015)
Published in Neuron (Cambridge, Mass.) (18.11.2015)
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Journal Article
Management of Neuroinflammatory Responses to AAV-Mediated Gene Therapies for Neurodegenerative Diseases
Perez, Barbara A, Shutterly, Alison, Chan, Ying Kai, Byrne, Barry J, Corti, Manuela
Published in Brain sciences (22.02.2020)
Published in Brain sciences (22.02.2020)
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Journal Article
CCG•CGG interruptions in high‐penetrance SCA8 families increase RAN translation and protein toxicity
Perez, Barbara A, Shorrock, Hannah K, Banez‐Coronel, Monica, Zu, Tao, Romano, Lisa EL, Laboissonniere, Lauren A, Reid, Tammy, Ikeda, Yoshio, Reddy, Kaalak, Gomez, Christopher M, Bird, Thomas, Ashizawa, Tetsuo, Schut, Lawrence J, Brusco, Alfredo, Berglund, J Andrew, Hasholt, Lis F, Nielsen, Jorgen E, Subramony, SH, Ranum, Laura PW
Published in EMBO molecular medicine (08.11.2021)
Published in EMBO molecular medicine (08.11.2021)
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Journal Article
SCA8 RAN polySer protein preferentially accumulates in white matter regions and is regulated by eIF3F
Ayhan, Fatma, Perez, Barbara A, Shorrock, Hannah K, Zu, Tao, Banez‐Coronel, Monica, Reid, Tammy, Furuya, Hirokazu, Clark, H Brent, Troncoso, Juan C, Ross, Christopher A, Subramony, SH, Ashizawa, Tetsuo, Wang, Eric T, Yachnis, Anthony T, Ranum, Laura PW
Published in The EMBO journal (01.10.2018)
Published in The EMBO journal (01.10.2018)
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Journal Article
In‐silico media optimization for continuous cultures using genome scale metabolic networks: The case of CHO‐K1
Pérez‐Fernández, Bárbara A., Fernandez‐de‐Cossio‐Diaz, Jorge, Boggiano, Tammy, León, Kalet, Mulet, Roberto
Published in Biotechnology and bioengineering (01.05.2021)
Published in Biotechnology and bioengineering (01.05.2021)
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Journal Article
SCA 8 RAN polySer protein preferentially accumulates in white matter regions and is regulated by eIF 3F
Ayhan, Fatma, Perez, Barbara A, Shorrock, Hannah K, Zu, Tao, Banez‐Coronel, Monica, Reid, Tammy, Furuya, Hirokazu, Clark, H Brent, Troncoso, Juan C, Ross, Christopher A, Subramony, SH, Ashizawa, Tetsuo, Wang, Eric T, Yachnis, Anthony T, Ranum, Laura PW
Published in The EMBO journal (01.10.2018)
Published in The EMBO journal (01.10.2018)
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Journal Article
A1 New starts and directions: understanding the role of hidden expansion proteins in HD
Bañez-Coronel, Monica, Ayhan, Fatma, Tarabochia, Alex D, Zu, Tao, Perez, Barbara A, Tusi, Solaleh Khoramian, Pletnikova, Olga, Borchelt, David R, Ross, Christopher A, Margolis, Russell L, T Yachnis, Anthony, Troncoso, Juan C, PW Ranum, Laura
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2016)
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2016)
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Journal Article
CCG•CGG interruptions in high penetrance SCA8 families increase RAN translation and protein toxicity
Perez, Barbara A, Shorrock, Hannah K, Banez-Coronel, Monica, Laboissonniere, Lauren A, Reid, Tammy, Ikeda, Yoshio, Reddy, Kaalak, Gomez, Christopher M, Bird, Thomas, Ashizawa, Tetsuo, Schut, Lawrence J, Brusco, Alfredo, Berglund, J Andrew, Hasholt, Lis F, Nielsen, Jorgen E, Subramony, Sh, Ranum, Laura Pw
Published in bioRxiv (10.02.2021)
Published in bioRxiv (10.02.2021)
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