Bleeding Outcomes in Participants with Factor VIII Activity <5 IU/DL Post-Gene Transfer in GENEr8-1
Mahlangu, Johnny, Ozelo, Margareth Castro, Tan, Chee Wee, Giermasz, Adam, Wang, Jiaan-Der, Osmond, Dane, Yu, Hua, Robinson, Tara M.
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Transitioning from emicizumab prophylaxis to valoctocogene roxaparvovec gene therapy: A simulation study for individuals with severe haemophilia A
Agarwal, Suresh, Hermans, Cedric, Miesbach, Wolfgang, Peyvandi, Flora, Sidonio, Robert, Osmond, Dane, Newman, Vanessa, Henshaw, Josh, Pipe, Steven
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.07.2024)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.07.2024)
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Valoctocogene roxaparvovec gene therapy provides durable haemostatic control for up to 7 years for haemophilia A
Symington, Emily, Rangarajan, Savita, Lester, Will, Madan, Bella, Pierce, Glenn F, Raheja, Priyanka, Millar, Carolyn, Osmond, Dane, Li, Mingjin, Robinson, Tara M
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.09.2024)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.09.2024)
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Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment
Symington, Emily, Rangarajan, Savita, Lester, Will, Madan, Bella, Pierce, Glenn F., Raheja, Priyanka, Robinson, Tara M., Osmond, Dane, Russell, Chris B., Vettermann, Christian, Agarwal, Suresh K., Li, Mingjin, Wong, Wing Yen, Laffan, Michael
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2024)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2024)
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Three-year outcomes of valoctocogene roxaparvovec gene therapy for hemophilia A
Madan, Bella, Ozelo, Margareth C., Raheja, Priyanka, Symington, Emily, Quon, Doris V., Leavitt, Andrew D., Pipe, Steven W., Lowe, Gillian, Kenet, Gili, Reding, Mark T., Mason, Jane, Wang, Michael, von Drygalski, Annette, Klamroth, Robert, Shapiro, Susan, Chambost, Hervé, Dunn, Amy L., Oldenburg, Johannes, Chou, Sheng-Chieh, Peyvandi, Flora, Millar, Carolyn M., Osmond, Dane, Yu, Hua, Dashiell-Aje, Ebony, Robinson, Tara M., Mahlangu, Johnny
Published in Journal of thrombosis and haemostasis (01.07.2024)
Published in Journal of thrombosis and haemostasis (01.07.2024)
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