LB952 A phase 1 trial of DSG3-CAART cells in mucosal-dominant pemphigus vulgaris (mPV) patients: Preliminary data
Chang, D.J., Basu, S., Micheletti, R., Maverakis, E., Marinkovich, M., Porter, D.L., Abedi, M., Weng, W., Hoffman, K., Volkov, J., Nunez, D., Milone, M.C., Binder, G.K., Payne, A.S.
Published in Journal of investigative dermatology (01.08.2022)
Published in Journal of investigative dermatology (01.08.2022)
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564 Preclinical rationale for a first-in-human trial to evaluate the safety and preliminary efficacy of desmoglein 3 chimeric autoantibody receptor T cells (DSG3-CAART) for mucosal pemphigus vulgaris
Payne, A.S., Lee, J., Lundgren, D.K., Mao, X., Manfredo-Vieira, S., Nunez-Cruz, S., Williams, E.F., Assenmacher, C., Radaelli, E., Wang, B., Ellebrecht, C.T., Fraietta, J.A., Milone, M.C.
Published in Journal of investigative dermatology (01.07.2020)
Published in Journal of investigative dermatology (01.07.2020)
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035 Temporally controlled B cell depletion with universal chimeric antigen receptor (CAR) T cells for pemphigus vulgaris (PV) therapy
Ellebrecht, C.T., Mao, X., Melenhorst, J.J., Lacey, S., Zhao, Y., Milone, M.C., Payne, A.S.
Published in Journal of investigative dermatology (01.05.2017)
Published in Journal of investigative dermatology (01.05.2017)
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Novel media formulations to enhance Chimeric Antigen Receptor (CAR) T-cell potency and anti-tumor cell function for adoptive immunotherapy
Ghassemi, S., Martinez-Becerra, F., Master, A., Richman, S.A., Heo, D., Leferovich, J., Tu, Y., Garcia-Canaveras, J.C., Ayari, A., Lu, Y., Wang, A., Rabinowitz, J.D., Milone, M.C., O'Connor, R.
Published in Cytotherapy (Oxford, England) (01.05.2020)
Published in Cytotherapy (Oxford, England) (01.05.2020)
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Iv Busulfan Administered Q12 Vs Q6 Hrs During Conditioning of Pediatric Allogeneic Stem Cell Transplant (AlloSCT) Recipients Has Comparable Pharmacokinetics and Significant Reduction in Nursing/Pharmacist Costs
LeGall, J, Milone, M.C, Waxman, I.M, Shaw, L.M, Harrison, L, Duffy, D, Militano, O, Bhatia, M, Satwani, P, George, D, Garvin, J.H, Bradley, M.B, van de Ven, C, Cairo, M.S
Published in Biology of blood and marrow transplantation (2011)
Published in Biology of blood and marrow transplantation (2011)
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Twice-Daily Intravenous (IV) Busulfan (Bu) x 4 Days In Children Undergoing Allogeneic Hematopoietic Stem Cell Transplantation (AlloHSCT) is Pharmacokinetically Similar to Q6 Hour Dosing in the Pediatric Population
Waxman, I, Milone, M.C, Bhatia, M, Shaw, L, Moore, V, Tallamy, B, Militano, O, Garvin, J.H, George, D, Bradley, M.B, Satwani, P, Schwartz, J, Wolownik, K, Foley, S, Hawks, R, Baxter-Lowe, L.A, van de Ven, C, Cairo, M.S
Published in Biology of blood and marrow transplantation (01.02.2009)
Published in Biology of blood and marrow transplantation (01.02.2009)
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A pilot study of reduced toxicity conditioning with BU, fludarabine and alemtuzumab before the allogeneic hematopoietic SCT in children and adolescents
STYCZYNSKI, J, TALLAMY, B, GEORGE, D, BRADLEY, M. B, GARVIN, J. H, SCHWARTZ, J, BAXTER-LOWE, L. A, CAIRO, M. S, WAXMAN, I, VAN DE VEN, C, MILONE, M. C, SHAW, L. M, HARRISON, L, MORRIS, E, SATWANI, P, BHATIA, M
Published in Bone marrow transplantation (Basingstoke) (01.06.2011)
Published in Bone marrow transplantation (Basingstoke) (01.06.2011)
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Pharmacokinetic targeting of i.v. BU with fludarabine as conditioning before hematopoietic cell transplant: the effect of first-dose area under the concentration time curve on transplant-related outcomes
PERKINS, J, FIELD, T, MILONE, M. C, GARDINER, J. A, MILLER, S, ANASETTI, C, KIM, J, KHARFAN-DABAJA, M. A, AYALA, E, PEREZ, L, FERNANDEZ, H, FANCHER, K, TATE, C, SHAW, L. M
Published in Bone marrow transplantation (Basingstoke) (01.11.2011)
Published in Bone marrow transplantation (Basingstoke) (01.11.2011)
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The pharmacokinetics and safety of twice daily i.v. BU during conditioning in pediatric allo-SCT recipients
LE GALL, J. B, MILONE, M. C, BHATIA, M, SATWANI, P, GEORGE, D, GARVIN, J. H, BRADLEY, M. B, SCHWARTZ, J, BAXTER-LOWE, L. A, CAIRO, M. S, WAXMAN, I. M, SHAW, L. M, HARRISON, L, DUFFY, D, DE VEN, C. Van, MILITANO, O, GEYER, M. B, MORRIS, E
Published in Bone marrow transplantation (Basingstoke) (01.01.2013)
Published in Bone marrow transplantation (Basingstoke) (01.01.2013)
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