Exon skipping restores dystrophin expression, but fails to prevent disease progression in later stage dystrophic dko mice
Wu, B, Cloer, C, Lu, P, Milazi, S, Shaban, M, Shah, S N, Marston-Poe, L, Moulton, H M, Lu, Q L
Published in Gene therapy (01.09.2014)
Published in Gene therapy (01.09.2014)
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Journal Article
Pluronic–PEI copolymers enhance exon-skipping of 2′-O-methyl phosphorothioate oligonucleotide in cell culture and dystrophic mdx mice
Wang, M, Wu, B, Lu, P, Tucker, J D, Milazi, S, Shah, S N, Lu, Q L
Published in Gene therapy (01.01.2014)
Published in Gene therapy (01.01.2014)
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Journal Article