Generation of gene-corrected functional osteoclasts from osteopetrotic induced pluripotent stem cells
Xian, Xiaojie, Moraghebi, Roksana, Löfvall, Henrik, Fasth, Anders, Henriksen, Kim, Richter, Johan, Woods, Niels-Bjarne, Moscatelli, Ilana
Published in Stem cell research & therapy (15.05.2020)
Published in Stem cell research & therapy (15.05.2020)
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Journal Article
Gene therapy for infantile malignant osteopetrosis: review of pre-clinical research and proof-of-concept for phenotypic reversal
Moscatelli, Ilana, Almarza, Elena, Schambach, Axel, Ricks, David, Schulz, Ansgar, Herzog, Christopher D., Henriksen, Kim, Askmyr, Maria, Schwartz, Jonathan D., Richter, Johan
Published in Molecular therapy. Methods & clinical development (12.03.2021)
Published in Molecular therapy. Methods & clinical development (12.03.2021)
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Journal Article
Transcriptome sequencing identifies a noncoding, deep intronic variant in CLCN7 causing autosomal recessive osteopetrosis
Chorin, Odelia, Yachelevich, Naomi, Mohamed, Khaled, Moscatelli, Ilana, Pappas, John, Henriksen, Kim, Evrony, Gilad D.
Published in Molecular genetics & genomic medicine (01.10.2020)
Published in Molecular genetics & genomic medicine (01.10.2020)
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Journal Article
A Comparison of Osteoclast-Rich and Osteoclast-Poor Osteopetrosis in Adult Mice Sheds Light on the Role of the Osteoclast in Coupling Bone Resorption and Bone Formation
Thudium, Christian S., Moscatelli, Ilana, Flores, Carmen, Thomsen, Jesper S., Brüel, Annemarie, Gudmann, Natasja Stæhr, Hauge, Ellen-Margrethe, Karsdal, Morten A., Richter, Johan, Henriksen, Kim
Published in Calcified tissue international (01.07.2014)
Published in Calcified tissue international (01.07.2014)
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Journal Article
A specific subtype of osteoclasts secretes factors inducing nodule formation by osteoblasts
Henriksen, Kim, Andreassen, Kim V, Thudium, Christian S, Gudmann, Karoline N.S, Moscatelli, Ilana, Crüger-Hansen, Catherine E, Schulz, Ansgar S, Dziegiel, Morten H, Richter, Johan, Karsdal, Morten A, Neutzsky-Wulff, Anita V
Published in Bone (New York, N.Y.) (01.09.2012)
Published in Bone (New York, N.Y.) (01.09.2012)
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Journal Article
Osteoclasts are not crucial for hematopoietic stem cell maintenance in adult mice
Flores, Carmen, Moscatelli, Ilana, Thudium, Christian S, Gudmann, Natasja Stæhr, Thomsen, Jesper S, Brüel, Annemarie, Karsdal, Morten A, Henriksen, Kim, Richter, Johan
Published in Haematologica (Roma) (01.12.2013)
Published in Haematologica (Roma) (01.12.2013)
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Journal Article
Hematopoietic Stem Cell-Targeted Neonatal Gene Therapy with a Clinically Applicable Lentiviral Vector Corrects Osteopetrosis in oc/oc Mice
Löfvall, Henrik, Rothe, Michael, Schambach, Axel, Henriksen, Kim, Richter, Johan, Moscatelli, Ilana
Published in Human gene therapy (01.11.2019)
Published in Human gene therapy (01.11.2019)
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Journal Article
Targeting NSG Mice Engrafting Cells with a Clinically Applicable Lentiviral Vector Corrects Osteoclasts in Infantile Malignant Osteopetrosis
Moscatelli, Ilana, Löfvall, Henrik, Schneider Thudium, Christian, Rothe, Michael, Montano, Carmen, Kertész, Zsuzsanna, Sirin, Mehtap, Schulz, Ansgar, Schambach, Axel, Henriksen, Kim, Richter, Johan
Published in Human gene therapy (01.08.2018)
Published in Human gene therapy (01.08.2018)
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Journal Article
Regulation and Function of Lentiviral Vector-Mediated TCIRG1 Expression in Osteoclasts from Patients with Infantile Malignant Osteopetrosis: Implications for Gene Therapy
Thudium, Christian Schneider, Moscatelli, Ilana, Löfvall, Henrik, Kertész, Zsuzsanna, Montano, Carmen, Bjurström, Carmen Flores, Karsdal, Morten Asser, Schulz, Ansgar, Richter, Johan, Henriksen, Kim
Published in Calcified tissue international (01.12.2016)
Published in Calcified tissue international (01.12.2016)
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Journal Article
Lentiviral gene transfer of TCIRG1 into peripheral blood CD34+ cells restores osteoclast function in infantile malignant osteopetrosis
Moscatelli, Ilana, Thudium, Christian Schneider, Flores, Carmen, Schulz, Ansgar, Askmyr, Maria, Gudmann, Natasja Stæhr, Andersen, Nanna Merete, Porras, Oscar, Karsdal, Morten Asser, Villa, Anna, Fasth, Anders, Henriksen, Kim, Richter, Johan
Published in Bone (New York, N.Y.) (01.11.2013)
Published in Bone (New York, N.Y.) (01.11.2013)
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Journal Article
Forced expression of human macrophage colony‐stimulating factor in CD34+ cells promotes monocyte differentiation in vitro and in vivo but blunts osteoclastogenesis in vitro
Montano Almendras, Carmen P., Thudium, Christian S., Löfvall, Henrik, Moscatelli, Ilana, Schambach, Axel, Henriksen, Kim, Richter, Johan
Published in European journal of haematology (01.05.2017)
Published in European journal of haematology (01.05.2017)
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Journal Article
Leptin attenuates ischemia-reperfusion injury in the rat liver
Carbone, Marco, Campagnolo, Luisa, Angelico, Mario, Tisone, Giuseppe, Almerighi, Cristiana, Telesca, Claudia, Lenci, Ilaria, Moscatelli, Ilana, Massoud, Renato, Baiocchi, Leonardo
Published in Transplant international (01.12.2012)
Published in Transplant international (01.12.2012)
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Journal Article
Gene Transfer to CD34+ Cells From Peripheral Blood Restores Osteoclast Function in Infantile Malignant Osteopetrosis
Moscatelli, Ilana, Thudium, Christian, Askmyr, Maria, Schulz, Ansgar S, Porras, Oscar, Fasth, Anders, Henriksen, Kim, Richter, Johan
Published in Blood (18.11.2011)
Published in Blood (18.11.2011)
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Journal Article
Leptin attenuates ischemia-reperfusion injury in the rat liver: Leptin and liver ischemia
Carbone, Marco, Campagnolo, Luisa, Angelico, Mario, Tisone, Giuseppe, Almerighi, Cristiana, Telesca, Claudia, Lenci, Ilaria, Moscatelli, Ilana, Massoud, Renato, Baiocchi, Leonardo
Published in Transplant international (01.12.2012)
Published in Transplant international (01.12.2012)
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Journal Article
Expression of EGFL7 in primordial germ cells and in adult ovaries and testes
Campagnolo, Luisa, Moscatelli, Ilana, Pellegrini, Manuela, Siracusa, Gregorio, Stuhlmann, Heidi
Published in Gene Expression Patterns (01.07.2008)
Published in Gene Expression Patterns (01.07.2008)
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Journal Article
Nonablative neonatal bone marrow transplantation rapidly reverses severe murine osteopetrosis despite low‐level engraftment and lack of selective expansion of the osteoclastic lineage
Flores, Carmen, de Vries, Teun J, Moscatelli, Ilana, Askmyr, Maria, Schoenmaker, Ton, Langenbach, Geerling EJ, Ehinger, Mats, Everts, Vincent, Richter, Johan
Published in Journal of bone and mineral research (01.09.2010)
Published in Journal of bone and mineral research (01.09.2010)
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Journal Article
Electrospun poly(ε-caprolactone)/Ca-deficient hydroxyapatite nanohybrids: Microstructure, mechanical properties and cell response by murine embryonic stem cells
Bianco, Alessandra, Di Federico, Erica, Moscatelli, Ilana, Camaioni, Antonella, Armentano, Ilaria, Campagnolo, Luisa, Dottori, Mariaserena, Kenny, Josè Maria, Siracusa, Gregorio, Gusmano, Gualtiero
Published in Materials Science & Engineering C (01.08.2009)
Published in Materials Science & Engineering C (01.08.2009)
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Journal Article
Regulation and function of lentiviral-mediated TCIRG1 expression in osteoclasts from infantile malignant osteopetrosis patients
Lofvall, Henrik, Thudium, Christian Schneider, Moscatelli, Ilana, Montano, Carmen, Schulz, Ansgar, Richter, Johan, Henriksen, Kim
Published in Bone Abstracts (21.04.2016)
Published in Bone Abstracts (21.04.2016)
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