Pathogenesis of SCA3 and implications for other polyglutamine diseases
McLoughlin, Hayley S., Moore, Lauren R., Paulson, Henry L.
Published in Neurobiology of disease (01.02.2020)
Published in Neurobiology of disease (01.02.2020)
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Journal Article
Oligonucleotide therapy mitigates disease in spinocerebellar ataxia type 3 mice
McLoughlin, Hayley S., Moore, Lauren R., Chopra, Ravi, Komlo, Robert, McKenzie, Megan, Blumenstein, Kate G., Zhao, Hien, Kordasiewicz, Holly B., Shakkottai, Vikram G., Paulson, Henry L.
Published in Annals of neurology (01.07.2018)
Published in Annals of neurology (01.07.2018)
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Journal Article
Evaluation of Antisense Oligonucleotides Targeting ATXN3 in SCA3 Mouse Models
Moore, Lauren R., Rajpal, Gautam, Dillingham, Ian T., Qutob, Maya, Blumenstein, Kate G., Gattis, Danielle, Hung, Gene, Kordasiewicz, Holly B., Paulson, Henry L., McLoughlin, Hayley S.
Published in Molecular therapy. Nucleic acids (16.06.2017)
Published in Molecular therapy. Nucleic acids (16.06.2017)
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Journal Article
Derivation of spinocerebellar ataxia type 3 human embryonic stem cell line UMICHe001-A/UM134-1
Moore, Lauren R., Keller, Laura, Paulson, Henry L., Smith, Gary D.
Published in Stem cell research (01.10.2022)
Published in Stem cell research (01.10.2022)
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Journal Article
Antisense oligonucleotide therapy rescues aggresome formation in a novel spinocerebellar ataxia type 3 human embryonic stem cell line
Moore, Lauren R., Keller, Laura, Bushart, David D., Delatorre, Rodrigo G., Li, Duojia, McLoughlin, Hayley S., do Carmo Costa, Maria, Shakkottai, Vikram G., Smith, Gary D., Paulson, Henry L.
Published in Stem cell research (01.08.2019)
Published in Stem cell research (01.08.2019)
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Journal Article
Comparison of spinocerebellar ataxia type 3 mouse models identifies early gain-of-function, cell-autonomous transcriptional changes in oligodendrocytes
Ramani, Biswarathan, Panwar, Bharat, Moore, Lauren R, Wang, Bo, Huang, Rogerio, Guan, Yuanfang, Paulson, Henry L
Published in Human molecular genetics (01.09.2017)
Published in Human molecular genetics (01.09.2017)
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Journal Article
Fatigue Impacts Quality of Life in People with Spinocerebellar Ataxias
Lai, Ruo-Yah, Rummey, Christian, Amlang, Christian J, Lin, Chi-Ying R, Chen, Tiffany X, Perlman, Susan, Wilmot, George, Gomez, Christopher M, Schmahmann, Jeremy D, Paulson, Henry, Ying, Sarah H, Onyike, Chiadi U, Zesiewicz, Theresa A, Bushara, Khalaf O, Geschwind, Michael D, Figueroa, Karla P, Pulst, Stefan M, Subramony, Sub H, Burns, Matthew R, Opal, Puneet, Duquette, Antoine, Ashizawa, Tetsuo, Hamedani, Ali G, Davis, Marie Y, Srinivasan, Sharan R, Moore, Lauren R, Shakkottai, Vikram G, Rosenthal, Liana S, Kuo, Sheng-Han
Published in Movement disorders clinical practice (Hoboken, N.J.) (01.05.2024)
Published in Movement disorders clinical practice (Hoboken, N.J.) (01.05.2024)
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Journal Article
Antisense oligonucleotide therapy rescues aggresome formation in a novel Spinocerebellar Ataxia type 3 human embryonic stem cell line
Moore, Lauren R, Keller, Laura, Bushart, David D, Delatorre, Rodrigo, Li, Duojia, Mcloughlin, Hayley, Do Carmo Costa, Maria, Shakkottai, Vikram G, Smith, Gary D, Paulson, Henry L
Published in bioRxiv (24.06.2019)
Published in bioRxiv (24.06.2019)
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