Ten years of the international Pompe survey: patient reported outcomes as a reliable tool for studying treated and untreated children and adults with non-classic Pompe disease
van der Meijden, J. C., Güngör, D., Kruijshaar, M. E., Muir, A. D. J., Broekgaarden, H. A., van der Ploeg, A. T.
Published in Journal of inherited metabolic disease (01.05.2015)
Published in Journal of inherited metabolic disease (01.05.2015)
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Journal Article
Ten Years of the International Pompe Survey: Patient-Reported Outcomes as a Reliable Tool for Studying Treated and Untreated Children and Adults with Non-Classic Pompe Disease
van der Meijden, J.C., Güngör, D., Kruijshaar, M.E., Muir, A.D.J., Broekgaarden, H.A., van der Ploeg, A.T.
Published in Journal of neuromuscular diseases (2015)
Published in Journal of neuromuscular diseases (2015)
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Journal Article