Psychometric validation of the Hypoparathyroidism Patient Experience Scales (HPES)
Brod, Meryl, McLeod, Lori, Markova, Denka, Gianettoni, Jill, Mourya, Sanchita, Lin, Zhengning, Shu, Aimee, Smith, Alden
Published in Journal of patient-reported outcomes (10.08.2021)
Published in Journal of patient-reported outcomes (10.08.2021)
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Journal Article
Design and topline results of TransCon PTH, a long-acting PTH, phase 2 trial in patients with hypoparathyroidism
Karpf, David B., Mourya, Sanchita, Khan, Aliya, Rejnmark, Lars
Published in Bone Reports (01.10.2020)
Published in Bone Reports (01.10.2020)
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Journal Article
Week 26 results from the PaTH Forward Open-Label Extension Trial Support TransCon PTH as a potential hormone replacement therapy for patients with hypoparathyroidism
Rejnmark, Lars, Schwarz, Peter, Rubin, Mishaela, Vokes, Tamara, Clarke, Bart, Ahmed, Intekhab, Palermo, Andrea, Marcocci, Claudio, Pagotto, Uberto, Eriksen, Erik, Mourya, Sanchita, Markova, Denka, Pihl, Susanne, Beckert, Michael, Shu, Aimee, Khan, Aliya
Published in Bone Reports (01.04.2021)
Published in Bone Reports (01.04.2021)
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Journal Article
BMF-219: A Novel Therapeutic Agent to Reestablish Functional Beta Cells and Provide Long-Term Glycemic Control
Frias, Juan P., Mourya, Sanchita, Munneke, Brian, Balakrishnan, Mini, Somanath, Priyanka, Butler, Thomas
Published in Metabolism, clinical and experimental (01.06.2024)
Published in Metabolism, clinical and experimental (01.06.2024)
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Journal Article
901-P: COVALENT 112-A Clinical Trial Assessing BMF-219, an Oral Covalent Menin Inhibitor in Type 1 Diabetes
Tran, Hien T, Katselnik, Daniel, Denham, Douglas S, Stevens-Brogan, Michelle K, Decker, Carl W, Mourya, Sanchita, Frias, Juan P, Butler, Thomas, Guzman, Cristina B
Published in Diabetes (New York, N.Y.) (01.06.2024)
Published in Diabetes (New York, N.Y.) (01.06.2024)
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Journal Article
A Randomized Double‐Blind Placebo‐Controlled First‐In‐Human Phase 1 Trial of TransCon PTH in Healthy Adults
Karpf, David B, Pihl, Susanne, Mourya, Sanchita, Mortensen, Eva, Kovoor, Eshwari, Markova, Denka, Leff, Jonathan A
Published in Journal of bone and mineral research (01.08.2020)
Published in Journal of bone and mineral research (01.08.2020)
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Journal Article
Covalent-103: A Phase 1, Open-Label, Dose-Escalation, and Dose-Expansion Study of Bmf-500, an Oral Covalent FLT3 Inhibitor, in Adults with Acute Leukemia (AL)
Rotta, Marcello, Ravandi, Farhad, Gandhi, Mitul, Koller, Paul B., Schiller, Gary J., Follit, Courtney, Vimal, Mona, Morris, Stephan W., Mourya, Sanchita, Butler, Thomas, Wang, Eunice S.
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
91-LB: COVALENT-111, a Phase 1/2 Trial of BMF-219, a Covalent Menin Inhibitor, in Patients with Type 2 Diabetes Mellitus—Preliminary Results
RODRIGUEZ, JOSE E., ABITBOL, ALEXANDER, ABUZGAYA, FATHI, PEREZ, CESAR, MOURYA, SANCHITA, MUNNEKE, BRIAN, MORRIS, STEPHAN W., BUTLER, THOMAS
Published in Diabetes (New York, N.Y.) (20.06.2023)
Published in Diabetes (New York, N.Y.) (20.06.2023)
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Journal Article
PaTH Forward: A Randomized, Double-Blind, Placebo-Controlled Phase 2 Trial of TransCon PTH in Adult Hypoparathyroidism
Khan, Aliya A, Rejnmark, Lars, Rubin, Mishaela, Schwarz, Peter, Vokes, Tamara, Clarke, Bart, Ahmed, Intekhab, Hofbauer, Lorenz, Marcocci, Claudio, Pagotto, Uberto, Palermo, Andrea, Eriksen, Erik, Brod, Meryl, Markova, Denka, Smith, Alden, Pihl, Susanne, Mourya, Sanchita, Karpf, David B, Shu, Aimee D
Published in The journal of clinical endocrinology and metabolism (01.01.2022)
Published in The journal of clinical endocrinology and metabolism (01.01.2022)
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Journal Article
113-LB: Oral Menin Inhibitor, BMF-219, Displays a Significant and Durable Reduction in HbA1c in a Type 2 Diabetes Mellitus Rat Model
SOMANATH, PRIYANKA, MOURYA, SANCHITA, LI, WEIQUN, ARCHER, TENLEY C., LAW, BRIAN, LU, DANIEL, RUGHWANI, TRIPTA, KUMAR, LEKHA, KINOSHITA, TAISEI, BALAKRISHNAN, MINI, BUTLER, THOMAS
Published in Diabetes (New York, N.Y.) (01.06.2022)
Published in Diabetes (New York, N.Y.) (01.06.2022)
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Journal Article
P-269: COVALENT-101: a Phase 1 study of BMF-219, a novel oral covalent menin inhibitor, in patients with relapsed/refractory (R/R) acute leukemia, diffuse large B-cell lymphoma, and multiple myeloma
Ravandi, Farhad, Carraway, Hetty, Khouri, Jack, Kishtagari, Ashwin, Curran, Emily, Schiller, Gary, Yadav, Bhagyashree (Kelshikar), Morris, Steve, Cacovean, Alex, Mourya, Sanchita, Butler, Thomas, Lancet, Jeffrey
Published in Clinical lymphoma, myeloma and leukemia (01.08.2022)
Published in Clinical lymphoma, myeloma and leukemia (01.08.2022)
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Journal Article
Acalabrutinib monotherapy in patients (pts) with relapsed/refractory (R/R) diffuse large B-cell lymphoma (DLBCL)
Dyer, Martin JS, De Vos, Sven, Ruan, Jia, Flowers, Christopher, Maddocks, Kami J., Rule, Simon, Hamdy, Ahmed M., Izumi, Raquel, Slatter, J. Greg, Cheung, Jean, Frigualt, Melanie M., Wei, Helen, Mourya, Sanchita, Hunder, Naomi N. H., Fowler, Nathan Hale
Published in Journal of clinical oncology (20.05.2018)
Published in Journal of clinical oncology (20.05.2018)
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Journal Article
Disease Burden of Patients Living With Hypoparathyroidism: Results From the Voices of Hypopara Survey
Murphy, Deborah, Sanders, Bob, Gulley, Loretta, Knoefler, Ami, Smith, Alden, Park, Minyoung, Tsao, Susana, Mourya, Sanchita, Rubin, Mishaela
Published in Journal of the Endocrine Society (03.05.2021)
Published in Journal of the Endocrine Society (03.05.2021)
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Journal Article
TransCon PTH as a Hormone Replacement Therapy for Patients with Hypoparathyroidism: 6-Month Update from the PaTH Forward Open-Label Extension
Rubin, Mishaela R, Rejnmark, Lars, Schwarz, Peter E, Vokes, Tamara J, Clarke, Bart, Ahmed, Intekhab, Hofbauer, Lorenz C, Palermo, Andrea, Marcocci, Claudio, Pagotto, Uberto, Eriksen, Erik F, Mourya, Sanchita, Markova, Denka, Pihl, Susanne, Shu, Aimee D, Khan, Aliya
Published in Journal of the Endocrine Society (03.05.2021)
Published in Journal of the Endocrine Society (03.05.2021)
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Journal Article
SAT-LB72 Design of the PaTH Forward Phase 2 Trial of TransCon PTH, a Long-Acting PTH, in Patients With Hypoparathyroidism
Khan, Aliya Aziz, Rejnmark, Lars, Schwarz, Peter E, Vokes, Tamara J, Clarke, Bart Lyman, Rubin, Mishaela Ruth, Hofbauer, Lorenz C, Erikson, Erik, Palermo, Andrea, Pagotto, Uberto, Marcocci, Claudio, Ahmed, Intekhab, Mourya, Sanchita, Markova, Denka, Karpf, David B
Published in Journal of the Endocrine Society (08.05.2020)
Published in Journal of the Endocrine Society (08.05.2020)
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Journal Article