Prevalence and pharmacological modulation of humoral immunity to AAV vectors in gene transfer to synovial tissue
Mingozzi, F, Chen, Y, Edmonson, S C, Zhou, S, Thurlings, R M, Tak, P P, High, K A, Vervoordeldonk, M J
Published in Gene therapy (01.04.2013)
Published in Gene therapy (01.04.2013)
Get full text
Journal Article
Photo-activated raster scanning thermal imaging at sub-diffraction resolution
Bouzin, M, Marini, M, Zeynali, A, Borzenkov, M, Sironi, L, D'Alfonso, L, Mingozzi, F, Granucci, F, Pallavicini, P, Chirico, G, Collini, M
Published in Nature communications (04.12.2019)
Published in Nature communications (04.12.2019)
Get full text
Journal Article
High AAV vector purity results in serotype- and tissue-independent enhancement of transduction efficiency
Ayuso, E, Mingozzi, F, Montane, J, Leon, X, Anguela, X M, Haurigot, V, Edmonson, S A, Africa, L, Zhou, S, High, K A, Bosch, F, Wright, J F
Published in Gene therapy (01.04.2010)
Published in Gene therapy (01.04.2010)
Get full text
Journal Article
Exosome-associated AAV vector as a robust and convenient neuroscience tool
Hudry, E, Martin, C, Gandhi, S, György, B, Scheffer, D I, Mu, D, Merkel, S F, Mingozzi, F, Fitzpatrick, Z, Dimant, H, Masek, M, Ragan, T, Tan, S, Brisson, A R, Ramirez, S H, Hyman, B T, Maguire, C A
Published in Gene therapy (01.04.2016)
Published in Gene therapy (01.04.2016)
Get full text
Journal Article
Muscle‐specific, liver‐detargeted adeno‐associated virus gene therapy rescues Pompe phenotype in adult and neonate Gaa−/− mice
Sellier, P., Vidal, P., Bertin, B., Gicquel, E., Bertil‐Froidevaux, E., Georger, C., Wittenberghe, L., Miranda, A., Daniele, N., Richard, I., Gross, D. A., Mingozzi, F., Collaud, F., Ronzitti, G.
Published in Journal of inherited metabolic disease (01.01.2024)
Published in Journal of inherited metabolic disease (01.01.2024)
Get full text
Journal Article
μMAPPS: a novel phasor approach to second harmonic analysis for in vitro-in vivo investigation of collagen microstructure
Radaelli, F, D'Alfonso, L, Collini, M, Mingozzi, F, Marongiu, L, Granucci, F, Zanoni, I, Chirico, G, Sironi, L
Published in Scientific reports (12.12.2017)
Published in Scientific reports (12.12.2017)
Get full text
Journal Article
Author Correction: μMAPPS: a novel phasor approach to second harmonic analysis for in vitro-in vivo investigation of collagen microstructure
Radaelli, F, D'Alfonso, L, Collini, M, Mingozzi, F, Marongiu, L, Granucci, F, Zanoni, I, Chirico, G, Sironi, L
Published in Scientific reports (17.04.2018)
Published in Scientific reports (17.04.2018)
Get full text
Journal Article
Exosome-associated AAV vector as a robust and convenient neuroscience tool
Hudry, E, Martin, C, Gandhi, S, György, B, Scheffer, D I, Mu, D, Merkel, S F, Mingozzi, F, Fitzpatrick, Z, Dimant, H, Masek, M, Ragan, T, Tan, S, Brisson, A R, Ramirez, S H, Hyman, B T, Maguire, C A
Published in Gene therapy (01.11.2016)
Published in Gene therapy (01.11.2016)
Get full text
Journal Article
Erratum: Exosome-associated AAV vector as a robust and convenient neuroscience tool
Hudry, E, Martin, C, Gandhi, S, György, B, Scheffer, D I, Mu, D, Merkel, S F
Published in Gene therapy (01.11.2016)
Published in Gene therapy (01.11.2016)
Get full text
Journal Article
Major role of local immune responses in antibody formation to factor IX in AAV gene transfer
WANG, L, CAO, O, SWALM, B, DOBRZYNSKI, E, MINGOZZI, F, HERZOG, R. W
Published in Gene therapy (01.10.2005)
Published in Gene therapy (01.10.2005)
Get full text
Journal Article
T.P.21
Masat, E, Laforet, P, Amelin, D, Veron, P, Laloui, K, Benveniste, O, Mingozzi, F
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
Get full text
Journal Article
Cytokine and chemokine profiling shows rapid activation of the immune system following enzyme replacement therapy in Pompe disease
Masat, E, Laforêt, P, Amelin, D, Veron, P, Perniconi, B, Taouagh, N, Benveniste, O, Mingozzi, F
Published in Neuromuscular disorders : NMD (01.10.2015)
Published in Neuromuscular disorders : NMD (01.10.2015)
Get full text
Journal Article
P1213 : Adeno-associated virus vector-mediated liver gene therapy for Crigler-Najjar syndrome
Bosma, P, Labrune, P, Brunetti-Pierri, N, D’Antiga, L, Ott, M, Beinat, M, Ronchi, F, Mavilio, F, Beuers, U, Muro, A, Baumann, U, Mingozzi, F
Published in Journal of hepatology (01.04.2015)
Published in Journal of hepatology (01.04.2015)
Get full text
Journal Article
Prolonged benefit from systemic rAAV8 in a canine model of myotubular myopathy
Elverman, M, Mack, D, Poulard, K, Goddard, M, Snyder, J, Grange, R, Latournerie, V, Veron, P, Meng, H, Mingozzi, F, Lawlor, M, Beggs, A, Childers, M, Buj-Bello, A
Published in Neuromuscular disorders : NMD (01.10.2016)
Published in Neuromuscular disorders : NMD (01.10.2016)
Get full text
Journal Article
Towards gene therapy for the treatment of rheumatoid arthritis: production and bioactivity of interferon in fibroblast-like synoviocytes transduced with adeno-associated virus type 5 expressing human interferon
Aalbers, C. J., Loiler, S. A., Mingozzi, F., Tak, P. P., Vervoordeldonk, M. J.
Published in Annals of the rheumatic diseases (01.03.2011)
Published in Annals of the rheumatic diseases (01.03.2011)
Get full text
Journal Article
Peripheral vein injection of AAV8-MTM1 leads to long-term survival and correction of severe muscle pathology in a canine model of X-linked myotubular myopathy: Results from a dose escalation study
Mack, D, Poulard, K, Goddard, M, Snyder, J, Grange, R, Doering, J, Strande, J, Latournerie, V, Veron, P, Yang, L, Buscara, L, Le Bec, C, Martin, S, O'Callaghan, M, Mingozzi, F, Beggs, A, Lawlor, M, Mavilio, F, Childers, M, Buj-Bello, A
Published in Neuromuscular disorders : NMD (01.10.2015)
Published in Neuromuscular disorders : NMD (01.10.2015)
Get full text
Journal Article
Natural history and functional status of patients with myotubular myopathy enrolled in a prospective and longitudinal study
R'guiba, N, Annoussamy, M, Cardas, R, Lilien, C, Ollivier, G, Muntoni, F, Bönnemann, C, Biancalana, V, Cuisset, J, Mayer, M, Landy, H, Ramsdell, D, Nelken, M, Le Moing, A, Gidaro, T, Mingozzi, F, Buj-Bello, A, Hogrel, J.Y, Voit, T, Servais, L
Published in Neuromuscular disorders : NMD (01.10.2015)
Published in Neuromuscular disorders : NMD (01.10.2015)
Get full text
Journal Article
Adeno-associated virus vector (AAV) microdystrophin gene therapy prolongs survival and restores muscle function in the canine model of Duchenne muscular dystrophy (DMD)
Le Guiner, C, Servais, L, Montus, M, Bodvael, F, Gjata, B, Hogrel, J.Y, Carlier, P, Moullec, S, Masurier, C, Adjali, O, Mingozzi, F, Koo, T, Athanasopoulos, T, Cherel, Y, Mavilio, F, Voit, T, Moullier, P, Dickson, G
Published in Neuromuscular disorders : NMD (2015)
Published in Neuromuscular disorders : NMD (2015)
Get full text
Journal Article