Critical design considerations for time-to-event endpoints in amyotrophic lateral sclerosis clinical trials
van Eijk, Ruben P A, Nikolakopoulos, Stavros, Roes, Kit C B, Middelkoop, Bas M, Ferguson, Toby A, Shaw, Pamela J, Leigh, P Nigel, Al-Chalabi, Ammar, Eijkemans, Marinus J C, van den Berg, Leonard H
Published in Journal of neurology, neurosurgery and psychiatry (01.12.2019)
Published in Journal of neurology, neurosurgery and psychiatry (01.12.2019)
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Randomized double-blind placebo-controlled crossover trial with pyridostigmine in spinal muscular atrophy types 2–4
Stam, Marloes, Wijngaarde, Camiel A, Bartels, Bart, Asselman, Fay-Lynn, Otto, Louise A M, Habets, Laura E, van Eijk, Ruben P A, Middelkoop, Bas M, Goedee, H Stephan, de Groot, Janke F, Roes, Kit C B, Schoenmakers, Marja A G C, Nieuwenhuis, Edward E S, Cuppen, Inge, van den Berg, Leonard H, Wadman, Renske I, van der Pol, W Ludo
Published in Brain communications (2023)
Published in Brain communications (2023)
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Prognosis for patients with amyotrophic lateral sclerosis: development and validation of a personalised prediction model
Westeneng, Henk-Jan, Debray, Thomas P A, Visser, Anne E, van Eijk, Ruben P A, Rooney, James P K, Calvo, Andrea, Martin, Sarah, McDermott, Christopher J, Thompson, Alexander G, Pinto, Susana, Kobeleva, Xenia, Rosenbohm, Angela, Stubendorff, Beatrice, Sommer, Helma, Middelkoop, Bas M, Dekker, Annelot M, van Vugt, Joke J F A, van Rheenen, Wouter, Vajda, Alice, Heverin, Mark, Kazoka, Mbombe, Hollinger, Hannah, Gromicho, Marta, Körner, Sonja, Ringer, Thomas M, Rödiger, Annekathrin, Gunkel, Anne, Shaw, Christopher E, Bredenoord, Annelien L, van Es, Michael A, Corcia, Philippe, Couratier, Philippe, Weber, Markus, Grosskreutz, Julian, Ludolph, Albert C, Petri, Susanne, de Carvalho, Mamede, Van Damme, Philip, Talbot, Kevin, Turner, Martin R, Shaw, Pamela J, Al-Chalabi, Ammar, Chiò, Adriano, Hardiman, Orla, Moons, Karel G M, Veldink, Jan H, van den Berg, Leonard H
Published in Lancet neurology (01.05.2018)
Published in Lancet neurology (01.05.2018)
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CHCHD10 variants in amyotrophic lateral sclerosis: Where is the evidence?
Tazelaar, Gijs H.P., van Rheenen, Wouter, Pulit, Sara L., van der Spek, Rick A.A., Dekker, Annelot M., Moisse, Matthieu, McLaughlin, Russell L., Sproviero, William, Kenna, Kevin P., Kooyman, Maarten, van Doormaal, Perry T.C., van Eijk, Kristel E., Middelkoop, Bas M., Schellevis, Raymond D., Brands, William J., Al‐Chalabi, Ammar, Morrison, Karen E., Shaw, Pamela J., Shaw, Christopher E., Newhouse, Stephen E., van Es, Michael A., Basak, A. Nazli, Akçimen, Fulya, Kocoglu, Cemile, Tunca, Ceren, Povedano, Monica, Mora, Jesus S., Glass, Jonathan D., Van Damme, Philip, Robberecht, Wim, HardimanMD, Orla, Landers, John E., van den Berg, Leonard H., Veldink, Jan H.
Published in Annals of neurology (01.07.2018)
Published in Annals of neurology (01.07.2018)
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