Short antisense oligonucleotides alleviate the pleiotropic toxicity of RNA harboring expanded CGG repeats
Derbis, Magdalena, Kul, Emre, Niewiadomska, Daria, Sekrecki, Michał, Piasecka, Agnieszka, Taylor, Katarzyna, Hukema, Renate K, Stork, Oliver, Sobczak, Krzysztof
Published in Nature communications (24.02.2021)
Published in Nature communications (24.02.2021)
Get full text
Journal Article
Cyclic mismatch binding ligands interact with disease-associated CGG trinucleotide repeats in RNA and suppress their translation
Konieczny, Patryk, Mukherjee, Sanjukta, Stepniak-Konieczna, Ewa, Taylor, Katarzyna, Niewiadomska, Daria, Piasecka, Agnieszka, Walczak, Agnieszka, Baud, Anna, Dohno, Chikara, Nakatani, Kazuhiko, Sobczak, Krzysztof
Published in Nucleic acids research (20.09.2021)
Published in Nucleic acids research (20.09.2021)
Get full text
Journal Article