Quality of life in thalassemia: A comparison of SF‐36 results from the thalassemia longitudinal cohort to reported literature and the US norms
Sobota, A., Yamashita, R., Xu, Y., Trachtenberg, F., Kohlbry, P., Kleinert, D.A., Giardina, P.J., Kwiatkowski, J.L., Foote, D., Thayalasuthan, V., Porter, J.B., Thompson, A.A., Schilling, L., Quinn, C.T., Neufeld, E.J.
Published in American journal of hematology (01.01.2011)
Published in American journal of hematology (01.01.2011)
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Journal Article
Pre-transplantation iron chelation in patients with MDS or acute leukemia and iron overload undergoing myeloablative allo-SCT
ARMAND, P, SAINVIL, M.-M, SOIFFER, R. J, ANTIN, J. H, KIM, H. T, RHODES, J, CUTLER, C, HO, V. T, KORETH, J, ALYEA, E. P, NEUFELD, E. J, KWONG, R. Y
Published in Bone marrow transplantation (Basingstoke) (01.01.2013)
Published in Bone marrow transplantation (Basingstoke) (01.01.2013)
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Journal Article
Deletion of SLC19A2, the high affinity thiamine transporter, causes selective inner hair cell loss and an auditory neuropathy phenotype
Liberman, M C, Tartaglini, E, Fleming, J C, Neufeld, E J
Published in Journal of the Association for Research in Otolaryngology (01.09.2006)
Published in Journal of the Association for Research in Otolaryngology (01.09.2006)
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Journal Article
The gene mutated in thiamine-responsive anaemia with diabetes and deafness (TRMA) encodes a functional thiamine transporter
Neufeld, Ellis J, Fleming, Judith C, Tartaglini, Elena, Steinkamp, Mara P, Schorderet, Daniel F, Cohen, Nadine
Published in Nature genetics (01.07.1999)
Published in Nature genetics (01.07.1999)
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Journal Article
Combined schedule of 7-valent pneumococcal conjugate vaccine followed by 23-valent pneumococcal vaccine in children and young adults with sickle cell disease
Vernacchio, Louis, Neufeld, Ellis J., MacDonald, Kristin, Kurth, Susan, Murakami, Saya, Hohne, Courtney, King, Michelle, Molrine, Deborah
Published in The Journal of pediatrics (01.08.1998)
Published in The Journal of pediatrics (01.08.1998)
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Journal Article
Rituximab for adolescents with haemophilia and high titre inhibitors
FOX, R. A., NEUFELD, E. J., BENNETT, C. M.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2006)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2006)
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Journal Article
Transition considerations for extended half-life factor products
Croteau, S. E., Neufeld, E. J.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2015)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2015)
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Journal Article
Recognizing the need for personalization of haemophilia patient-reported outcomes in the prophylaxis era
Recht, M., Konkle, B. A., Jackson, S., Neufeld, E. J., Rockwood, K., Pipe, S.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2016)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2016)
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Journal Article
Immunogenicity, efficacy and safety of Nuwiq® (human‐cl rhFVIII) in previously untreated patients with severe haemophilia A—Interim results from the NuProtect Study
Liesner, R. J., Abashidze, M., Aleinikova, O., Altisent, C., Belletrutti, M. J., Borel‐Derlon, A., Carcao, M., Chambost, H., Chan, A. K. C., Dubey, L., Ducore, J., Fouzia, N. A., Gattens, M., Gruel, Y., Guillet, B., Kavardakova, N., El Khorassani, M., Klukowska, A., Lambert, T., Lohade, S., Sigaud, M., Turea, V., Wu, J. K. M., Vdovin, V., Pavlova, A., Jansen, M., Belyanskaya, L., Walter, O., Knaub, S., Neufeld, E. J.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2018)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2018)
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Journal Article
Mechanism of thiamine uptake by human colonocytes: studies with cultured colonic epithelial cell line NCM460
Said, H M, Ortiz, A, Subramanian, V S, Neufeld, E J, Moyer, M P, Dudeja, P K
Published in American journal of physiology: Gastrointestinal and liver physiology (01.07.2001)
Published in American journal of physiology: Gastrointestinal and liver physiology (01.07.2001)
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Journal Article
Correlation between dispensed and prescribed doses of factor products for bleeding disorders: can a small, centre-based pharmacy hit the mark?
Croteau, S. E., Saxena, K., Neufeld, E. J.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2015)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2015)
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Journal Article
Perioperative management of haemophilia B: A critical appraisal of the evidence and current practices
Neufeld, E. J., Solimeno, L., Quon, D., Walsh, C., Seremetis, S., Cooper, D., Iyer, N. N., Hoxer, C. S., Giangrande, P.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2017)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2017)
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Journal Article
Recombinant porcine factor VIII for high‐risk surgery in paediatric congenital haemophilia A with high‐titre inhibitor
Croteau, S. E., Abajas, Y. L., Wolberg, A. S., Nielsen, B. I., Marx, G. R., Baird, C. W., Neufeld, E. J., Monahan, P. E.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2017)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2017)
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Journal Article
Recombinant activated factor VII in approved indications: Update on safety
Neufeld, E. J., Négrier, C., Benchikh el Fegoun, S., Cooper, D. L., Rojas‐Rios, A., Seremetis, S.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.07.2018)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.07.2018)
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Journal Article
The use of a single von Willebrand factor‐containing, plasma‐derived FVIII product in hemophilia A immune tolerance induction: the US experience
KURTH, M., PUETZ, J., KOUIDES, P., SANDERS, J., SEXAUER, C., BERNSTEIN, J., GRUPPO, R., MANCO‐JOHNSON, M., NEUFELD, E. J., RODRIGUEZ, N., WICKLUND, B., QUON, D., ALEDORT, L.
Published in Journal of thrombosis and haemostasis (01.11.2011)
Published in Journal of thrombosis and haemostasis (01.11.2011)
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Journal Article
Coagulation Abnormalities in Pediatric and Adult Patients After Sclerotherapy or Embolization of Vascular Anomalies
Mason, Keira P, Neufeld, Ellis J, Karian, Victoria E, Zurakowski, David, Koka, Babu V, Burrows, Patricia E
Published in American journal of roentgenology (1976) (01.12.2001)
Published in American journal of roentgenology (1976) (01.12.2001)
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Journal Article
Asparaginase-associated lipid abnormalities in children with acute lymphoblastic leukemia
PARSONS, S. K, SKAPEK, S. X, NEUFELD, E. J, KUHLMAN, C, YOUNG, M. L, DONNELLY, M, BRUNZELL, J. D, OTVOS, J. D, SALLAN, S. E, RIFAI, N
Published in Blood (15.03.1997)
Published in Blood (15.03.1997)
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Journal Article
Safety of recombinant activated factor VII (rFVIIa) in patients with congenital haemophilia with inhibitors: overall rFVIIa exposure and intervals following high (>240 μg kg−1) rFVIIa doses across clinical trials and registries
Shapiro, A. D., Neufeld, E. J., Blanchette, V., Salaj, P., Gut, R. Z., Cooper, D. L.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2014)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2014)
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Journal Article