Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy
Mercuri, Eugenio, Darras, Basil T, Chiriboga, Claudia A, Day, John W, Campbell, Craig, Connolly, Anne M, Iannaccone, Susan T, Kirschner, Janbernd, Kuntz, Nancy L, Saito, Kayoko, Shieh, Perry B, Tulinius, Már, Mazzone, Elena S, Montes, Jacqueline, Bishop, Kathie M, Yang, Qingqing, Foster, Richard, Gheuens, Sarah, Bennett, C. Frank, Farwell, Wildon, Schneider, Eugene, De Vivo, Darryl C, Finkel, Richard S
Published in The New England journal of medicine (15.02.2018)
Published in The New England journal of medicine (15.02.2018)
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