Novel approaches to analysis of the North Star Ambulatory Assessment (NSAA) in Duchenne muscular dystrophy (DMD): Observations from a phase 2 trial
Muntoni, Francesco, Guglieri, Michela, Mah, Jean K., Wagner, Kathryn R., Brandsema, John F., Butterfield, Russell J., McDonald, Craig M., Mayhew, Anna G., Palmer, Jeffrey P., Marraffino, Shannon, Charnas, Lawrence, Mercuri, Eugenio
Published in PloS one (23.08.2022)
Published in PloS one (23.08.2022)
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Randomized phase 2 trial and open-label extension of domagrozumab in Duchenne muscular dystrophy
Wagner, Kathryn R., Abdel-Hamid, Hoda Z., Mah, Jean K., Campbell, Craig, Guglieri, Michela, Muntoni, Francesco, Takeshima, Yasuhiro, McDonald, Craig M., Kostera-Pruszczyk, Anna, Karachunski, Peter, Butterfield, Russell J., Mercuri, Eugenio, Fiorillo, Chiara, Bertini, Enrico S., Tian, Cuixia, Statland, Jeffery, Sadosky, Alesia B., Purohit, Vivek S., Sherlock, Sarah P., Palmer, Jeffrey P., Binks, Michael, Charnas, Lawrence, Marraffino, Shannon, Wong, Brenda L.
Published in Neuromuscular disorders : NMD (01.06.2020)
Published in Neuromuscular disorders : NMD (01.06.2020)
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Pectin acetylesterase 8 influences pectin acetylation in the seed coat, seed imbibition, and dormancy in common bean (Phaseolus vulgaris L.)
Palmer, Jeffrey P., Pajak, Aga, Robson, Blake, Zhang, BaiLing, Joshi, Jaya, Diapari, Marwan, Pauls, K. Peter, Marsolais, Frédéric
Published in Legume science (01.09.2022)
Published in Legume science (01.09.2022)
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A RANDOMIZED, DOUBLE-BLIND, DOUBLE-DUMMY, CONTROLLED DOSE COMPARISON OF THALIDOMIDE FOR TREATMENT OF ERYTHEMA NODOSUM LEPROSUM
VILLAHERMOSA, LAARNI G, FAJARDO, TRANQUILINO T., JR, ABALOS, RODOLFO M, BALAGON, MARIA V, TAN, ESTERLINA V, CELLONA, ROLAND V, PALMER, JEFFREY P, WITTES, JANET, THOMAS, STEVEN D, KOOK, KARIN A, WALSH, GERALD P, WALSH, DOUGLAS S
Published in The American journal of tropical medicine and hygiene (01.05.2005)
Published in The American journal of tropical medicine and hygiene (01.05.2005)
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A randomized, double-blind, double-dummy, controlled dose comparison of thalidomide for treatment of erythema nodosum leprosum
VILLAHERMOSA, Laarni G, FAJARDO, Tranquilino T, WALSH, Gerald P, WALSH, Douglas S, ABALOS, Rodolfo M, BALAGON, Maria V, TAN, Esterlina V, CELLONA, Roland V, PALMER, Jeffrey P, WITTES, Janet, THOMAS, Steven D, KOOK, Karin A
Published in The American journal of tropical medicine and hygiene (2005)
Published in The American journal of tropical medicine and hygiene (2005)
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Journal Article
Novel approaches to analysis of the North Star Ambulatory Assessment
Muntoni, Francesco, Guglieri, Michela, Mah, Jean K, Wagner, Kathryn R, Brandsema, John F, Butterfield, Russell J, McDonald, Craig M, Mayhew, Anna G, Palmer, Jeffrey P, Marraffino, Shannon, Charnas, Lawrence, Mercuri, Eugenio
Published in PloS one (23.08.2022)
Published in PloS one (23.08.2022)
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Journal Article
Novel approaches to analysis of the North Star Ambulatory Assessment : Observations from a phase 2 trial
Muntoni, Francesco, Guglieri, Michela, Mah, Jean K, Wagner, Kathryn R, Brandsema, John F, Butterfield, Russell J, McDonald, Craig M, Mayhew, Anna G, Palmer, Jeffrey P, Marraffino, Shannon, Charnas, Lawrence, Mercuri, Eugenio
Published in PloS one (23.08.2022)
Published in PloS one (23.08.2022)
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Palmer, Jeffrey P, Pajak, Aga, Robson, Blake, Zhang, BaiLing, Joshi, Jaya, Diapari, Marwan, Pauls, K Peter, Marsolais, Frédéric
Published in Legume science (01.09.2022)
Published in Legume science (01.09.2022)
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Journal Article
Cover Image
Palmer, Jeffrey P., Pajak, Aga, Robson, Blake, Zhang, BaiLing, Joshi, Jaya, Diapari, Marwan, Pauls, K. Peter, Marsolais, Frédéric
Published in Legume science (01.09.2022)
Published in Legume science (01.09.2022)
Get full text
Journal Article
Novel approaches to analysis of the North Star Ambulatory Assessment (NSAA) in Duchenne muscular dystrophy (DMD): Observations from a phase 2 trial
Francesco Muntoni, Michela Guglieri, Jean K. Mah, Kathryn R. Wagner, John F. Brandsema, Russell J. Butterfield, Craig M. McDonald, Anna G. Mayhew, Jeffrey P. Palmer, Shannon Marraffino, Lawrence Charnas, Eugenio Mercuri
Published in PloS one (01.01.2022)
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Published in PloS one (01.01.2022)
Journal Article