310. Analysis of AAV5 Biodistribution and Viral Shedding in the Presence or Absence of Neutralizing Antibodies
Salas, David, Majowicz, Anna, Zabaleta, Nerea, Rodríguez-Garcia, Estefania, Petry, Harald, Ferreira, Valerie, Aseguinolaza, Gloria Gonzalez
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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700. Successful Repeated Hepatic Gene Delivery in Mice and Non-Human Primates Achieved by Sequential Administration of AAV5 and AAV1 Vector Serotypes
Majowicz, Anna, Salas, David, Zabaleta, Nerea, Rodríguez-Garcia, Estefania, Aseguinolaza, Gloria Gonzalez, Petry, Harald, Ferreira, Valerie
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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618. Directional Transduction of AAV-5 Vectors in the NHP Brain
Blits, Bas, Samaranch, Lluis, Bringas, John, Sebastian, Waldy San, Bankiewicz, Krystoff, Petry, Harald
Published in Molecular therapy (01.05.2016)
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Safe, Efficient, and Reproducible Gene Therapy of the Brain in the Dog Models of Sanfilippo and Hurler Syndromes
Ellinwood, N Matthew, Ausseil, Jérôme, Desmaris, Nathalie, Bigou, Stéphanie, Liu, Song, Jens, Jackie K, Snella, Elizabeth M, Mohammed, Eman EA, Thomson, Christopher B, Raoul, Sylvie, Joussemet, Béatrice, Roux, Françoise, Chérel, Yan, Lajat, Yaouen, Piraud, Monique, Benchaouir, Rachid, Hermening, Stephan, Petry, Harald, Froissart, Roseline, Tardieu, Marc, Ciron, Carine, Moullier, Philippe, Parkes, Jennifer, Kline, Karen L, Maire, Irène, Vanier, Marie-Thérèse, Heard, Jean-Michel, Colle, Marie-Anne
Published in Molecular therapy (01.02.2011)
Published in Molecular therapy (01.02.2011)
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Mir-142-3p target sequences reduce transgene-directed immunogenicity following intramuscular adeno-associated virus 1 vector-mediated gene delivery
Majowicz, Anna, Maczuga, Piotr, Kwikkers, Karin L., van der Marel, Sander, van Logtenstein, Richard, Petry, Harald, van Deventer, Sander J., Konstantinova, Pavlina, Ferreira, Valerie
Published in The journal of gene medicine (01.06.2013)
Published in The journal of gene medicine (01.06.2013)
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Safety and Efficacy of an Adeno Associated Virus-Based Vector Carrying the Human Clotting Factor IX Gene (AAV5-hFIX) As Studied in Non-Human Primates
Nijmeijer, Bart, Petry, Harald, Spronck, Lisa, Van Der Kruijssen, Corina, Petersen, Jorgen, Salmon, Florence
Published in Blood (06.12.2014)
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Phase 1-2 Clinical Trial of a Recombinant AAV5 Vector Containing the Human FIX Gene in Patients with Severe or Moderately Severe Haemophilia B
Miesbach, Wolfgang A., Meyer, Christian, Nijmeijer, Bart, Salmon, Florence, Grosios, Nadina, Petry, Harald, Leebeek, Frank W.G.
Published in Blood (06.12.2014)
Published in Blood (06.12.2014)
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Safety and liver transduction efficacy of rAAV5-cohPBGD in nonhuman primates: a potential therapy for acute intermittent porphyria
Pañeda, Astrid, Lopez-Franco, Esperanza, Kaeppel, Christine, Unzu, Carmen, Gil-Royo, Ana Gloria, D'Avola, Delia, Beattie, Stuart G, Olagüe, Cristina, Ferrero, Roberto, Sampedro, Ana, Mauleon, Itsaso, Hermening, Stephan, Salmon, Florence, Benito, Alberto, Gavira, Juan Jose, Cornet, María Eugenia, del Mar Municio, María, von Kalle, Christof, Petry, Harald, Prieto, Jesus, Schmidt, Manfred, Fontanellas, Antonio, González-Aseguinolaza, Gloria
Published in Human gene therapy (01.12.2013)
Published in Human gene therapy (01.12.2013)
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L5 Pre-clinical evaluation of aav5-mihtt gene therapy of huntington’s disease in rodents
Miniarikova, Jana, Zanella, Ilaria, Blits, Bas, Evers, Melvin, Zimmer, Virginie, Spoerl, Alexia, Southwell, Amber, Hayden, Michael, Deventer, Sander van, Deglon, Nicole, Petry, Harald, Konstantinova, Pavlina
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2016)
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2016)
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L4 Sustained and strong HTT silencing by AAV5-miHTT as therapy for huntington’s disease
Evers, Melvin, Miniarikova, Jana, Blits, Bas, Spronck, Lisa, Brouwers, Cynthia, Déglon, Nicole, Motlik, Jan, Bankiewicz, Krystof, Southwell, Amber, Haan, Martin de, Richard, Charles, Petry, Harald, Konstantinova, Pavlina
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2016)
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2016)
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Impaired thymopoietic potential of immature CD3–CD4+CD8– T cell precursors from SIV-infected rhesus monkeys
Neben, Kai, Heidbreder, Marc, Müller, Justus, Marxer, Anke, Petry, Harald, Didier, Andrea, Schimpl, Anneliese, Hünig, Thomas, Kerkau, Thomas
Published in International immunology (01.09.1999)
Published in International immunology (01.09.1999)
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Embedding siRNA sequences targeting Apolipoprotein B100 in shRNA and miRNA scaffolds results in differential processing and in vivo efficacy
Maczuga, Piotr, Lubelski, Jacek, van Logtenstein, Richard, Borel, Florie, Blits, Bas, Fakkert, Erwin, Costessi, Adalberto, Butler, Derek, van Deventer, Sander, Petry, Harald, Koornneef, Annemart, Konstantinova, Pavlina
Published in Molecular therapy (01.01.2013)
Published in Molecular therapy (01.01.2013)
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I04 AAV5-MIHTT gene therapy demonstrates broad distribution and strong human mutant huntingtin lowering in a huntington disease minipig model
Klima, Jiri, Evers, Melvin M, Miniarikova, Jana, Juhas, Stefan, Vallès, Astrid, Bohuslavova, Bozena, Juhasova, Jana, Skalnikova, Helena Kupcova, Vodicka, Petr, Valekova, Ivona, Brouwers, Cynthia, Blits, Bas, Lubelski, Jacek, Kovarova, Hana, van Deventer, Sander J, Petry, Harald, Motlik, Jan, Konstantinova, Pavlina, Ellederova, Zdenka
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2018)
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2018)
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Apolipoprotein B Knockdown by AAV-delivered shRNA Lowers Plasma Cholesterol in Mice
Koornneef, Annemart, Maczuga, Piotr, van Logtenstein, Richard, Borel, Florie, Blits, Bas, Ritsema, Tita, van Deventer, Sander, Petry, Harald, Konstantinova, Pavlina
Published in Molecular therapy (01.04.2011)
Published in Molecular therapy (01.04.2011)
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Pathogenic classification of LPL gene variants reported to be associated with LPL deficiency
Rodrigues, Rute, Artieda, Marta, Tejedor, Diego, Martínez, Antonio, Konstantinova, Pavlina, Petry, Harald, Meyer, Christian, Corzo, Deya, Sundgreen, Claus, Klor, Hans U, Gouni-Berthold, Ioanna, Westphal, Sabine, Steinhagen-Thiessen, Elisabeth, Julius, Ulrich, Winkler, Karl, Stroes, Erik, Vogt, Anja, Hardt, Phillip, Prophet, Heinrich, Otte, Britta, Nordestgaard, Borge G, Deeb, Samir S, Brunzell, John D
Published in Journal of clinical lipidology (01.03.2016)
Published in Journal of clinical lipidology (01.03.2016)
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664. Improving AAV Gene Therapy Safety Analysis: Multiplex LAM-PCR Provide New Insights Into AAV Vector Integration
Gil-Farina, Irene, Käppel, Christine, Wilkening, Stefan, Lopez-Franco, Esperanza, Astrid Paneda, Maria, Prieto, Jesús, Spronck, Lisa, von Kalle, Christof, Petry, Harald, Gonzalez-Aseguinolaza, Gloria, Schmidt, Manfred
Published in Molecular therapy (01.05.2015)
Published in Molecular therapy (01.05.2015)
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Neutralizing antibodies against adeno‐associated viruses in inflammatory bowel disease patients: Implications for gene therapy
van der Marel, Sander, Comijn, Elisabeth M., Verspaget, Hein W., van Deventer, Sander, van den Brink, Gijs R., Petry, Harald, Hommes, Daniel W., Ferreira, Valerie
Published in Inflammatory bowel diseases (01.12.2011)
Published in Inflammatory bowel diseases (01.12.2011)
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곤충 세포에서의 개선된 AAV 캡시드 생산
DU PLESSIS DAVID JOHANNES FRANCOIS, PETRY HARALD PETER ALBERT, TER BRAKE OLIVIER, BOSMA SEBASTIAAN MENNO, LUBELSKI JACEK
Year of Publication 04.05.2020
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Year of Publication 04.05.2020
Patent
Reply to: NGS library preparation may generate artifactual integration sites of AAV vectors
Kaeppel, Christine, Beattie, Stuart G, Fronza, Raffaele, van Logtenstein, Richard, Salmon, Florence, Schmidt, Sabine, Wolf, Stephan, Nowrouzi, Ali, Glimm, Hanno, von Kalle, Christof, Petry, Harald, Gaudet, Daniel, Schmidt, Manfred
Published in Nature medicine (01.06.2014)
Published in Nature medicine (01.06.2014)
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