Delivery technologies for in utero gene therapy
Palanki, Rohan, Peranteau, William H., Mitchell, Michael J.
Published in Advanced drug delivery reviews (01.02.2021)
Published in Advanced drug delivery reviews (01.02.2021)
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Journal Article
In utero CRISPR-mediated therapeutic editing of metabolic genes
Rossidis, Avery C, Stratigis, John D, Chadwick, Alexandra C, Hartman, Heather A, Ahn, Nicholas J, Li, Haiying, Singh, Kshitiz, Coons, Barbara E, Li, Li, Lv, Wenjian, Zoltick, Philip W, Alapati, Deepthi, Zacharias, William, Jain, Rajan, Morrisey, Edward E, Musunuru, Kiran, Peranteau, William H
Published in Nature medicine (01.10.2018)
Published in Nature medicine (01.10.2018)
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Journal Article
Drug delivery technologies for fetal, neonatal, and maternal therapy
Palanki, Rohan, Peranteau, William H, Mitchell, Michael J
Published in Advanced drug delivery reviews (01.10.2022)
Published in Advanced drug delivery reviews (01.10.2022)
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Journal Article
An extra-uterine system to physiologically support the extreme premature lamb
Partridge, Emily A, Davey, Marcus G, Hornick, Matthew A, McGovern, Patrick E, Mejaddam, Ali Y, Vrecenak, Jesse D, Mesas-Burgos, Carmen, Olive, Aliza, Caskey, Robert C, Weiland, Theodore R, Han, Jiancheng, Schupper, Alexander J, Connelly, James T, Dysart, Kevin C, Rychik, Jack, Hedrick, Holly L, Peranteau, William H, Flake, Alan W
Published in Nature communications (25.04.2017)
Published in Nature communications (25.04.2017)
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Journal Article
Morphologic Features in Congenital Pulmonary Airway Malformations and Pulmonary Sequestrations Correlate With Mutation Status: A Mechanistic Approach to Classification
Nelson, Nya D, Xu, Feng, Peranteau, William H, Li, Marilyn, Pogoriler, Jennifer
Published in The American journal of surgical pathology (01.05.2023)
Published in The American journal of surgical pathology (01.05.2023)
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Journal Article
Transumbilical extracorporeal laparoscopic-assisted appendectomy
Perea, Lindsey, Peranteau, William H., Laje, Pablo
Published in Journal of pediatric surgery (01.02.2018)
Published in Journal of pediatric surgery (01.02.2018)
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Journal Article
Rapid and definitive treatment of phenylketonuria in variant-humanized mice with corrective editing
Brooks, Dominique L, Carrasco, Manuel J, Qu, Ping, Peranteau, William H, Ahrens-Nicklas, Rebecca C, Musunuru, Kiran, Alameh, Mohamad-Gabriel, Wang, Xiao
Published in Nature communications (10.06.2023)
Published in Nature communications (10.06.2023)
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Journal Article
Fetal Myelomeningocele Repair: The Post-MOMS Experience at the Children's Hospital of Philadelphia
Moldenhauer, Julie S., Soni, Shelly, Rintoul, Natalie E., Spinner, Susan S., Khalek, Nahla, Martinez-Poyer, Juan, Flake, Alan W., Hedrick, Holly L., Peranteau, William H., Rendon, Norma, Koh, Jamie, Howell, Lori J., Heuer, Gregory G., Sutton, Leslie N., Johnson, Mark P., Adzick, N. Scott
Published in Fetal diagnosis and therapy (01.04.2015)
Published in Fetal diagnosis and therapy (01.04.2015)
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Journal Article
InUtero Gene Therapy: Progress and Challenges
Bose, Sourav K., Menon, Pallavi, Peranteau, William H.
Published in Trends in molecular medicine (01.08.2021)
Published in Trends in molecular medicine (01.08.2021)
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Journal Article
Foetal genome editing
Bose, Sourav K, Kennedy, Kara, Peranteau, William H
Published in Current opinion in obstetrics & gynecology (01.04.2023)
Published in Current opinion in obstetrics & gynecology (01.04.2023)
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Journal Article
Mucinous Cell Clusters in Infantile Congenital Pulmonary Airway Malformations Mimic Adult Mucinous Adenocarcinoma But Are Not Associated With Poor Outcomes When Appropriately Resected
Nelson, Nya D, Litzky, Leslie A, Peranteau, William H, Pogoriler, Jennifer
Published in The American journal of surgical pathology (01.08.2020)
Published in The American journal of surgical pathology (01.08.2020)
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Journal Article
Fetal stem cell and gene therapy
Witt, Russell, MacKenzie, Tippi C, Peranteau, William H
Published in Seminars in fetal & neonatal medicine (01.12.2017)
Published in Seminars in fetal & neonatal medicine (01.12.2017)
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Journal Article
In utero adenine base editing corrects multi-organ pathology in a lethal lysosomal storage disease
Bose, Sourav K, White, Brandon M, Kashyap, Meghana V, Dave, Apeksha, De Bie, Felix R, Li, Haiying, Singh, Kshitiz, Menon, Pallavi, Wang, Tiankun, Teerdhala, Shiva, Swaminathan, Vishal, Hartman, Heather A, Jayachandran, Sowmya, Chandrasekaran, Prashant, Musunuru, Kiran, Jain, Rajan, Frank, David B, Zoltick, Philip, Peranteau, William H
Published in Nature communications (13.07.2021)
Published in Nature communications (13.07.2021)
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Journal Article
Amniotic fluid stabilized lipid nanoparticles for in utero intra-amniotic mRNA delivery
Swingle, Kelsey L., Billingsley, Margaret M., Bose, Sourav K., White, Brandon, Palanki, Rohan, Dave, Apeksha, Patel, Savan K., Gong, Ningqiang, Hamilton, Alex G., Alameh, Mohamad-Gabriel, Weissman, Drew, Peranteau, William H., Mitchell, Michael J.
Published in Journal of controlled release (01.01.2022)
Published in Journal of controlled release (01.01.2022)
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Journal Article
In utero gene editing for monogenic lung disease
Alapati, Deepthi, Zacharias, William J, Hartman, Heather A, Rossidis, Avery C, Stratigis, John D, Ahn, Nicholas J, Coons, Barbara, Zhou, Su, Li, Hiaying, Singh, Kshitiz, Katzen, Jeremy, Tomer, Yaniv, Chadwick, Alexandra C, Musunuru, Kiran, Beers, Michael F, Morrisey, Edward E, Peranteau, William H
Published in Science translational medicine (17.04.2019)
Published in Science translational medicine (17.04.2019)
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Journal Article
Ionizable lipid nanoparticles for in utero mRNA delivery
Riley, Rachel S, Kashyap, Meghana V, Billingsley, Margaret M, White, Brandon, Alameh, Mohamad-Gabriel, Bose, Sourav K, Zoltick, Philip W, Li, Hiaying, Zhang, Rui, Cheng, Andrew Y, Weissman, Drew, Peranteau, William H, Mitchell, Michael J
Published in Science advances (01.01.2021)
Published in Science advances (01.01.2021)
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Journal Article
Molecular and Cellular In Utero Therapy
Berkowitz, Cara L, Luks, Valerie L, Puc, Marcelina, Peranteau, William H
Published in Clinics in perinatology (01.12.2022)
Published in Clinics in perinatology (01.12.2022)
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Journal Article
Inhaled Nitric Oxide Is Associated with Improved Oxygenation in a Subpopulation of Infants with Congenital Diaphragmatic Hernia and Pulmonary Hypertension
Lawrence, Kendall M., Monos, Stylianos, Adams, Samantha, Herkert, Lisa, Peranteau, William H., Munson, David A., Hopper, Rachel K., Avitabile, Catherine M., Rintoul, Natalie E., Hedrick, Holly L.
Published in The Journal of pediatrics (01.04.2020)
Published in The Journal of pediatrics (01.04.2020)
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Journal Article