Multiplexed in vivo homology-directed repair and tumor barcoding enables parallel quantification of Kras variant oncogenicity
Winters, Ian P., Chiou, Shin-Heng, Paulk, Nicole K., McFarland, Christopher D., Lalgudi, Pranav V., Ma, Rosanna K., Lisowski, Leszek, Connolly, Andrew J., Petrov, Dmitri A., Kay, Mark A., Winslow, Monte M.
Published in Nature communications (12.12.2017)
Published in Nature communications (12.12.2017)
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Journal Article
Methods Matter: Standard Production Platforms for Recombinant AAV Produce Chemically and Functionally Distinct Vectors
Rumachik, Neil G., Malaker, Stacy A., Poweleit, Nicole, Maynard, Lucy H., Adams, Christopher M., Leib, Ryan D., Cirolia, Giana, Thomas, Dennis, Stamnes, Susan, Holt, Kathleen, Sinn, Patrick, May, Andrew P., Paulk, Nicole K.
Published in Molecular therapy. Methods & clinical development (11.09.2020)
Published in Molecular therapy. Methods & clinical development (11.09.2020)
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Journal Article
Editorial: "AAV Gene Therapy: Immunology and Immunotherapeutics"
Martinez-Navio, José M, Paulk, Nicole K, Gao, Guangping
Published in Frontiers in immunology (21.12.2021)
Published in Frontiers in immunology (21.12.2021)
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Journal Article
Comparison of highly pure rAAV9 vector stocks produced in suspension by PEI transfection or HSV infection reveals striking quantitative and qualitative differences
Trivedi, Prasad D., Yu, Chenghui, Chaudhuri, Payel, Johnson, Evan J., Caton, Tina, Adamson, Laura, Byrne, Barry J., Paulk, Nicole K., Clément, Nathalie
Published in Molecular therapy. Methods & clinical development (10.03.2022)
Published in Molecular therapy. Methods & clinical development (10.03.2022)
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Journal Article
Ploidy reductions in murine fusion-derived hepatocytes
Duncan, Andrew W, Hickey, Raymond D, Paulk, Nicole K, Culberson, Andrew J, Olson, Susan B, Finegold, Milton J, Grompe, Markus
Published in PLoS genetics (01.02.2009)
Published in PLoS genetics (01.02.2009)
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Journal Article
Bioengineered Viral Platform for Intramuscular Passive Vaccine Delivery to Human Skeletal Muscle
Paulk, Nicole K., Pekrun, Katja, Charville, Gregory W., Maguire-Nguyen, Katie, Wosczyna, Michael N., Xu, Jianpeng, Zhang, Yue, Lisowski, Leszek, Yoo, Bryan, Vilches-Moure, Jose G., Lee, Gordon K., Shrager, Joseph B., Rando, Thomas A., Kay, Mark A.
Published in Molecular therapy. Methods & clinical development (21.09.2018)
Published in Molecular therapy. Methods & clinical development (21.09.2018)
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Journal Article
Bioengineered AAV Capsids with Combined High Human Liver Transduction In Vivo and Unique Humoral Seroreactivity
Paulk, Nicole K., Pekrun, Katja, Zhu, Erhua, Nygaard, Sean, Li, Bin, Xu, Jianpeng, Chu, Kirk, Leborgne, Christian, Dane, Allison P., Haft, Annelise, Zhang, Yue, Zhang, Feijie, Morton, Chris, Valentine, Marcus B., Davidoff, Andrew M., Nathwani, Amit C., Mingozzi, Federico, Grompe, Markus, Alexander, Ian E., Lisowski, Leszek, Kay, Mark A.
Published in Molecular therapy (03.01.2018)
Published in Molecular therapy (03.01.2018)
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Journal Article
Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase
Puzzo, Francesco, Colella, Pasqualina, Biferi, Maria G, Bali, Deeksha, Paulk, Nicole K, Vidal, Patrice, Collaud, Fanny, Simon-Sola, Marcelo, Charles, Severine, Hardet, Romain, Leborgne, Christian, Meliani, Amine, Cohen-Tannoudji, Mathilde, Astord, Stephanie, Gjata, Bernard, Sellier, Pauline, van Wittenberghe, Laetitia, Vignaud, Alban, Boisgerault, Florence, Barkats, Martine, Laforet, Pascal, Kay, Mark A, Koeberl, Dwight D, Ronzitti, Giuseppe, Mingozzi, Federico
Published in Science translational medicine (29.11.2017)
Published in Science translational medicine (29.11.2017)
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Journal Article
An orange calcium-modulated bioluminescent indicator for non-invasive activity imaging
Oh, Younghee, Park, Yunhee, Cho, Julia H., Wu, Haodi, Paulk, Nicole K., Liu, Lan Xiang, Kim, Namdoo, Kay, Mark A., Wu, Joseph C., Lin, Michael Z.
Published in Nature chemical biology (01.05.2019)
Published in Nature chemical biology (01.05.2019)
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Journal Article
Fast-Seq: A Simple Method for Rapid and Inexpensive Validation of Packaged Single-Stranded Adeno-Associated Viral Genomes in Academic Settings
Maynard, Lucy H, Smith, Olivia, Tilmans, Nicolas P, Tham, Eleonore, Hosseinzadeh, Shayan, Tan, Weilun, Leenay, Ryan, May, Andrew P, Paulk, Nicole K
Published in Human gene therapy. Part B. Methods (01.12.2019)
Published in Human gene therapy. Part B. Methods (01.12.2019)
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Journal Article
In Vivo Selection of Transplanted Hepatocytes by Pharmacological Inhibition of Fumarylacetoacetate Hydrolase in Wild-type Mice
Paulk, Nicole K, Wursthorn, Karsten, Haft, Annelise, Pelz, Carl, Clarke, Gregory, Newell, Amy H, Olson, Susan B, Harding, Cary O, Finegold, Milton J, Bateman, Raymond L, Witte, John F, McClard, Ronald, Grompe, Markus
Published in Molecular therapy (01.10.2012)
Published in Molecular therapy (01.10.2012)
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Journal Article
262. Directed Evolution of Improved AAV Capsids for the Ideal Human Liver Vector–Can Human Liver Tropism and Human Immune Evasion Be Achieved?
Paulk, Nicole K., Pekrun, Katja, Lisowski, Leszek, Zhang, Yue, Chu, Kirk, Kay, Mark A.
Published in Molecular therapy (01.05.2015)
Published in Molecular therapy (01.05.2015)
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Journal Article
722. AAV Capsid Evolution for Enhanced Antibody Delivery to Human Skeletal Muscle for Use in Next-Generation HIV Vaccines and Muscle Gene Therapies
Paulk, Nicole K., Charville, Gregory, Maguire, Katie, Pekrun, Katja, Zhang, Yue, Tiffany, Matthew, Vilches-Moure, Jose, Lee, Gordon, Shrager, Joseph, Rando, Thomas, Kay, Mark A.
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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Journal Article
In Vivo Selection of Transplanted Hepatocytes by Pharmacological Inhibition of Fumarylacetoacetate Hydrolase in Wild-type Mice
Paulk, Nicole K, Wursthorn, Karsten, Haft, Annelise, Pelz, Carl, Clarke, Gregory, Newell, Amy H, Olson, Susan B, Harding, Cary O, Finegold, Milton J, Bateman, Raymond L, Witte, John F, McClard, Ronald, Grompe, Markus
Published in Molecular therapy (01.10.2012)
Published in Molecular therapy (01.10.2012)
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Journal Article
Ploidy Reductions in Murine Fusion-Derived Hepatocytes: e1000385
Duncan, Andrew W, Hickey, Raymond D, Paulk, Nicole K, Culberson, Andrew J, Olson, Susan B, Finegold, Milton J, Grompe, Markus
Published in PLoS genetics (01.02.2009)
Published in PLoS genetics (01.02.2009)
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Journal Article