Development of an inducible anti-VEGF rAAV gene therapy strategy for the treatment of wet AMD
Reid, Christopher A, Nettesheim, Emily R, Connor, Thomas B, Lipinski, Daniel M
Published in Scientific reports (06.08.2018)
Published in Scientific reports (06.08.2018)
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Journal Article
Presynaptic Expression of LRIT3 Transsynaptically Organizes the Postsynaptic Glutamate Signaling Complex Containing TRPM1
Hasan, Nazarul, Pangeni, Gobinda, Cobb, Catherine A, Ray, Thomas A, Nettesheim, Emily R, Ertel, Kristina J, Lipinski, Daniel M, McCall, Maureen A, Gregg, Ronald G
Published in Cell reports (Cambridge) (11.06.2019)
Published in Cell reports (Cambridge) (11.06.2019)
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Journal Article
Prostaglandin-based rAAV-mediated glaucoma gene therapy in Brown Norway rats
Chern, Kristina J, Nettesheim, Emily R, Reid, Christopher A, Li, Nathan W, Marcoe, Gavin J, Lipinski, Daniel M
Published in Communications biology (03.11.2022)
Published in Communications biology (03.11.2022)
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Journal Article
A Destabilizing Domain Allows for Fast, Noninvasive, Conditional Control of Protein Abundance in the Mouse Eye - Implications for Ocular Gene Therapy
Datta, Shyamtanu, Renwick, Marian, Chau, Viet Q, Zhang, Fang, Nettesheim, Emily R, Lipinski, Daniel M, Hulleman, John D
Published in Investigative ophthalmology & visual science (01.10.2018)
Published in Investigative ophthalmology & visual science (01.10.2018)
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Journal Article
Improved Cardiac Function in Postischemic Rats Using an Optimized Cardiac Reprogramming Cocktail Delivered in a Single Novel Adeno-Associated Virus
Zhou, Huanyu, Yang, Jin, Srinath, Chetan, Zeng, Aliya, Wu, Iris, Leon, Elena C., Qureshi, Tawny Neal, Reid, Christopher A., Nettesheim, Emily R., Xu, Emma, Duclos, Zoe, Mohamed, Tamer M.A., Farshidfar, Farshad, Fejes, Anthony, Liu, Jun, Jones, Samantha, Feathers, Charles, Chung, Tae Won, Jing, Frank, Prince, William S., Lin, JianMin, Yu, Pengzhi, Srivastava, Deepak, Hoey, Timothy, Ivey, Kathryn N., Lombardi, Laura M.
Published in Circulation (New York, N.Y.) (03.10.2023)
Published in Circulation (New York, N.Y.) (03.10.2023)
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Journal Article
A candidate activation pathway for coagulation factor VII
Misenheimer, Tina M, Kumfer, Kraig T, Bates, Barbara E, Nettesheim, Emily R, Schwartz, Bradford S
Published in Biochemical journal (15.10.2019)
Published in Biochemical journal (15.10.2019)
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Journal Article
Long-term progression of retinal degeneration in a preclinical model of CLN7 Batten disease as a baseline for testing clinical therapeutics
Rowe, Ashley A., Chen, Xin, Nettesheim, Emily R., Issioui, Yacine, Dong, Thomas, Hu, Yuhui, Messahel, Souad, Kayani, Saima N., Gray, Steven J., Wert, Katherine J.
Published in EBioMedicine (01.11.2022)
Published in EBioMedicine (01.11.2022)
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Journal Article
Abstract 543: Clinical Development of Cardiac Reprogramming Gene Therapy
Zhou, Huanyu, Lombardi, Laura M, Reid, Christopher A, Yang, Jin, Srinath, Chetan, Zeng, Aliya, Leon, Elena C, Qureshi, Tawny N, Nettesheim, Emily R, Xu, Emma, Duclos, Zoe, Liu, Jun, Jones, Samantha, Feathers, Charles, Chung, Tae Won, Jing, Frank, Prince, William, Lin, JianMin, Hoey, Timothy, Ivey, Kathryn
Published in Circulation research (31.07.2020)
Published in Circulation research (31.07.2020)
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Long-term progression of retinal degeneration in a preclinical model of CLN7 Batten disease as a baseline for testing clinical therapeuticsResearch in context
Ashley A. Rowe, Xin Chen, Emily R. Nettesheim, Yacine Issioui, Thomas Dong, Yuhui Hu, Souad Messahel, Saima N. Kayani, Steven J. Gray, Katherine J. Wert
Published in EBioMedicine (01.11.2022)
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Published in EBioMedicine (01.11.2022)
Journal Article
Neuronal Ceroid Lipofuscinoses Type 7 (CLN7)- A Case Series Reporting Cross Sectional and Retrospective Clinical Data to Evaluate Validity of Standardized Tools to Assess Disease Progression, Quality of Life, and Adaptive Skills
Kayani, Saima, Edgar, Veronica Bordes, Lowden, Andrea, Nettesheim, Emily R, Dahshi, Hamza, Messahel, Souad, Minassian, Berge A, Greenberg, Benjamin M
Published in Research square (26.06.2024)
Published in Research square (26.06.2024)
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