Gene therapy ameliorates cardiovascular disease in dogs with mucopolysaccharidosis VII
Sleeper, M M, Fornasari, B, Ellinwood, N M, Weil, M A, Melniczek, J, O'Malley, T M, Sammarco, C D, Xu, L, Ponder, K P, Haskins, M E
Published in Circulation (New York, N.Y.) (17.08.2004)
Published in Circulation (New York, N.Y.) (17.08.2004)
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Therapeutic Neonatal Hepatic Gene Therapy in Mucopolysaccharidosis VII Dogs
Ponder, Katherine Parker, Melniczek, John R., Xu, Lingfei, Weil, Margaret A., O'Malley, Thomas M., O'Donnell, Patricia A., Knox, Van W., Aguirre, Gustavo D., Mazrier, Hamutal, Ellinwood, N. Matthew, Sleeper, Meg, Maguire, Albert M., Volk, Susan W., Mango, Robert L., Zweigle, Jean, Wolfe, John H., Haskins, Mark E.
Published in Proceedings of the National Academy of Sciences - PNAS (01.10.2002)
Published in Proceedings of the National Academy of Sciences - PNAS (01.10.2002)
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CD30 + Lymphoproliferative Disorders of the Skin
Sauder, Maxwell B, O'Malley, John T, LeBoeuf, Nicole R
Published in Hematology/oncology clinics of North America (01.04.2017)
Published in Hematology/oncology clinics of North America (01.04.2017)
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Expression in blood cells may contribute to biochemical and pathological improvements after neonatal intravenous gene therapy for mucopolysaccharidosis VII in dogs
Wang, Bin, O’Malley, Thomas M., Xu, Lingfei, Vite, Charles, Wang, Ping, O’Donnell, Patricia A., Ellinwood, N. Matthew, Haskins, Mark E., Ponder, Katherine Parker
Published in Molecular genetics and metabolism (2006)
Published in Molecular genetics and metabolism (2006)
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Transduction of Hepatocytes after Neonatal Delivery of a Moloney Murine Leukemia Virus Based Retroviral Vector Results in Long-Term Expression of β-Glucuronidase in Mucopolysaccharidosis VII Dogs
Xu, Lingfei, Haskins, Mark E, Melniczek, John R, Gao, Cuihua, Weil, Margaret A, O'Malley, Thomas M, O'Donnell, Patricia A, Mazrier, Hamutal, Ellinwood, N Matthew, Zweigle, Jean, Wolfe, John H, Ponder, Katherine Parker
Published in Molecular therapy (01.02.2002)
Published in Molecular therapy (01.02.2002)
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Mucopolysaccharidosis type VII in a German Shepherd dog
Silverstein Dombrowski, D.C, Carmichael, K.P, Wang, P, O'Malley, T.M, Haskins, M.E, Giger, U
Published in Journal of the American Veterinary Medical Association (15.02.2004)
Published in Journal of the American Veterinary Medical Association (15.02.2004)
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