Transduction characteristics of alternative adeno-associated virus serotypes in the cat brain by intracisternal delivery
Hunter, Jacqueline E., Molony, Caitlyn M., Bagel, Jessica H., O’Donnell, Patricia A., Kaler, Stephen G., Wolfe, John H.
Published in Molecular therapy. Methods & clinical development (08.09.2022)
Published in Molecular therapy. Methods & clinical development (08.09.2022)
Get full text
Journal Article
Clinical Improvement of Alpha-mannosidosis Cat Following a Single Cisterna Magna Infusion of AAV1
Yoon, Sea Young, Bagel, Jessica H, O'Donnell, Patricia A, Vite, Charles H, Wolfe, John H
Published in Molecular therapy (01.01.2016)
Published in Molecular therapy (01.01.2016)
Get full text
Journal Article
The effect of neonatal gene therapy with a gamma retroviral vector on cardiac valve disease in mucopolysaccharidosis VII dogs after a decade
Bigg, Paul W., Sleeper, Meg M., O'Donnell, Patricia A., Liu, Yuli, Wu, Susan, Casal, Margret L., Haskins, Mark E., Ponder, Katherine P.
Published in Molecular genetics and metabolism (01.11.2013)
Published in Molecular genetics and metabolism (01.11.2013)
Get full text
Journal Article
Pathogenesis of mitral valve disease in mucopolysaccharidosis VII dogs
Bigg, Paul W., Baldo, Guilherme, Sleeper, Meg M., O'Donnell, Patricia A., Bai, Hanqing, Rokkam, Venkata R.P., Liu, Yuli, Wu, Susan, Giugliani, Roberto, Casal, Margret L., Haskins, Mark E., Ponder, Katherine P.
Published in Molecular genetics and metabolism (01.11.2013)
Published in Molecular genetics and metabolism (01.11.2013)
Get full text
Journal Article
Therapeutic Neonatal Hepatic Gene Therapy in Mucopolysaccharidosis VII Dogs
Ponder, Katherine Parker, Melniczek, John R., Xu, Lingfei, Weil, Margaret A., O'Malley, Thomas M., O'Donnell, Patricia A., Knox, Van W., Aguirre, Gustavo D., Mazrier, Hamutal, Ellinwood, N. Matthew, Sleeper, Meg, Maguire, Albert M., Volk, Susan W., Mango, Robert L., Zweigle, Jean, Wolfe, John H., Haskins, Mark E.
Published in Proceedings of the National Academy of Sciences - PNAS (01.10.2002)
Published in Proceedings of the National Academy of Sciences - PNAS (01.10.2002)
Get full text
Journal Article
Global CNS correction in a large brain model of human alpha-mannosidosis by intravascular gene therapy
Yoon, Sea Young, Hunter, Jacqueline E, Chawla, Sanjeev, Clarke, Dana L, Molony, Caitlyn, O'Donnell, Patricia A, Bagel, Jessica H, Kumar, Manoj, Poptani, Harish, Vite, Charles H, Wolfe, John H
Published in Brain (London, England : 1878) (01.07.2020)
Published in Brain (London, England : 1878) (01.07.2020)
Get full text
Journal Article
Expression in blood cells may contribute to biochemical and pathological improvements after neonatal intravenous gene therapy for mucopolysaccharidosis VII in dogs
Wang, Bin, O’Malley, Thomas M., Xu, Lingfei, Vite, Charles, Wang, Ping, O’Donnell, Patricia A., Ellinwood, N. Matthew, Haskins, Mark E., Ponder, Katherine Parker
Published in Molecular genetics and metabolism (2006)
Published in Molecular genetics and metabolism (2006)
Get full text
Journal Article
AAVrh10 Gene Therapy Ameliorates Central and Peripheral Nervous System Disease in Canine Globoid Cell Leukodystrophy (Krabbe Disease)
Bradbury, Allison M, Rafi, Mohammed A, Bagel, Jessica H, Brisson, Becky K, Marshall, Michael S, Pesayco Salvador, Jill, Jiang, Xuntain, Swain, Gary P, Prociuk, Maria L, ODonnell, Patricia A, Fitzgerald, Caitlin, Ory, Daniel S, Bongarzone, Ernesto R, Shelton, G Diane, Wenger, David A, Vite, Charles H
Published in Human gene therapy (01.07.2018)
Published in Human gene therapy (01.07.2018)
Get more information
Journal Article
Clinical, electrophysiological, and biochemical markers of peripheral and central nervous system disease in canine globoid cell leukodystrophy (Krabbe's disease)
Bradbury, Allison M., Bagel, Jessica H., Jiang, Xuntian, Swain, Gary P., Prociuk, Maria L., Fitzgerald, Caitlin A., O'Donnell, Patricia A., Braund, Kyle G., Ory, Daniel S., Vite, Charles H.
Published in Journal of neuroscience research (01.11.2016)
Published in Journal of neuroscience research (01.11.2016)
Get full text
Journal Article
The effect of neonatal gene therapy on skeletal manifestations in mucopolysaccharidosis VII dogs after a decade
Xing, Elizabeth M., Knox, Van W., O'Donnell, Patricia A., Sikura, Tracey, Liu, Yuli, Wu, Susan, Casal, Margret L., Haskins, Mark E., Ponder, Katherine P.
Published in Molecular genetics and metabolism (01.06.2013)
Published in Molecular genetics and metabolism (01.06.2013)
Get full text
Journal Article
Neonatal Gene Therapy With a Gamma Retroviral Vector in Mucopolysaccharidosis VI Cats
Ponder, Katherine P, O'Malley, Thomas M, Wang, Ping, O'Donnell, Patricia A, Traas, Anne M, Knox, Van W, Aguirre, Gustavo A, Ellinwood, N Matthew, Metcalf, Jason A, Wang, Bin, Parkinson-Lawrence, Emma J, Sleeper, Meg M, Brooks, Doug A, Hopwood, John J, Haskins, Mark E
Published in Molecular therapy (01.05.2012)
Published in Molecular therapy (01.05.2012)
Get full text
Journal Article
Clinician Perceptions of a Changing Hospital Environment
Maguire, Denise J., Burger, Kristina J., O'Donnell, Patricia A., Parnell, Lisa
Published in HERD (01.04.2013)
Published in HERD (01.04.2013)
Get full text
Journal Article
Cerebrospinal fluid and serum glycosphingolipid biomarkers in canine globoid cell leukodystrophy (Krabbe Disease)
Corado, Carley R., Pinkstaff, Jason, Jiang, Xuntian, Galban, Evelyn M., Fisher, Samantha J., Scholler, Oriane, Russell, Chris, Bagel, Jessica H., ODonnell, Patricia A., Ory, Daniel S., Vite, Charles H., Bradbury, Allison M.
Published in Molecular and cellular neuroscience (01.01.2020)
Published in Molecular and cellular neuroscience (01.01.2020)
Get full text
Journal Article
Transduction of Hepatocytes after Neonatal Delivery of a Moloney Murine Leukemia Virus Based Retroviral Vector Results in Long-Term Expression of β-Glucuronidase in Mucopolysaccharidosis VII Dogs
Xu, Lingfei, Haskins, Mark E, Melniczek, John R, Gao, Cuihua, Weil, Margaret A, O'Malley, Thomas M, O'Donnell, Patricia A, Mazrier, Hamutal, Ellinwood, N Matthew, Zweigle, Jean, Wolfe, John H, Ponder, Katherine Parker
Published in Molecular therapy (01.02.2002)
Published in Molecular therapy (01.02.2002)
Get full text
Journal Article
Identification of the Identical Human Mutation in ACVR1 in 2 Cats With Fibrodysplasia Ossificans Progressiva
Casal, Margret L., Engiles, Julie B., Zakošek Pipan, Maja, Berkowitz, Asaf, Porat-Mosenco, Yael, Mai, Wilfried, Wurzburg, Kirsten, Xu, Mei-Qi, Allen, Robyn, ODonnell, Patricia A., Henthorn, Paula S., Thompson, Keith, Shore, Eileen M.
Published in Veterinary pathology (01.07.2019)
Published in Veterinary pathology (01.07.2019)
Get full text
Journal Article
13. Post-Symptomatic Intrathecal Infusion of AAV1 Results in Reversal of Storage Lesions Throughout the Brain in the Cat Model of Alpha-Mannnosidosis Leading To Clinical Improvement
Young Yoon, Sea, Bagel, Jessica H., Kumar, Manoj, O'Donnell, Patricia A., Poptani, Harish, Vite, Charles H., Wolfe, John H.
Published in Molecular therapy (01.05.2015)
Published in Molecular therapy (01.05.2015)
Get full text
Journal Article
Urinary glycosaminoglycan concentration as a biomarker for effectiveness of enzyme replacement and gene therapy in large animal models of mucopolysaccharidoses
Casal, Margret L., Wang, Ping, ODonnell, Patricia A., Sikora, Tracey, Langan, Therese, O'Malley, Thomas, Ferla, Rita, Auricchio, Alberto, Wilson, James M., Gao, Guangping, Ponder, Katherine, Haskins, Mark E.
Published in Molecular genetics and metabolism (01.02.2016)
Published in Molecular genetics and metabolism (01.02.2016)
Get full text
Journal Article
Transduction of Hepatocytes after Neonatal Delivery of a Moloney Murine Leukemia Virus Based Retroviral Vector Results in Long-Term Expression of [beta]-Glucuronidase in Mucopolysaccharidosis VII Dogs
Xu, Lingfei, Haskins, Mark E, Melniczek, John R, Gao, Cuihua, Weil, Margaret A, O'malley, Thomas M, O'donnell, Patricia A, Mazrier, Hamutal, Ellinwood, N Matthew, Zweigle, Jean, Wolfe, John H, Ponder, Katherine Parker
Published in Molecular therapy (01.02.2002)
Published in Molecular therapy (01.02.2002)
Get full text
Journal Article
Transfusion of 28 Day-Old Leukoreduced or Non-Leukoreduced Stored Red Blood Cells Induces an Inflammatory Response in Healthy Dogs
Callan, Mary Beth, Patel, Reema T., Rux, Ann H., Bandyopadhyay, Sheila, Sireci, Anthony N., O’Donnell, Patricia A., Ruane, Therese, Sikora, Tracey, Marryott, Kimberly, Sachais, Bruce S., Hod, Eldad A.
Published in Vox sanguinis (13.06.2013)
Published in Vox sanguinis (13.06.2013)
Get full text
Journal Article