Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins
Pavani, Giulia, Laurent, Marine, Fabiano, Anna, Cantelli, Erika, Sakkal, Aboud, Corre, Guillaume, Lenting, Peter J., Concordet, Jean-Paul, Toueille, Magali, Miccio, Annarita, Amendola, Mario
Published in Nature communications (29.07.2020)
Published in Nature communications (29.07.2020)
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Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements
Lattanzi, Annalisa, Meneghini, Vasco, Pavani, Giulia, Amor, Fatima, Ramadier, Sophie, Felix, Tristan, Antoniani, Chiara, Masson, Cecile, Alibeu, Olivier, Lee, Ciaran, Porteus, Matthew H., Bao, Gang, Amendola, Mario, Mavilio, Fulvio, Miccio, Annarita
Published in Molecular therapy (02.01.2019)
Published in Molecular therapy (02.01.2019)
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CRISPR-Based Gene Therapies: From Preclinical to Clinical Treatments
Laurent, Marine, Geoffroy, Marine, Pavani, Giulia, Guiraud, Simon
Published in Cells (Basel, Switzerland) (08.05.2024)
Published in Cells (Basel, Switzerland) (08.05.2024)
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Overcoming preexisting humoral immunity to AAV using capsid decoys
Mingozzi, Federico, Anguela, Xavier M, Pavani, Giulia, Chen, Yifeng, Davidson, Robert J, Hui, Daniel J, Yazicioglu, Mustafa, Elkouby, Liron, Hinderer, Christian J, Faella, Armida, Howard, Carolann, Tai, Alex, Podsakoff, Gregory M, Zhou, Shangzhen, Basner-Tschakarjan, Etiena, Wright, John Fraser, High, Katherine A
Published in Science translational medicine (17.07.2013)
Published in Science translational medicine (17.07.2013)
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p65 signaling dynamics drive the developmental progression of hematopoietic stem and progenitor cells through cell cycle regulation
Campbell, Clyde A., Calderon, Rodolfo, Pavani, Giulia, Cheng, Xiaoyi, Barakat, Radwa, Snella, Elizabeth, Liu, Fang, Peng, Xiyu, Essner, Jeffrey J., Dorman, Karin S., McGrail, Maura, Gadue, Paul, French, Deborah L., Espin-Palazon, Raquel
Published in Nature communications (06.09.2024)
Published in Nature communications (06.09.2024)
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Nod1-dependent NF-kB activation initiates hematopoietic stem cell specification in response to small Rho GTPases
Cheng, Xiaoyi, Barakat, Radwa, Pavani, Giulia, Usha, Masuma Khatun, Calderon, Rodolfo, Snella, Elizabeth, Gorden, Abigail, Zhang, Yudi, Gadue, Paul, French, Deborah L., Dorman, Karin S., Fidanza, Antonella, Campbell, Clyde A., Espin-Palazon, Raquel
Published in Nature communications (23.11.2023)
Published in Nature communications (23.11.2023)
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Author Correction: Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins
Pavani, Giulia, Laurent, Marine, Fabiano, Anna, Cantelli, Erika, Sakkal, Aboud, Corre, Guillaume, Lenting, Peter J., Concordet, Jean-Paul, Toueille, Magali, Miccio, Annarita, Amendola, Mario
Published in Nature communications (13.08.2020)
Published in Nature communications (13.08.2020)
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Catalytic domain modification and viral gene delivery of activated factor VII confers hemostasis at reduced expression levels and vector doses in vivo
Margaritis, Paris, Roy, Elise, Faella, Armida, Downey, Harre D., Ivanciu, Lacramioara, Pavani, Giulia, Zhou, Shangzhen, Bunte, Ralph M., High, Katherine A.
Published in Blood (14.04.2011)
Published in Blood (14.04.2011)
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In vivo hematopoietic stem cell modification by mRNA delivery
Breda, Laura, Papp, Tyler E, Triebwasser, Michael P, Yadegari, Amir, Fedorky, Megan T, Tanaka, Naoto, Abdulmalik, Osheiza, Pavani, Giulia, Wang, Yongping, Grupp, Stephan A, Chou, Stella T, Ni, Houping, Mui, Barbara L, Tam, Ying K, Weissman, Drew, Rivella, Stefano, Parhiz, Hamideh
Published in Science (American Association for the Advancement of Science) (28.07.2023)
Published in Science (American Association for the Advancement of Science) (28.07.2023)
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Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human b-globin locus
Antoniani, Chiara, Meneghini, Vasco, Lattanzi, Annalisa, Felix, Tristan, Romano, Oriana, Magrin, Elisa, Weber, Leslie, Pavani, Giulia, El Hoss, Sara, Kurita, Ryo, Nakamura, Yukio, Cradick, Thomas, Lundberg, Ante, Porteus, Matthew, Amendola, Mario, El Nemer, Wassim, Cavazzana, Marina, Mavilio, Fulvio, Miccio, Annarita
Published in Blood (26.04.2018)
Published in Blood (26.04.2018)
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3069 – OSCILLATORY SIGNALING DYNAMICS DICTATE THE DEVELOPMENTAL PROGRESSION OF HEMATOPOIETIC STEM CELLS
Campbell, Clyde, Calderon, Rodolfo, Pavani, Giulia, Barakat, Radwa, Cheng, Xiaoyi, Gaude, Paul, French, Deborah, Palazon, Raquel Espin
Published in Experimental hematology (01.08.2024)
Published in Experimental hematology (01.08.2024)
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2009 – TRACING BACK THE ANCESTORS OF HEMATOPOIETIC STEM AND PROGENITOR CELLS REVEAL THEIR UNIQUE MOLECULAR CHARACTERISTICS
Palazon, Raquel Espin, Campbell, Clyde, Calderon, Rodolfo, Pavani, Giulia, Barakat, Radwa, Cheng, Xiaoyi, French, Deborah, Gaude, Paul
Published in Experimental hematology (01.08.2024)
Published in Experimental hematology (01.08.2024)
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Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locus
Antoniani, Chiara, Meneghini, Vasco, Lattanzi, Annalisa, Felix, Tristan, Romano, Oriana, Magrin, Elisa, Weber, Leslie, Pavani, Giulia, El Hoss, Sara, Kurita, Ryo, Nakamura, Yukio, Cradick, Thomas J., Lundberg, Ante S., Porteus, Matthew, Amendola, Mario, El Nemer, Wassim, Cavazzana, Marina, Mavilio, Fulvio, Miccio, Annarita
Published in Blood (26.04.2018)
Published in Blood (26.04.2018)
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2004 – INFLAMMATORY FACTORS ORCHESTRATE THE BIRTH OF HSPCS THROUGH THEIR OSCILLATORY SIGNALING DYNAMICS
Campbell, Clyde, Barakat, Radwa, Calderon, Rodolfo, Pavani, Giulia, Dorman, Karin, Gaude, Paul, French, Deborah, Espin-Palazon, Raquel
Published in Experimental hematology (2023)
Published in Experimental hematology (2023)
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