Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
Mendell, Jerry R, Al-Zaidy, Samiah, Shell, Richard, Arnold, W. Dave, Rodino-Klapac, Louise R, Prior, Thomas W, Lowes, Linda, Alfano, Lindsay, Berry, Katherine, Church, Kathleen, Kissel, John T, Nagendran, Sukumar, L’Italien, James, Sproule, Douglas M, Wells, Courtney, Cardenas, Jessica A, Heitzer, Marjet D, Kaspar, Allan, Corcoran, Sarah, Braun, Lyndsey, Likhite, Shibi, Miranda, Carlos, Meyer, Kathrin, Foust, K.D, Burghes, Arthur H.M, Kaspar, Brian K
Published in The New England journal of medicine (02.11.2017)
Published in The New England journal of medicine (02.11.2017)
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Journal Article
Impact of Age and Motor Function in a Phase 1/2A Study of Infants With SMA Type 1 Receiving Single-Dose Gene Replacement Therapy
Lowes, Linda P., Alfano, Lindsay N., Arnold, W. David, Shell, Richard, Prior, Thomas W., McColly, Markus, Lehman, Kelly J., Church, Kathleen, Sproule, Douglas M., Nagendran, Sukumar, Menier, Melissa, Feltner, Douglas E., Wells, Courtney, Kissel, John T., Al-Zaidy, Samiah, Mendell, Jerry
Published in Pediatric neurology (01.09.2019)
Published in Pediatric neurology (01.09.2019)
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Journal Article
AVXS-101 (Onasemnogene Abeparvovec) for SMA1: Comparative Study with a Prospective Natural History Cohort
Al-Zaidy, Samiah A., Kolb, Stephen J., Lowes, Linda, Alfano, Lindsay N., Shell, Richard, Church, Kathleen R., Nagendran, Sukumar, Sproule, Douglas M., Feltner, Douglas E., Wells, Courtney, Ogrinc, Francis, Menier, Melissa, L’Italien, James, Arnold, W. David, Kissel, John T., Kaspar, Brian K., Mendell, Jerry R.
Published in Journal of neuromuscular diseases (2019)
Published in Journal of neuromuscular diseases (2019)
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Journal Article
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
Mendell, Jerry R., Al-Zaidy, Samiah, Shell, Richard, Arnold, W. Dave, Rodino-Klapac, Louise R., Prior, Thomas W., Lowes, Linda, Alfano, Lindsay, Berry, Katherine, Church, Kathleen, Kissel, John T., Nagendran, Sukumar, L’Italien, James, Sproule, Douglas M., Wells, Courtney, Cardenas, Jessica A., Heitzer, Marjet D., Kaspar, Allan, Corcoran, Sarah, Braun, Lyndsey, Likhite, Shibi, Miranda, Carlos, Meyer, Kathrin, Foust, K.D., Burghes, Arthur H.M., Kaspar, Brian K.
Published in The New England journal of medicine (02.11.2017)
Published in The New England journal of medicine (02.11.2017)
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Journal Article
Impact of metformin-induced gastrointestinal symptoms on quality of life and adherence in patients with type 2 diabetes
Florez, Hermes, Luo, Jiacong, Castillo-Florez, Sumaya, Mitsi, Georgia, Hanna, John, Tamariz, Leonardo, Palacio, Ana, Nagendran, Sukumar, Hagan, Michael
Published in Postgraduate medicine (01.03.2010)
Published in Postgraduate medicine (01.03.2010)
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Journal Article
AVXS-101 Phase 1 gene therapy clinical trial in SMA Type 1: Interim data demonstrates improvements in supportive care use
Shell, Richard, Al-Zaidy, Samiah, Arnold, W. Dave, Rodino-Klapac, Louise, Prior, Thomas W, Lowes, Linda, Alfano, Lindsay, Berry, Katherine, Church, Kathleen, Kissel, John T, Nagendran, Sukumar, L'Italien, James, Sproule, Douglas M, Burghes, Arthur H.M, Foust, K.D, Meyer, Kathrin, Likhite, Shibi, Kaspar, Brian K, Mendell, Jerry R
Published in European journal of paediatric neurology (01.06.2017)
Published in European journal of paediatric neurology (01.06.2017)
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Journal Article
Concomitant reduction in low-density lipoprotein cholesterol and glycated hemoglobin with colesevelam hydrochloride in patients with type 2 diabetes: a pooled analysis
Jialal, Ishwarlal, Abby, Stacey L, Misir, Soamnauth, Nagendran, Sukumar
Published in Metabolic syndrome and related disorders (01.06.2009)
Published in Metabolic syndrome and related disorders (01.06.2009)
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Journal Article
AVXS-101 Phase 1 gene therapy clinical trial in SMA Type 1: Event free survival and achievement of developmental milestones
Mendell, Jerry R, Al-Zaidy, Samiah, Shell, Richard, Arnold, W. David, Rodino-Klapac, Louise, Prior, Thomas W, Lowes, Linda, Alfano, Lindsay, Berry, Katherine, Church, Kathleen, Kissel, John T, Nagendran, Sukumar, L'Italien, James, Sproule, Douglas M, Cardenas, Jessica, Burghes, Arthur H.M, Foust, K.D, Meyer, Kathrin, Likhite, Shibi, Kaspar, Brian K
Published in European journal of paediatric neurology (01.06.2017)
Published in European journal of paediatric neurology (01.06.2017)
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Journal Article
Colesevelam hydrochloride to treat hypercholesterolemia and improve glycemia in prediabetes: a randomized, prospective study
Handelsman, Yehuda, Goldberg, Ronald B, Garvey, W Timothy, Fonseca, Vivian A, Rosenstock, Julio, Jones, Michael R, Lai, Yu-Ling, Jin, Xiaoping, Misir, Soamnauth, Nagendran, Sukumar, Abby, Stacey L
Published in Endocrine practice (01.07.2010)
Published in Endocrine practice (01.07.2010)
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Journal Article
The effect of colesevelam hydrochloride on insulin sensitivity and secretion in patients with type 2 diabetes: a pilot study
Schwartz, Sherwyn L, Lai, Yu-Ling, Xu, Jianbo, Abby, Stacey L, Misir, Soamnauth, Jones, Michael R, Nagendran, Sukumar
Published in Metabolic syndrome and related disorders (01.04.2010)
Published in Metabolic syndrome and related disorders (01.04.2010)
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Journal Article
Initial combination therapy with metformin plus colesevelam in drug-naïve Hispanic patients with early type 2 diabetes
Rosenstock, Julio, Hernandez-Triana, Eric, Handelsman, Yehuda, Misir, Soamnauth, Jones, Michael R, Nagendran, Sukumar
Published in Postgraduate medicine (01.07.2012)
Published in Postgraduate medicine (01.07.2012)
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Journal Article
Initial combination therapy with metformin and colesevelam for achievement of glycemic and lipid goals in early type 2 diabetes
Rosenstock, Julio, Fonseca, Vivian A, Garvey, W Timothy, Goldberg, Ronald B, Handelsman, Yehuda, Abby, Stacey L, Lai, Yu-Ling, Jin, Xiaoping, Misir, Soamnauth, Nagendran, Sukumar, Jones, Michael R
Published in Endocrine practice (01.07.2010)
Published in Endocrine practice (01.07.2010)
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Journal Article
Rationale and design of a clinical trial to evaluate metformin and colesevelam HCl as first-line therapy in type 2 diabetes and colesevelam HCl in prediabetes
Jones, Michael R, Mudaliar, Sunder, Hernandez-Triana, Eric, Unnikrishnan, Ambika G, Lai, Yu-Ling, Abby, Stacey L, Misir, Soamnauth, Jin, Xiaoping, Nagendran, Sukumar
Published in Current medical research and opinion (01.09.2009)
Published in Current medical research and opinion (01.09.2009)
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Journal Article
Initial Combination Therapy with Metformin and Colesevelam for Achievement of Glycemic and Lipid Goals Min Early Type 2 Diabetes
Rosenstock, Julio, Fonseca, Vivian A., Garvey, W. Timothy, Goldberg, Ronald B., Handelsman, Yehuda, Abby, Stacey L., Lai, Yu-Ling, Jin, Xiaoping, Misir, Soamnauth, Nagendran, Sukumar, Jones, Michael R.
Published in Endocrine practice (01.07.2010)
Published in Endocrine practice (01.07.2010)
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Journal Article
Colesevelam HCl to Treat Hypercholesterolemia and Improve Glycemia in Prediabetes: A Randomized, Prospective Study
Misir, Sam, PharmD, Handelsman, Yehuda, Garvey, Timothy W, Fonseca, Vivian A, Rosenstock, Julio, Jones, Michael R, Lai, Yu-Ling, Jin, Xiaoping, Nagendran, Sukumar, Abby, Stacey L
Published in Journal of clinical lipidology (2010)
Published in Journal of clinical lipidology (2010)
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Journal Article