AAV5–Factor VIII Gene Transfer in Severe Hemophilia A
Rangarajan, Savita, Walsh, Liron, Lester, Will, Perry, David, Madan, Bella, Laffan, Michael, Yu, Hua, Vettermann, Christian, Pierce, Glenn F, Wong, Wing Y, Pasi, K. John
Published in The New England journal of medicine (28.12.2017)
Published in The New England journal of medicine (28.12.2017)
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Journal Article
Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A
Pasi, K. John, Rangarajan, Savita, Mitchell, Nina, Lester, Will, Symington, Emily, Madan, Bella, Laffan, Michael, Russell, Chris B, Li, Mingjin, Pierce, Glenn F, Wong, Wing Y
Published in The New England journal of medicine (02.01.2020)
Published in The New England journal of medicine (02.01.2020)
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Journal Article
Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A
Pasi, K John, Rangarajan, Savita, Mitchell, Nina, Lester, Will, Symington, Emily, Madan, Bella, Laffan, Michael, Russell, Chris B, Li, Mingjin, Pierce, Glenn F, Wong, Wing Y
Published in The New England journal of medicine (02.01.2020)
Published in The New England journal of medicine (02.01.2020)
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Towards achieving a haemophilia‐free mind
Hermans, Cedric, Pierce, Glenn F.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.07.2023)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.07.2023)
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Journal Article
The COVID‐19 pandemic: New global challenges for the haemophilia community
Hermans, Cedric, Weill, Alain, Pierce, Glenn F.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2020)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2020)
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Web Resource
WFH Guidelines for the Management of Hemophilia, 3rd edition
Srivastava, Alok, Santagostino, Elena, Dougall, Alison, Kitchen, Steve, Sutherland, Megan, Pipe, Steven W., Carcao, Manuel, Mahlangu, Johnny, Ragni, Margaret V., Windyga, Jerzy, Llinás, Adolfo, Goddard, Nicholas J., Mohan, Richa, Poonnoose, Pradeep M., Feldman, Brian M., Lewis, Sandra Zelman, Berg, H. Marijke, Pierce, Glenn F.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.08.2020)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.08.2020)
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The underevaluated impacts of the therapeutic revolution of hemophilia on women and girls
Hermans, Cedric, Krumb, Evelien, Rotellini, Dawn, Pierce, Glenn F.
Published in Journal of thrombosis and haemostasis (01.04.2024)
Published in Journal of thrombosis and haemostasis (01.04.2024)
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Interindividual variability in transgene mRNA and protein production following adeno-associated virus gene therapy for hemophilia A
Fong, Sylvia, Yates, Bridget, Sihn, Choong-Ryoul, Mattis, Aras N., Mitchell, Nina, Liu, Su, Russell, Chris B., Kim, Benjamin, Lawal, Adebayo, Rangarajan, Savita, Lester, Will, Bunting, Stuart, Pierce, Glenn F., Pasi, K. John, Wong, Wing Yen
Published in Nature medicine (01.04.2022)
Published in Nature medicine (01.04.2022)
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Journal Article
Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A
Ozelo, Margareth C, Mahlangu, Johnny, Pasi, K. John, Giermasz, Adam, Leavitt, Andrew D, Laffan, Michael, Symington, Emily, Quon, Doris V, Wang, Jiaan-Der, Peerlinck, Kathelijne, Pipe, Steven W, Madan, Bella, Key, Nigel S, Pierce, Glenn F, O’Mahony, Brian, Kaczmarek, Radoslaw, Henshaw, Joshua, Lawal, Adebayo, Jayaram, Kala, Huang, Mei, Yang, Xinqun, Wong, Wing Y, Kim, Benjamin
Published in The New England journal of medicine (17.03.2022)
Published in The New England journal of medicine (17.03.2022)
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Journal Article
Persistence of haemostatic response following gene therapy with valoctocogene roxaparvovec in severe haemophilia A
Pasi, K John, Laffan, Michael, Rangarajan, Savita, Robinson, Tara M, Mitchell, Nina, Lester, Will, Symington, Emily, Madan, Bella, Yang, Xinqun, Kim, Benjamin, Pierce, Glenn F, Wong, Wing Yen
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2021)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2021)
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