Translation from a DMD exon 5 IRES results in a functional dystrophin isoform that attenuates dystrophinopathy in humans and mice
Wein, Nicolas, Vulin, Adeline, Falzarano, Maria S, Szigyarto, Christina Al-Khalili, Maiti, Baijayanta, Findlay, Andrew, Heller, Kristin N, Uhlén, Mathias, Bakthavachalu, Baskar, Messina, Sonia, Vita, Giuseppe, Passarelli, Chiara, Passarelli, Simona, Bovolenta, Matteo, Neri, Marcella, Gualandi, Francesca, Wilton, Steve D, Rodino-Klapac, Louise R, Yang, Lin, Dunn, Diane M, Schoenberg, Daniel R, Weiss, Robert B, Howard, Michael T, Ferlini, Alessandra, Flanigan, Kevin M
Published in Nature medicine (01.09.2014)
Published in Nature medicine (01.09.2014)
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