AAV9-DOK7 gene therapy reduces disease severity in Smn2B/- SMA model mice
Kaifer, Kevin A., Villalón, Eric, Smith, Caley E., Simon, Madeline E., Marquez, Jose, Hopkins, Abigail E., Morcos, Toni I., Lorson, Christian L.
Published in Biochemical and biophysical research communications (10.09.2020)
Published in Biochemical and biophysical research communications (10.09.2020)
Get full text
Journal Article
AAV9-DOK7 gene therapy reduces disease severity in Smn SMA model mice
Kaifer, Kevin A., Villalón, Eric, Smith, Caley E., Simon, Madeline E., Marquez, Jose, Hopkins, Abigail E., Morcos, Toni I., Lorson, Christian L.
Published in Biochemical and biophysical research communications (10.09.2020)
Published in Biochemical and biophysical research communications (10.09.2020)
Get full text
Journal Article
AAV9-DOK7 gene therapy reduces disease severity in Smn 2B/- SMA model mice
Kaifer, Kevin A, Villalón, Eric, Smith, Caley E, Simon, Madeline E, Marquez, Jose, Hopkins, Abigail E, Morcos, Toni I, Lorson, Christian L
Published in Biochemical and biophysical research communications (10.09.2020)
Get full text
Published in Biochemical and biophysical research communications (10.09.2020)
Journal Article