G.P.104
Naryshkin, N.A, Dakka, A, Gabbeta, V, Pichardo, J, Woll, M.G, Zhang, N, Karp, G.M, Welch, E.M
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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Journal Article
P3.12 Small molecule compounds that correct alternative splicing of the SMN2 gene and restore SMN protein expression and function
Naryshkin, N.A, Narasimhan, J, Dakka, A, Gabbeta, V, Haley, M, Crona, J, Jung, S, Vazirani, P, Furia, B, Qi, H, Woll, M, Yang, T, Lee, S, Choi, S, Chen, G, Zhang, S, Zhang, N, Huang, S, Li, C, Turpoff, A, Hedrick, J, Zhao, X, Mollin, A, Letinski, S, Risher, N, Paushkin, S, Kobayashi, D, McCarthy, K, Pleiss, M, Chen, K, Almstead, N, Colacino, J, Babiak, J, Peltz, S, Karp, G, Weetall, M, Welch, E.M
Published in Neuromuscular disorders : NMD (01.10.2011)
Published in Neuromuscular disorders : NMD (01.10.2011)
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Journal Article
G.P.104: Oral small molecule compounds that promote the skipping of exon 51 in the DMD gene
Naryshkin, N.A., Dakka, A., Gabbeta, V., Pichardo, J., Woll, M.G., Zhang, N., Karp, G.M., Welch, E.M.
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
Get full text
Journal Article