Burosumab versus conventional therapy in children with X-linked hypophosphataemia: a randomised, active-controlled, open-label, phase 3 trial
Imel, Erik A, Glorieux, Francis H, Whyte, Michael P, Munns, Craig F, Ward, Leanne M, Nilsson, Ola, Simmons, Jill H, Padidela, Raja, Namba, Noriyuki, Cheong, Hae Il, Pitukcheewanont, Pisit, Sochett, Etienne, Högler, Wolfgang, Muroya, Koji, Tanaka, Hiroyuki, Gottesman, Gary S, Biggin, Andrew, Perwad, Farzana, Mao, Meng, Chen, Chao-Yin, Skrinar, Alison, San Martin, Javier, Portale, Anthony A
Published in The Lancet (British edition) (15.06.2019)
Published in The Lancet (British edition) (15.06.2019)
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Global Consensus Recommendations on Prevention and Management of Nutritional Rickets
Munns, Craig F, Shaw, Nick, Kiely, Mairead, Specker, Bonny L, Thacher, Tom D, Ozono, Keiichi, Michigami, Toshimi, Tiosano, Dov, Mughal, M. Zulf, Mäkitie, Outi, Ramos-Abad, Lorna, Ward, Leanne, DiMeglio, Linda A, Atapattu, Navoda, Cassinelli, Hamilton, Braegger, Christian, Pettifor, John M, Seth, Anju, Idris, Hafsatu Wasagu, Bhatia, Vijayalakshmi, Fu, Junfen, Goldberg, Gail, Sävendahl, Lars, Khadgawat, Rajesh, Pludowski, Pawel, Maddock, Jane, Hyppönen, Elina, Oduwole, Abiola, Frew, Emma, Aguiar, Magda, Tulchinsky, Ted, Butler, Gary, Högler, Wolfgang
Published in The journal of clinical endocrinology and metabolism (01.02.2016)
Published in The journal of clinical endocrinology and metabolism (01.02.2016)
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Effect of Burosumab Compared With Conventional Therapy on Younger vs Older Children With X-linked Hypophosphatemia
Ward, Leanne M, Glorieux, Francis H, Whyte, Michael P, Munns, Craig F, Portale, Anthony A, Hogler, Wolfgang, Simmons, Jill H, Gottesman, Gary S, Padidela, Raja, Namba, Noriyuki, Cheong, Hae Il, Nilsson, Ola, Mao, Meng, Chen, Angel, Skrinar, Alison, Roberts, Mary Scott, Imel, Erik A
Published in The journal of clinical endocrinology and metabolism (01.08.2022)
Published in The journal of clinical endocrinology and metabolism (01.08.2022)
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Fracture prediction and the definition of osteoporosis in children and adolescents: the ISCD 2013 Pediatric Official Positions
Bishop, Nick, Arundel, Paul, Clark, Emma, Dimitri, Paul, Farr, Joshua, Jones, Graeme, Makitie, Outi, Munns, Craig F, Shaw, Nick
Published in Journal of clinical densitometry (01.04.2014)
Published in Journal of clinical densitometry (01.04.2014)
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Consensus guidelines on the use of bisphosphonate therapy in children and adolescents
Simm, Peter J, Biggin, Andrew, Zacharin, Margaret R, Rodda, Christine P, Tham, Elaine, Siafarikas, Aris, Jefferies, Craig, Hofman, Paul L, Jensen, Diane E, Woodhead, Helen, Brown, Justin, Wheeler, Benjamin J, Brookes, Denise, Lafferty, Antony, Munns, Craig F
Published in Journal of paediatrics and child health (01.03.2018)
Published in Journal of paediatrics and child health (01.03.2018)
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Mutations in SLC34A3/NPT2c are associated with kidney stones and nephrocalcinosis
Dasgupta, Debayan, Wee, Mark J, Reyes, Monica, Li, Yuwen, Simm, Peter J, Sharma, Amita, Schlingmann, Karl-Peter, Janner, Marco, Biggin, Andrew, Lazier, Joanna, Gessner, Michaela, Chrysis, Dionisios, Tuchman, Shamir, Baluarte, H Jorge, Levine, Michael A, Tiosano, Dov, Insogna, Karl, Hanley, David A, Carpenter, Thomas O, Ichikawa, Shoji, Hoppe, Bernd, Konrad, Martin, Sävendahl, Lars, Munns, Craig F, Lee, Hang, Jüppner, Harald, Bergwitz, Clemens
Published in Journal of the American Society of Nephrology (01.10.2014)
Published in Journal of the American Society of Nephrology (01.10.2014)
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Risedronate in children with osteogenesis imperfecta: a randomised, double-blind, placebo-controlled trial
Bishop, Nick, Prof, Adami, Silvano, MD, Ahmed, S Faisal, MD, Antón, Jordi, MD, Arundel, Paul, MD, Burren, Christine P, MD, Devogelaer, Jean-Pierre, MD, Hangartner, Thomas, PhD, Hosszú, Eva, MD, Lane, Joseph M, MD, Lorenc, Roman, MD, Mäkitie, Outi, MD, Munns, Craig F, MD, Paredes, Ana, MD, Pavlov, Helene, MD, Plotkin, Horacio, MD, Raggio, Cathleen L, MD, Reyes, Maria Loreto, MD, Schoenau, Eckhard, MD, Semler, Oliver, MD, Sillence, David O, MD, Steiner, Robert D, MD
Published in The Lancet (British edition) (26.10.2013)
Published in The Lancet (British edition) (26.10.2013)
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Burosumab vs Phosphate/Active Vitamin D in Pediatric X-Linked Hypophosphatemia: A Subgroup Analysis by Dose Level
Imel, Erik A, Glorieux, Francis H, Whyte, Michael P, Portale, Anthony A, Munns, Craig F, Nilsson, Ola, Simmons, Jill H, Padidela, Raja, Namba, Noriyuki, Cheong, Hae Il, Pitukcheewanont, Pisit, Sochett, Etienne, Högler, Wolfgang, Muroya, Koji, Tanaka, Hiroyuki, Gottesman, Gary S, Biggin, Andrew, Perwad, Farzana, Chen, Angel, Roberts, Mary Scott, Ward, Leanne M
Published in The journal of clinical endocrinology and metabolism (18.10.2023)
Published in The journal of clinical endocrinology and metabolism (18.10.2023)
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Patient-Reported Outcomes from a Randomized, Active-Controlled, Open-Label, Phase 3 Trial of Burosumab Versus Conventional Therapy in Children with X-Linked Hypophosphatemia
Padidela, Raja, Whyte, Michael P., Glorieux, Francis H., Munns, Craig F., Ward, Leanne M., Nilsson, Ola, Portale, Anthony A., Simmons, Jill H., Namba, Noriyuki, Cheong, Hae Il, Pitukcheewanont, Pisit, Sochett, Etienne, Högler, Wolfgang, Muroya, Koji, Tanaka, Hiroyuki, Gottesman, Gary S., Biggin, Andrew, Perwad, Farzana, Williams, Angela, Nixon, Annabel, Sun, Wei, Chen, Angel, Skrinar, Alison, Imel, Erik A.
Published in Calcified tissue international (01.05.2021)
Published in Calcified tissue international (01.05.2021)
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P450 Oxidoreductase Deficiency: A Systematic Review and Meta-analysis of Genotypes, Phenotypes, and Their Relationships
Dean, Benjamin, Chrisp, Georgina L, Quartararo, Maria, Maguire, Ann M, Hameed, Shihab, King, Bruce R, Munns, Craig F, Torpy, David J, Falhammar, Henrik, Rushworth, R Louise
Published in The journal of clinical endocrinology and metabolism (01.03.2020)
Published in The journal of clinical endocrinology and metabolism (01.03.2020)
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Variations in the management of acute illness in children with congenital adrenal hyperplasia: An audit of three paediatric hospitals
Chrisp, Georgina L., Maguire, Ann M., Quartararo, Maria, Falhammar, Henrik, King, Bruce R., Munns, Craig F., Torpy, David J., Hameed, Shihab, Rushworth, R. Louise
Published in Clinical endocrinology (Oxford) (01.11.2018)
Published in Clinical endocrinology (Oxford) (01.11.2018)
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Burosumab Versus Phosphate/Active Vitamin D in Pediatric X-Linked Hypophosphatemia: A Sub-group Analysis by Dose Level
Imel, Erik A, Glorieux, Francis H, Whyte, Michael P, Portale, Anthony A, Munns, Craig F, Nilsson, Ola, Simmons, Jill H, Padidela, Raja, Namba, Noriyuki, Cheong, Hae Il, Pitukcheewanont, Pisit, Sochett, Etienne, Högler, Wolfgang, Muroya, Koji, Tanaka, Hiroyuki, Gottesman, Gary S, Biggin, Andrew, Perwad, Farzana, Chen, Angel, Roberts, Mary Scott, Ward, Leanne M
Published in The journal of clinical endocrinology and metabolism (2023)
Published in The journal of clinical endocrinology and metabolism (2023)
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The effect of patient‐managed stress dosing on electrolytes and blood pressure in acute illness in children with adrenal insufficiency
Chrisp, Georgina L, Torpy, David J, Maguire, Ann M, Quartararo, Maria, Falhammar, Henrik, King, Bruce R, Munns, Craig F, Hameed, Shihab, Rushworth, R Louise
Published in Clinical endocrinology (Oxford) (01.08.2020)
Published in Clinical endocrinology (Oxford) (01.08.2020)
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Burosumab vs conventional therapy in children with X-linked hypophosphatemia: results of the open-label, phase 3 extension period
Ward, Leanne M, Högler, Wolfgang, Glorieux, Francis H, Portale, Anthony A, Whyte, Michael P, Munns, Craig F, Nilsson, Ola, Simmons, Jill H, Padidela, Raja, Namba, Noriyuki, Cheong, Hae Il, Sochett, Etienne, Muroya, Koji, Tanaka, Hiroyuki, Pitukcheewanont, Pisit, Gottesman, Gary S, Biggin, Andrew, Perwad, Farzana, Chen, Angel, Lawrence Merritt Ii, John, Imel, Erik A
Published in JBMR plus (2024)
Published in JBMR plus (2024)
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In Pediatric X-linked Hypophosphatemia (XLH), Burosumab Improved Clinical Outcomes Versus Higher and Lower Doses of Oral Phosphate and/or Active Vitamin D
Imel, EA, Glorieux, FH, Whyte, MP, Portale, AA, Munns, CF, Nilsson, O, Simmons, JH, Padidela, R, Namba, N, Cheong, HI, Pitukcheewanont, P, Sochett, E, Hogler, W, Muroya, K, Tanaka, H, Gottesman, GS, Biggin, A, Perwad, F, Chen, A, Roberts, MS, Ward, L
Published in JOURNAL OF BONE AND MINERAL RESEARCH (2020)
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Published in JOURNAL OF BONE AND MINERAL RESEARCH (2020)
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