Long-Term Rescue of Dystrophin Expression and Improvement in Muscle Pathology and Function in Dystrophic mdx Mice by Peptide-Conjugated Morpholino
Wu, Bo, Lu, Peijuan, Cloer, Caryn, Shaban, Mona, Grewal, Snimar, Milazi, Stephanie, Shah, Sapana N, Moulton, Hong M, Lu, Qi Long
Published in The American journal of pathology (01.08.2012)
Published in The American journal of pathology (01.08.2012)
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Journal Article
Glucocorticoid Steroid and Alendronate Treatment Alleviates Dystrophic Phenotype with Enhanced Functional Glycosylation of α-Dystroglycan in Mouse Model of Limb-Girdle Muscular Dystrophy with FKRPP448L Mutation
Wu, Bo, Shah, Sapana N, Lu, Peijuan, Milazi, Stephanie, Bollinger, Lauren E, Blaeser, Anthony, Madden, Kyle L, Sun, Yubo, Luckie, Taylor M, Cox, Michael D, Sparks, Susan, Harper, Amy D, Lu, Qi Long
Published in The American journal of pathology (01.06.2016)
Published in The American journal of pathology (01.06.2016)
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Journal Article
148. Screening and Optimization of Antisense Oligonucleotide for Skipping Human Dystrophin Exon 51 and 53
Wu, Bo, Lu, Peijuan, Shah, Sapana N., Milazi, Stephanie, Bollinger, Lauren E., Long Lu, Qi
Published in Molecular therapy (01.05.2015)
Published in Molecular therapy (01.05.2015)
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Journal Article
Long-Term Rescue of Skeletal and Cardiac Muscles in Dystrophic Mdx Mice by Peptide- Conjugated Morpholino
Wu, Bo, Lu, Peijuan, Cloer, Caryn, Shaban, Mona, Grewal, Snimar, Milazi, Stephanie, Shah, Sapana N, Moulton, Hong, Lu, Qi Long
Published in Molecular therapy (01.09.2012)
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Published in Molecular therapy (01.09.2012)
Journal Article